Targeting RNA-Mediated Toxicity in C9orf72 ALS and/or FTD by RNAi-Based Gene Therapy von Martier, Raygene, Liefhebber, Jolanda M., García-Osta, Ana, Miniarikova, Jana, Cuadrado-Tejedor, Mar, Espelosin, Maria, Ursua, Susana, Petry, Harald, van Deventer, Sander J., Evers, Melvin M., Konstantinova, Pavlina

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Artificial MicroRNAs Targeting C9orf72 Can Reduce Accumulation of Intra-nuclear Transcripts in ALS and FTD Patients von Martier, Raygene, Liefhebber, Jolanda M., Miniarikova, Jana, van der Zon, Tom, Snapper, Jolanda, Kolder, Iris, Petry, Harald, van Deventer, Sander J., Evers, Melvin M., Konstantinova, Pavlina

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Modulation of Triglyceride and Cholesterol Ester Synthesis Impairs Assembly of Infectious Hepatitis C Virus von Liefhebber, Jolanda M.P., Hague, Charlotte V., Zhang, Qifeng, Wakelam, Michael J.O., McLauchlan, John

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PhP.B Enhanced Adeno-Associated Virus Mediated-Expression Following Systemic Delivery or Direct Brain Administration von Pietersz, Kimberly L., Du Plessis, Francois, Pouw, Stephan M., Liefhebber, Jolanda M., van Deventer, Sander J., Martens, Gerard J. M., Konstantinova, Pavlina S., Blits, Bas

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In-Depth Characterization of a Mifepristone-Regulated Expression System for AAV5-Mediated Gene Therapy in the Liver von Liefhebber, Jolanda M., Martier, Raygene, Van der Zon, Tom, Keskin, Sonay, Huseinovic, Angelina, Lubelski, Jacek, Blits, Bas, Petry, Harald, Konstantinova, Pavlina

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Characterization of hepatitis C virus NS3 modifications in the context of replication von LIEFHEBBER, Jolanda M. P, HENSBERGEN, Paul J, DEELDER, André M, SPAAN, Willy J. M, VAN LEEUWEN, Hans C

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Repair and Polyadenylation of a Naturally Occurring Hepatitis C Virus 3′ Nontranslated Region-Shorter Variant in Selectable Replicon Cell Lines von VAN LEEUWEN, Hans C, LIEFHEBBER, Jolanda M. P, SPAAN, Willy J. M

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Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model von Zancanella, Vanessa, Vallès, Astrid, Liefhebber, Jolanda M.P., Paerels, Lieke, Tornero, Carlos Vendrell, Wattimury, Hendrina, van der Zon, Tom, van Rooijen, Kristel, Golinska, Monika, Grevelink, Tamar, Ehlert, Erich, Pieterman, Elsbet Jantine, Keijzer, Nanda, Princen, Hans Marinus Gerardus, Stokman, Geurt, Liu, Ying Poi

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Natural swimming speed of Dascyllus reticulatus increases with water temperature von Beyan, Cigdem, Boom, Bastian J, Liefhebber, Jolanda M P, Shao, Kwang-Tsao, Fisher, Robert B

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Hepatitis C virus NS4B carboxy terminal domain is a membrane binding domain von Liefhebber, Jolanda M P, Brandt, Bernd W, Broer, Rene, Spaan, Willy J M, van Leeuwen, Hans C

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Viral genotype correlates with distinct liver gene transcription signatures in chronic hepatitis C virus infection von Robinson, Mark W., Aranday-Cortes, Elihu, Gatherer, Derek, Swann, Rachael, Liefhebber, Jolanda M. P., Filipe, Ana Da Silva, Sigruener, Alex, Barclay, Stephen T., Mills, Peter R., Patel, Arvind H., McLauchlan, John

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Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model von Zancanella, Vanessa, Vallès, Astrid, Liefhebber, Jolanda M.P., Paerels, Lieke, Tornero, Carlos Vendrell, Wattimury, Hendrina, van der Zon, Tom, van Rooijen, Kristel, Golinska, Monika, Grevelink, Tamar, Ehlert, Erich, Pieterman, Elsbet Jantine, Keijzer, Nanda, Gerardus Princen, Hans Marinus, Stokman, Geurt, Liu, Ying Poi

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The human collagen beta(1-O)galactosyltransferase, GLT25D1, is a soluble endoplasmic reticulum localized protein von Liefhebber, Jolanda Mp, Punt, Simone, Spaan, Willy Jm, van Leeuwen, Hans C

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Exosomes contain ubiquitinated proteins von Buschow, Sonja I., Liefhebber, Jolanda M.P., Wubbolts, Richard, Stoorvogel, Willem

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Erratum: Proof-of-concept study for liver-directed miQURE technology in a dyslipidemic mouse model von Zancanella, Vanessa, Vallès, Astrid, Liefhebber, Jolanda M P, Paerels, Lieke, Tornero, Carlos Vendrell, Wattimury, Hendrina, van der Zon, Tom, van Rooijen, Kristel, Golinska, Monika, Grevelink, Tamar, Ehlert, Erich, Pieterman, Elsbet Jantine, Keijzer, Nanda, Gerardus Princen, Hans Marinus, Stokman, Geurt, Liu, Ying Poi

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The human collagen betagalactosyltransferase, GLT25D1, is a soluble endoplasmic reticulum localized protein von Liefhebber, Jolanda MP, Punt, Simone, Spaan, Willy JM, van Leeuwen, Hans C

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Preclinical efficacy and safety of adeno-associated virus 5 alpha-galactosidase A gene therapy for Fabry disease von Liefhebber, Jolanda M.P., Brasser, Giso, Spronck, Elisabeth A., Ottenhoff, Roelof, Paerels, Lieke, Ferraz, Maria J., Schwarz, Lukas K., Efthymiopoulou, Nikoleta, Kuo, Chi-Lin, Montenegro-Miranda, Paula S., Evers, Melvin M., Aerts, Johannes M.F.G., Liu, Ying Poi

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Development of an AAV5-based gene therapy for Fabry disease von Liu, Ying Poi, Liefhebber, Jolanda M.P., van der Zon, Tom, Paerels, Lieke, Ferraz, Maria J., Ottenhoff, Roelof, Zancanella, Vanessa, Au, Betty, Kuo, Chi-Lin, de Vries, Carlie J.M., Evers, Melvin M., Konstantinova, Pavlina, Aerts, Johannes M.F.G., Van Deventer, Sander J.

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