Gene Therapy in a Patient with Sickle Cell Disease von Ribeil, Jean-Antoine, Hacein-Bey-Abina, Salima, Payen, Emmanuel, Magnani, Alessandra, Semeraro, Michaela, Magrin, Elisa, Caccavelli, Laure, Neven, Benedicte, Bourget, Philippe, El Nemer, Wassim, Bartolucci, Pablo, Weber, Leslie, Puy, Hervé, Meritet, Jean-François, Grevent, David, Beuzard, Yves, Chrétien, Stany, Lefebvre, Thibaud, Ross, Robert W, Negre, Olivier, Veres, Gabor, Sandler, Laura, Soni, Sandeep, de Montalembert, Mariane, Blanche, Stéphane, Leboulch, Philippe, Cavazzana, Marina

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Long-term outcomes of lentiviral gene therapy for the β-hemoglobinopathies: the HGB-205 trial von Magrin, Elisa, Semeraro, Michaela, Hebert, Nicolas, Joseph, Laure, Magnani, Alessandra, Chalumeau, Anne, Gabrion, Aurélie, Roudaut, Cécile, Marouene, Jouda, Lefrere, Francois, Diana, Jean-Sebastien, Denis, Adeline, Neven, Bénédicte, Funck-Brentano, Isabelle, Negre, Olivier, Renolleau, Sylvain, Brousse, Valentine, Kiger, Laurent, Touzot, Fabien, Poirot, Catherine, Bourget, Philippe, El Nemer, Wassim, Blanche, Stéphane, Tréluyer, Jean-Marc, Asmal, Mohammed, Walls, Courtney, Beuzard, Yves, Schmidt, Manfred, Hacein-Bey-Abina, Salima, Asnafi, Vahid, Guichard, Isabelle, Poirée, Maryline, Monpoux, Fabrice, Touraine, Philippe, Brouzes, Chantal, de Montalembert, Mariane, Payen, Emmanuel, Six, Emmanuelle, Ribeil, Jean-Antoine, Miccio, Annarita, Bartolucci, Pablo, Leboulch, Philippe, Cavazzana, Marina

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Lovo‐cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB‐206 study von Kanter, Julie, Thompson, Alexis A., Pierciey, Francis J., Hsieh, Matthew, Uchida, Naoya, Leboulch, Philippe, Schmidt, Manfred, Bonner, Melissa, Guo, Ruiting, Miller, Alex, Ribeil, Jean‐Antoine, Davidson, David, Asmal, Mohammed, Walters, Mark C., Tisdale, John F.

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Current and future alternative therapies for beta-thalassemia major von de Dreuzy, Edouard, Bhukhai, Kanit, Leboulch, Philippe, Payen, Emmanuel

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Angiogenic synergism, vascular stability and improvement of hind-limb ischemia by a combination of PDGF-BB and FGF-2 von Cao, Renhai, Bråkenhielm, Ebba, Pawliuk, Robert, Wariaro, David, Post, Mark J., Wahlberg, Eric, Leboulch, Philippe, Cao, Yihai

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Dynamics of gene-modified progenitor cells analyzed by tracking retroviral integration sites in a human SCID-X1 gene therapy trial von Wang, Gary P., Berry, Charles C., Malani, Nirav, Leboulch, Philippe, Fischer, Alain, Hacein-Bey-Abina, Salima, Cavazzana-Calvo, Marina, Bushman, Frederic D.

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Atypical BSE (BASE) transmitted from asymptomatic aging cattle to a primate von Comoy, Emmanuel E, Casalone, Cristina, Lescoutra-Etchegaray, Nathalie, Zanusso, Gianluigi, Freire, Sophie, Marcé, Dominique, Auvré, Frédéric, Ruchoux, Marie-Magdeleine, Ferrari, Sergio, Monaco, Salvatore, Salès, Nicole, Caramelli, Maria, Leboulch, Philippe, Brown, Paul, Lasmézas, Corinne I, Deslys, Jean-Philippe

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A method to sequence and quantify DNA integration for monitoring outcome in gene therapy von Brady, Troy, Roth, Shoshannah L., Malani, Nirav, Wang, Gary P., Berry, Charles C., Leboulch, Philippe, Hacein-Bey-Abina, Salima, Cavazzana-Calvo, Marina, Papapetrou, Eirini P., Sadelain, Michel, Savilahti, Harri, Bushman, Frederic D.

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Clinical outcomes of lentiviral gene therapy for the beta-hemogolobinpathies von Leboulch, Philippe

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Five Year Outcome of Lentiviral Gene Therapy for Human Beta-Thalassemia, Lessons and Prospects von Leboulch, Philippe

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Is normal hematopoiesis maintained solely by long-term multipotent stem cells? von Cavazzana-Calvo, Marina, Fischer, Alain, Bushman, Frederic D., Payen, Emmanuel, Hacein-Bey-Abina, Salima, Leboulch, Philippe

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Primed for take-off von Leboulch, Philippe

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Gene therapy: primed for take-off von Leboulch, Philippe

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Bench to Bedside-Gene Therapy for Thalassemia and Sickle Cell Disease von Leboulch, Philippe

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Deficiency of the Cytoskeletal Protein SPECC1L Leads to Oblique Facial Clefting von Saadi, Irfan, Alkuraya, Fowzan S., Gisselbrecht, Stephen S., Goessling, Wolfram, Cavallesco, Resy, Turbe-Doan, Annick, Petrin, Aline L., Harris, James, Siddiqui, Ursela, Grix, Arthur W., Hove, Hanne D., Leboulch, Philippe, Glover, Thomas W., Morton, Cynthia C., Richieri-Costa, Antonio, Murray, Jeffrey C., Erickson, Robert P., Maas, Richard L.

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The LXCXE Retinoblastoma Protein-Binding Motif of FOG-2 Regulates Adipogenesis von Goupille, Olivier, Penglong, Tipparat, Kadri, Zahra, Granger-Locatelli, Marine, Denis, Raphaël, Luquet, Serge, Badoual, Cécile, Fucharoen, Suthat, Maouche-Chrétien, Leila, Leboulch, Philippe, Chrétien, Stany

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Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics von Grosselin, Jeanne, Sii‐Felice, Karine, Payen, Emmanuel, Chretien, Stany, Roux, Diana Tronik‐Le, Leboulch, Philippe

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Phenotypic and Functional Changes Induced in Hematopoietic Stem/Progenitor Cells After Gamma‐Ray Radiation Exposure von Simonnet, Arthur J., Nehmé, Johnny, Vaigot, Pierre, Barroca, Vilma, Leboulch, Philippe, Tronik‐Le Roux, Diana

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Direct binding of pRb/E2F-2 to GATA-1 regulates maturation and terminal cell division during erythropoiesis von Kadri, Zahra, Shimizu, Ritsuko, Ohneda, Osamu, Maouche-Chretien, Leila, Gisselbrecht, Sylvie, Yamamoto, Masayuki, Romeo, Paul-Henri, Leboulch, Philippe, Chretien, Stany

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Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice von Abed, Soumeya, Tubsuwan, Alisa, Chaichompoo, Porntip, Park, In Hyun, Pailleret, Alice, Benyoucef, Aïssa, Tosca, Lucie, De Dreuzy, Edouard, Paulard, Anais, Granger-Locatelli, Marine, Relouzat, Francis, Prost, Stéphane, Tachdjian, Gerard, Fucharoen, Suthat, Daley, George Q, Payen, Emmanuel, Chrétien, Stany, Leboulch, Philippe, Maouche-Chrétien, Leïla

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