The Phenotype of a Germline Mutation in PIGA: The Gene Somatically Mutated in Paroxysmal Nocturnal Hemoglobinuria von Johnston, Jennifer J., Gropman, Andrea L., Sapp, Julie C., Teer, Jamie K., Martin, Jodie M., Liu, Cyndi F., Yuan, Xuan, Ye, Zhaohui, Cheng, Linzhao, Brodsky, Robert A., Biesecker, Leslie G.

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Differential Sensitivity to JAK Inhibitory Drugs by Isogenic Human Erythroblasts and Hematopoietic Progenitors Generated from Patient‐Specific Induced Pluripotent Stem Cells von Ye, Zhaohui, Liu, Cyndi F., Lanikova, Lucie, Dowey, Sarah N., He, Chaoxia, Huang, Xiaosong, Brodsky, Robert A., Spivak, Jerry L., Prchal, Josef T., Cheng, Linzhao

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Efficient Derivation and Genetic Modifications of Human Pluripotent Stem Cells on Engineered Human Feeder Cell Lines von Zou, Chunlin, Chou, Bin-Kuan, Dowey, Sarah N., Tsang, Kitman, Huang, Xiaosong, Liu, Cyndi F., Smith, Cory, Yen, Jonathan, Mali, Prashant, Zhang, Yu Alex, Cheng, Linzhao, Ye, Zhaohui

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Hematopoietic cells as sources for patient-specific iPSCs and disease modeling von Ye, Zhaohui, Liu, Cyndi F., Jang, Yoon-Young

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Generation of Glycosylphosphatidylinositol Anchor Protein‐Deficient Blood Cells From Human Induced Pluripotent Stem Cells von Yuan, Xuan, Braunstein, Evan M., Ye, Zhaohui, Liu, Cyndi F., Chen, Guibin, Zou, Jizhong, Cheng, Linzhao, Brodsky, Robert A.

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Direct Reprogramming of Human Primordial Germ Cells into Induced Pluripotent Stem Cells: Efficient Generation of Genetically Engineered Germ Cells von Bazley, Faith A., Liu, Cyndi F., Yuan, Xuan, Hao, Haiping, All, Angelo H., De Los Angeles, Alejandro, Zambidis, Elias T., Gearhart, John D., Kerr, Candace L.

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Generation of GPI Anchor Deficient Blood Cells From Human iPSCs von Yuan, Xuan, Ye, Zhaohui, Liu, Cyndi F., Zou, Jizhong, Cheng, Linzhao, Brodsky, Robert A.

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Distinct Induced Pluripotent Stem Cell Clones with Somatic Mutations Prepared From PV Patients von Ye, Zhaohui, Piterkova, Lucie, Liu, Cyndi F, Dowey, Sarah N, Chou, Bin-Kuan, Huang, Xiaosong, Spivak, Jerry L., Swierczek, Sabina, Moliterno, Alison R., Prchal, Josef T., Cheng, Linzhao

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Clinical sites of the Undiagnosed Diseases Network: unique contributions to genomic medicine and science von Schoch, Kelly, Esteves, Cecilia, Bican, Anna, Spillmann, Rebecca, Cope, Heidi, McConkie-Rosell, Allyn, Walley, Nicole, Fernandez, Liliana, Kohler, Jennefer N., Bonner, Devon, Reuter, Chloe, Stong, Nicholas, Mulvihill, John J., Novacic, Donna, Wolfe, Lynne, Abdelbaki, Ayat, Toro, Camilo, Tifft, Cyndi, Malicdan, May, Gahl, William, Liu, Pengfei, Newman, John, Goldstein, David B., Hom, Jason, Sampson, Jacinda, Wheeler, Matthew T., Cogan, Joy, Bernstein, Jonathan A., Adams, David R., McCray, Alexa T., Shashi, Vandana

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Direct and indirect costs associated with stereotactic radiosurgery or open surgery for medial temporal lobe epilepsy: Results from the ROSE trial von Langfitt, John T., Quigg, Mark, Yan, Guofen, Yu, Wei, Ward, Mariann M., Barbaro, Nicholas M., Chang, Edward F., Broshek, Donna K., Laxer, Kenneth D., Cole, Andrew J., Sneed, Penny K., Hess, Christopher, Tripathi, Manjari, Heck, Christiaanne N., Miller, John W., Garcia, Paul A., McEvoy, Andrew, Fountain, Nathan B., Salanova, Vicenta, Knowlton, Robert C., Bagić, Anto, Henry, Thomas, Kapoor, Siddharth, McKhann, Guy, Palade, Adriana E., Reuber, Markus, Tecoma, Evelyn

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Biological Differences in rAAV Transduction of Airway Epithelia in Humans and in Old World Non-human Primates von Liu, Xiaoming, Luo, Meihui, Trygg, Cyndi, Yan, Ziying, Lei-Butters, Diana CM, Smith, Carolina I, Fischer, Anne C, Munson, Keith, Guggino, William B, Bunnell, Bruce A, Engelhardt, John F

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1. Species Choice for Animal Modeling Cystic Fibrosis and Gene Therapy to the Airway von Liu, Xiaoming, Yan, Ziying, Luo, Meihui, Zhang, Liang N., Trygg, Cyndi, Smith, Carolina, Munson, Keith, Guggino, William, Bunnell, Bruce, Engelhardt, John F.

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