Transient Inhibition of TrkB Kinase after Status Epilepticus Prevents Development of Temporal Lobe Epilepsy von Liu, Gumei, Gu, Bin, He, Xiao-Ping, Joshi, Rasesh B., Wackerle, Harold D., Rodriguiz, Ramona Marie, Wetsel, William C., McNamara, James O.

Volltext

Analysis of the first ten years of FDA's rare pediatric disease priority review voucher program: designations, diseases, and drug development von Mease, Catherine, Miller, Kathleen L, Fermaglich, Lewis J, Best, Jeanine, Liu, Gumei, Torjusen, Erika

Volltext

Correction to: Analysis of the first ten years of FDA's rare pediatric disease priority review voucher program: designations, diseases, and drug development von Mease, Catherine, Miller, Kathleen L, Fermaglich, Lewis J, Best, Jeanine, Liu, Gumei, Torjusen, Erika

Volltext

FDA orphan products clinical trial grants: assessment of outcomes and impact on rare disease product development von Miller, Kathleen L, Mueller, Christine, Liu, Gumei, Miller Needleman, Katherine I, Maynard, Janet

Volltext

Cross-sector sponsorship of research in eosinophilic esophagitis: A collaborative model for rational drug development in rare diseases von Fiorentino, Robert, MD, Liu, Gumei, MD, PhD, Pariser, Anne R., MD, Mulberg, Andrew E., MD

Volltext

Antiseizure effects of TrkB kinase inhibition von Liu, Gumei, Kotloski, Robert J, McNamara, James O.

Volltext

Altered Purkinje cell miRNA expression and SCA1 pathogenesis von Rodriguez-Lebron, Edgardo, Liu, Gumei, Keiser, Megan, Behlke, Mark A, Davidson, Beverly L

Volltext

The cellular and synaptic location of activated TrkB in mouse hippocampus during limbic epileptogenesis von Helgager, Jeffrey, Liu, Gumei, McNamara, James O.

Volltext

Functional Correction of CNS Phenotypes in a Lysosomal Storage Disease Model Using Adeno-Associated Virus Type 4 Vectors von Liu, Gumei, Martins, Ines, Wemmie, John A, Chiorini, John A, Davidson, Beverly L

Volltext

Long-term Antibacterial Properties and Bond Strength of Experimental Nano Silver-containing Orthodontic Cements von Li, Fujun, Li, Zubing, Liu, Gumei, He, Hong

Volltext

Conditional deletion of TrkC does not modify limbic epileptogenesis von Soren Leonard, A, Puranam, Ram S, Helgager, Jeffrey, Liu, Gumei, McNamara, James O

Volltext

Food and Drug Administration's Humanitarian Device Exemption Marketing Approval Pathway: Insights for Developing Devices for Rare Diseases von Liu, Gumei, Chen, Eric, Lewis, Debra, Rao, Gayatri

Volltext

The cellular and synaptic location of activated TrkB in mouse hippocampus during limbic epileptogenesis von Helgager, Jeffrey, Liu, Gumei, McNamara, James O.

Volltext

Transient Inhibition of TrkB Kinase Following Status Epilepticus Prevents Development of Temporal Lobe Epilepsy von Liu, Gumei, Gu, Bin, He, Xiao-Ping, Joshi, Rasesh B., Wackerle, Harold D., Rodriguiz, Ramona Marie, Wetsel, William C., McNamara, James O.

Volltext

8th European Conference on Rare Diseases Orphan Products von Schlander, Michael, Holm, Saren, Nord, Erik, Richardson, Jeff, Garattini, Silvio, Kolominsky-Rabas, Peter, Marshall, Deborah, Persson, Ulf, Postma, Maarten, Simoens, Steven, de Sola Morales, Oriol, Tolley, Keith, Toumi, Mondher, Telser, Harry, Bonham, James R, Hintner, Helmut, Diem, Anja, Laimer, Martin, Hnbert, Rnjean, Dasgupta, Nabarun, Pierce, Carrie E, Jordan, Melissa, Bori, Barbara, Fors, Mohanad, Prazakova, Emilie, Day, Simon, Croce, Thomas J, Fransson, Jonas, Wood, Philip, Lauridsen, Anne-Grethe, Higgs, Joanne, Aleksovska, Vesna Stojmirova, Olsen, Christina, Head, Ritchie, Asero, Antonio, Papa, Vincenzo, van Kan, Christa, Favennec, Loic, Venturella, Silvana, Salvador, Michela, Krol, Alan, Nielsen, Stephanie J, Holm, Birthe B, Lewi, Daniel, DurA£o, Patricia, Band, Heather, West, Andrea, Hammann, Marinda J. A, Effing-Boele, Marije C, Dekker, Hanka K, Hunter, Amy, Simpson, Amy, Liu, Gumei, Needleman, Katherine, Lewis, Debra, Rao, Gayatri, Whitaker, Martin J, Castro, Raquel

Volltext

8th European Conference on Rare Diseases & Orphan Products (ECRD 2016): Edinburgh, UK. 26-28 May 2016 von Schlander, Michael, Holm, Søren, Nord, Erik, Richardson, Jeff, Garattini, Silvio, Kolominsky-Rabas, Peter, Marshall, Deborah, Persson, Ulf, Postma, Maarten, Simoens, Steven, de Solà Morales, Oriol, Tolley, Keith, Toumi, Mondher, Telser, Harry, Bonham, James R, Hintner, Helmut, Diem, Anja, Laimer, Martin, Hébert, Réjean, Dasgupta, Nabarun, Pierce, Carrie E., Jordan, Melissa, Bori, Barbara, Fors, Mohanad, Prazakova, Emilie, Day, Simon, Croce, Thomas J., Fransson, Jonas, Wood, Philip, Lauridsen, Anne-Grethe, Higgs, Joanne, Aleksovska, Vesna Stojmirova, Olsen, Christina, Head, Ritchie, Asero, Antonio, Papa, Vincenzo, van Kan, Christa, Favennec, Loic, Venturella, Silvana, Salvador, Michela, Krol, Alan, Nielsen, Stephanie J., Holm, Birthe B., Lewi, Daniel, Durão, Patricia, Band, Heather, West, Andrea, Hammann, Marinda J. A., Effing-Boele, Marije C., Dekker, Hanka K., Hunter, Amy, Simpson, Amy, Liu, Gumei, Needleman, Katherine, Lewis, Debra, Rao, Gayatri, Whitaker, Martin J., Castro, Raquel

Volltext

Adeno-associated Virus Type 5 Reduces Learning Deficits and Restores Glutamate Receptor Subunit Levels in MPS VII Mice CNS von Liu, Gumei, Chen, Yong Hong, He, Xiaohua, Martins, Inês, Heth, Jason A, Chiorini, John A, Davidson, Beverly L

Volltext

229. AAV4 Mediated Gene Transfer in Mucopolysaccharidosis Type VII Mice von Liu, Gumei, Chiorini, John A, Davidson, Beverly L

Volltext

230. Neural Progenitor Cell Transduction with AAV Serotypes 1 and 4 von Liu, Gumei, Kotin, Robert M, Chiorini, John A, Davidson, Beverly L

Volltext

Methods for the Prevention or Treatment of Epilepsy von Liu, Gumei, Mook, Robert, McNamara, James O, Gu, Bin, Huang, Yangzhong, Krishnamurthy, Kamesh, He, Xiao-Ping

Volltext bestellen