CRISPR-Cas9 cytidine and adenosine base editing of splice-sites mediates highly-efficient disruption of proteins in primary and immortalized cells von Kluesner, Mitchell G., Lahr, Walker S., Lonetree, Cara-lin, Smeester, Branden A., Qiu, Xiaohong, Slipek, Nicholas J., Claudio Vázquez, Patricia N., Pitzen, Samuel P., Pomeroy, Emily J., Vignes, Madison J., Lee, Samantha C., Bingea, Samuel P., Andrew, Aneesha A., Webber, Beau R., Moriarity, Branden S.

Volltext

Highly efficient multiplex human T cell engineering without double-strand breaks using Cas9 base editors von Webber, Beau R., Lonetree, Cara-lin, Kluesner, Mitchell G., Johnson, Matthew J., Pomeroy, Emily J., Diers, Miechaleen D., Lahr, Walker S., Draper, Garrett M., Slipek, Nicholas J., Smeester, Branden A., Lovendahl, Klaus N., McElroy, Amber N., Gordon, Wendy R., Osborn, Mark J., Moriarity, Branden S.

Volltext

A Genetically Engineered Primary Human Natural Killer Cell Platform for Cancer Immunotherapy von Pomeroy, Emily J., Hunzeker, John T., Kluesner, Mitchell G., Lahr, Walker S., Smeester, Branden A., Crosby, Margaret R., Lonetree, Cara-lin, Yamamoto, Kenta, Bendzick, Laura, Miller, Jeffrey S., Geller, Melissa A., Walcheck, Bruce, Felices, Martin, Webber, Beau R., Starr, Timothy K., Moriarity, Branden S.

Volltext

A New Immuno‐, Dystrophin‐Deficient Model, the NSG‐mdx4Cv Mouse, Provides Evidence for Functional Improvement Following Allogeneic Satellite Cell Transplantation von Arpke, Robert W., Darabi, Radbod, Mader, Tara L., Zhang, Yu, Toyama, Akira, Lonetree, Cara‐lin, Nash, Nardina, Lowe, Dawn A., Perlingeiro, Rita C.R., Kyba, Michael

Volltext

Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases von Osborn, Mark J, Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, Tennis, Nicole, DeFeo, Anthony P, McElroy, Amber N, Starker, Colby G, Lee, Catherine, Merkel, Sarah, Lund, Troy C, Kelly-Spratt, Karen S, Jensen, Michael C, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Gabriel, Richard, Hippen, Keli L, Miller, Jeffrey S, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R

Volltext

A Pan-RNase Inhibitor Enabling CRISPR-mRNA Platforms for Engineering of Primary Human Monocytes von Laoharawee, Kanut, Johnson, Matthew J., Lahr, Walker S., Sipe, Christopher J., Kleinboehl, Evan, Peterson, Joseph J., Lonetree, Cara-lin, Bell, Jason B., Slipek, Nicholas J., Crane, Andrew T., Webber, Beau R., Moriarity, Branden S.

Volltext

CRISPR/Cas9-based genetic correction for recessive dystrophic epidermolysis bullosa von Webber, Beau R, Osborn, Mark J, McElroy, Amber N, Twaroski, Kirk, Lonetree, Cara-lin, DeFeo, Anthony P, Xia, Lily, Eide, Cindy, Lees, Christopher J, McElmurry, Ron T, Riddle, Megan J, Kim, Chong Jai, Patel, Dharmeshkumar D, Blazar, Bruce R, Tolar, Jakub

Volltext

CRISPR/Cas9 Targeted Gene Editing and Cellular Engineering in Fanconi Anemia von Osborn, Mark J., Lonetree, Cara-lin, Webber, Beau R., Patel, Dharmeshkumar, Dunmire, Samantha, DeFeo, Anthony P., McElroy, Amber N., MacMillan, Margaret L., Wagner, John E., Blazar, Bruce R., Tolar, Jakub

Volltext

Author Correction: Highly efficient multiplex human T cell engineering without double-strand breaks using Cas9 base editors von Webber, Beau R., Lonetree, Cara-lin, Kluesner, Mitchell G., Johnson, Matthew J., Pomeroy, Emily J., Diers, Miechaleen D., Lahr, Walker S., Draper, Garrett M., Slipek, Nicholas J., Smeester, Branden A., Lovendahl, Klaus N., McElroy, Amber N., Gordon, Wendy R., Osborn, Mark J., Moriarity, Branden S.

