In vivo discovery of a peptide that prevents CUG-RNA hairpin formation and reverses RNA toxicity in myotonic dystrophy models von García-López, Amparo, Llamusí, Beatriz, Orzáez, Mar, Pérez-Payá, Enrique, Artero, Ruben D

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Therapeutic Potential of AntagomiR-23b for Treating Myotonic Dystrophy von Cerro-Herreros, Estefanía, González-Martínez, Irene, Moreno-Cervera, Nerea, Overby, Sarah, Pérez-Alonso, Manuel, Llamusí, Beatriz, Artero, Rubén

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Expanded CCUG repeat RNA expression in Drosophila heart and muscle trigger Myotonic Dystrophy type 1-like phenotypes and activate autophagocytosis genes von Cerro-Herreros, Estefania, Chakraborty, Mouli, Pérez-Alonso, Manuel, Artero, Rubén, Llamusí, Beatriz

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Quantitative Assessment of Eye Phenotypes for Functional Genetic Studies Using Drosophila melanogaster von Iyer, Janani, Wang, Qingyu, Le, Thanh, Pizzo, Lucilla, Grönke, Sebastian, Ambegaokar, Surendra S, Imai, Yuzuru, Srivastava, Ashutosh, Troisí, Beatriz Llamusí, Mardon, Graeme, Artero, Ruben, Jackson, George R, Isaacs, Adrian M, Partridge, Linda, Lu, Bingwei, Kumar, Justin P, Girirajan, Santhosh

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The Drosophila junctophilin gene is functionally equivalent to its four mammalian counterparts and is a modifier of a Huntingtin poly-Q expansion and the Notch pathway von Calpena, Eduardo, López Del Amo, Víctor, Chakraborty, Mouli, Llamusí, Beatriz, Artero, Rubén, Espinós, Carmen, Galindo, Máximo I

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BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSALR Mice von Overby, Sarah J., Cerro-Herreros, Estefanía, Espinosa-Espinosa, Jorge, González-Martínez, Irene, Moreno, Nerea, Fernández-Costa, Juan M., Balaguer-Trias, Jordina, Ramón-Azcón, Javier, Pérez-Alonso, Manuel, Møller, Thorleif, Llamusí, Beatriz, Artero, Rubén

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BlockmiR AONs as Site-Specific Therapeutic MBNL Modulation in Myotonic Dystrophy 2D and 3D Muscle Cells and HSA[sup.LR] Mice von Overby, Sarah J, Cerro-Herreros, Estefanía, Espinosa-Espinosa, Jorge, González-Martínez, Irene, Moreno, Nerea, Fernández-Costa, Juan M, Balaguer-Trias, Jordina, Ramón-Azcón, Javier, Pérez-Alonso, Manuel, Møller, Thorleif, Llamusí, Beatriz, Artero, Rubén

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Molecular Effects of the CTG Repeats in Mutant Dystrophia Myotonica Protein Kinase Gene von Llamusí, Beatriz, Artero, Ruben

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Telomerase protects adult rodent olfactory ensheathing glia from early senescence von Llamusí, María-Beatriz, Rubio, Mari-Paz, Ramón-Cueto, Almudena

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Peptide-conjugated antimiRs improve myotonic dystrophy type 1 phenotypes by promoting endogenous MBNL1 expression von González-Martínez, Irene, Cerro-Herreros, Estefanía, Moreno, Nerea, García-Rey, Andrea, Espinosa-Espinosa, Jorge, Carrascosa-Sàez, Marc, Piqueras-Losilla, Diego, Arzumanov, Andrey, Seoane-Miraz, David, Jad, Yahya, Raz, Richard, Wood, Matthew J., Varela, Miguel A., Llamusí, Beatriz, Artero, Rubén

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Proof of concept of peptide-linked blockmiR-induced MBNL functional rescue in myotonic dystrophy type 1 mouse model von Overby, Sarah J., Cerro-Herreros, Estefanía, González-Martínez, Irene, Varela, Miguel A., Seoane-Miraz, David, Jad, Yahya, Raz, Richard, Møller, Thorleif, Pérez-Alonso, Manuel, Wood, Matthew J., Llamusí, Beatriz, Artero, Rubén

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RNA-mediated therapies in myotonic dystrophy von Overby, Sarah J., Cerro-Herreros, Estefanía, Llamusi, Beatriz, Artero, Ruben

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miR-23b and miR-218 silencing increase Muscleblind-like expression and alleviate myotonic dystrophy phenotypes in mammalian models von Cerro-Herreros, Estefania, Sabater-Arcis, Maria, Fernandez-Costa, Juan M., Moreno, Nerea, Perez-Alonso, Manuel, Llamusi, Beatriz, Artero, Ruben

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Rabphilin silencing causes dilated cardiomyopathy in a Drosophila model of nephrocyte damage von Selma-Soriano, Estela, Casillas-Serra, Carlos, Artero, Rubén, Llamusi, Beatriz, Navarro, Juan Antonio, Redón, Josep

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Preclinical characterization of antagomiR-218 as a potential treatment for myotonic dystrophy von Cerro-Herreros, Estefanía, González-Martínez, Irene, Moreno, Nerea, Espinosa-Espinosa, Jorge, Fernández-Costa, Juan M., Colom-Rodrigo, Anna, Overby, Sarah J., Seoane-Miraz, David, Poyatos-García, Javier, Vilchez, Juan J., López de Munain, Adolfo, Varela, Miguel A., Wood, Matthew J., Pérez-Alonso, Manuel, Llamusí, Beatriz, Artero, Rubén

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Defined d-hexapeptides bind CUG repeats and rescue phenotypes of myotonic dystrophy myotubes in a Drosophila model of the disease von Rapisarda, Anna, Bargiela, Ariadna, Llamusi, Beatriz, Pont, Isabel, Estrada-Tejedor, Roger, Garcia-España, Enrique, Artero, Ruben, Perez-Alonso, Manuel

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The use of whole‐mount in situ hybridization to illustrate gene expression regulation von Llamusí, Beatriz, Muñoz‐Soriano, Verónica, Paricio, Nuria, Artero, Rubén

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rbFOX1/MBNL1 competition for CCUG RNA repeats binding contributes to myotonic dystrophy type 1/type 2 differences von Sellier, Chantal, Cerro-Herreros, Estefanía, Blatter, Markus, Freyermuth, Fernande, Gaucherot, Angeline, Ruffenach, Frank, Sarkar, Partha, Puymirat, Jack, Udd, Bjarne, Day, John W., Meola, Giovanni, Bassez, Guillaume, Fujimura, Harutoshi, Takahashi, Masanori P., Schoser, Benedikt, Furling, Denis, Artero, Ruben, Allain, Frédéric H. T., Llamusi, Beatriz, Charlet-Berguerand, Nicolas

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Chronic Spinal Injury Repair by Olfactory Bulb Ensheathing Glia and Feasibility for Autologous Therapy von Muñoz-Quiles, Cintia, Santos-Benito, Fernando F, Llamusi, M Beatriz, Ramón-Cueto, Almudena

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Alternative splicing regulation by Muscleblind proteins: from development to disease von Fernandez-Costa, Juan M., Llamusi, M. Beatriz, Garcia-Lopez, Amparo, Artero, Ruben

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