Volltext

A new immuno-, dystrophin-deficient model, the NSG-mdx(4Cv) mouse, provides evidence for functional improvement following allogeneic satellite cell transplantation von Arpke, Robert W, Darabi, Radbod, Mader, Tara L, Zhang, Yu, Toyama, Akira, Lonetree, Cara-Lin, Nash, Nardina, Lowe, Dawn A, Perlingeiro, Rita C R, Kyba, Michael

Volltext

Multiplex Human T Cell Engineering without Double-Strand Break Induction Using the Cas9 Base Editor System von Webber, Beau, Lonetree, Cara-lin, Diers, Miechaleen, Lahr, Walker S, Mitchell, Kluesner, Johnson, Matthew J, Moriarity, Branden S

Volltext

Megatal, Crispr/Cas9, and Talen T-Cell Receptor Gene Editing von Osborn, Mark J., Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, DeFeo, Anthony, McElroy, Amber, Starker, Colby, Gabriel, Richard, Merkel, Sarah, Hippen, Keli L., Voytas, Daniel, von Kalle, Christof, Schmidt, Manfred, Miller, Jeffrey S., Jarjour, Jordan, Astrakhan, Alexander, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R.

Volltext

A New Immuno-, Dystrophin-Deficient Model, the NSG-mdx 4Cv Mouse, Provides Evidence for Functional Improvement Following Allogeneic Satellite Cell Transplantation von Arpke, Robert W., Darabi, Radbod, Mader, Tara L., Zhang, Yu, Toyama, Akira, Lonetree, Cara-lin, Nash, Nardina, Lowe, Dawn A., Perlingeiro, Rita C.R., Kyba, Michael

Volltext

A New Immuno-, Dystrophin-Deficient Model, the NSG-mdx super(4Cv) Mouse, Provides Evidence for Functional Improvement Following Allogeneic Satellite Cell Transplantation von Arpke, Robert W, Darabi, Radbod, Mader, Tara L, Zhang, Yu, Toyama, Akira, Lonetree, Cara-lin, Nash, Nardina, Lowe, Dawn A, Perlingeiro, Rita CR, Kyba, Michael

Volltext

LYMPHOHEMATOPOIETIC ENGINEERING USING CAS9 BASE EDITORS von CARA-LIN LONETREE, BRANDEN MORIARITY, WALKER LAHR, MIECHALEEN DIERS, MITCHELL KLUESNER, EMILY JOY POMEROY, BEAU WEBBER

Volltext bestellen

LYMPHOHEMATOPOIETIC ENGINEERING USING CAS9 BASE EDITORS von DIERS, Miechaleen, LAHR, Walker, WEBBER, Beau, LONETREE, Cara-Lin, MORIARITY, Branden, KLUESNER, Mitchell, POMEROY, Emily Joy

Volltext bestellen

LYMPHOHEMATOPOIETIC ENGINEERING USING CAS9 BASE EDITORS von Diers, Miechaleen, Lahr, Walker, Lonetree, Cara-Lin, Pomeroy, Emily Joy, Moriarity, Branden, Webber, Beau, Kluesner, Mitchell

Volltext bestellen

LYMPHOHEMATOPOIETIC ENGINEERING USING CAS9 BASE EDITORS von DIERS, Miechaleen, LAHR, Walker, WEBBER, Beau, LONETREE, Cara-Lin, MORIARITY, Branden, KLUESNER, Mitchell, POMEROY, Emily Joy

Volltext bestellen

Lymphohematopoietic engineering using Cas9 base editors von DIERS, Miechaleen, LAHR, Walker, WEBBER, Beau, LONETREE, Cara-Lin, MORIARITY, Branden, KLUESNER, Mitchell, POMEROY, Emily Joy

Volltext bestellen

LYMPHOHEMATOPOIETIC ENGINEERING USING CAS9 BASE EDITORS von DIERS, Miechaleen, LAHR, Walker, WEBBER, Beau, LONETREE, Cara-Lin, POMEROY, Emily, MORIARITY, Branden, KLUESNER, Mitchell

Volltext bestellen