Optimization of a Class of Dihydrobenzofurane Analogs toward Orally Efficacious YAP‐TEAD Protein‐Protein Interaction Inhibitors von Sellner, Holger, Chapeau, Emilie, Furet, Pascal, Voegtle, Markus, Salem, Bahaa, Le Douget, Mickaël, Bordas, Vincent, Groell, Jean‐Marc, Le Goff, Anne‐Laure, Rouzet, Christine, Wietlisbach, Thomas, Zimmermann, Thomas, McKenna, Joseph, Brocklehurst, Cara E., Chène, Patrick, Wartmann, Markus, Scheufler, Clemens, Kallen, Joerg, Williams, Gareth, Harlfinger, Stephanie, Traebert, Martin, Dumotier, Bérengère M., Schmelzle, Tobias, Soldermann, Nicolas

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Assessment of the validity and reliability of the 32-item Motor Function Measure in individuals with Type 2 or non-ambulant Type 3 spinal muscular atrophy von Trundell, Dylan, Le Scouiller, Stephanie, Le Goff, Laure, Gorni, Ksenija, Vuillerot, Carole

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Use of MFM-20 to monitor SMA types 1 and 2 patients treated with nusinersen von Le Goff, Laure, Seferian, Andreea, Phelep, Aurelie, Rippert, Pascal, Mathieu, Marie-Laure, Cances, Claude, de Lattre, Capucine, Durigneux, Julien, Gousse, Gaelle, Vincent-Genod, Dominique, Ribault, Shams, Gomez Garcia de la Banda, Marta, Quijano-Roy, Susana, Sarret, Catherine, Servais, Laurent, Vuillerot, Carole

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Psychometric Characteristics of the Motor Function Measure in Neuromuscular Diseases: A Systematic Review von Ribault, Shams, Rippert, Pascal, Jain, Minal, Laure Le Goff, Genod, Dominique Vincent, Barriere, Aurélie, Berruyer, Anne, Garde, Camille, Tinat, Marie, Pons, Christelle, Vuillerot, Carole

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Responsiveness and Minimal Clinically Important Difference of the Motor Function Measure in Collagen VI-Related Dystrophies and Laminin Alpha2-Related Muscular Dystrophy von Le Goff, Laure, Meilleur, Katherine G., Norato, Gina, Rippert, Pascal, Jain, Minal, Fink, Margaret, Foley, A. Reghan, Waite, Melissa, Donkervoort, Sandra, Bönnemann, Carsten G., Vuillerot, Carole

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Correction to: Use of MFM-20 to monitor SMA types 1 and 2 patients treated with nusinersen von Le Goff, Laure, Seferian, Andreea, Phelep, Aurelie, Rippert, Pascal, Mathieu, Marie-Laure, Cances, Claude, de Lattre, Capucine, Durigneux, Julien, Gousse, Gaelle, Vincent-Genod, Dominique, Ribault, Shams, Gómez García de la Banda, Marta, Quijano-Roy, Susana, Sarret, Catherine, Servais, Laurent, Vuillerot, Carole

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Severe congenital myasthenic syndromes caused by agrin mutations affecting secretion by motoneurons von Jacquier, Arnaud, Risson, Valérie, Simonet, Thomas, Roussange, Florine, Lacoste, Nicolas, Ribault, Shams, Carras, Julien, Theuriet, Julian, Girard, Emmanuelle, Grosjean, Isabelle, Le Goff, Laure, Kröger, Stephan, Meltoranta, Julia, Bauché, Stéphanie, Sternberg, Damien, Fournier, Emmanuel, Kostera-Pruszczyk, Anna, O’Connor, Emily, Eymard, Bruno, Lochmüller, Hanns, Martinat, Cécile, Schaeffer, Laurent

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Scoring People With Spinal Muscular Atrophy on the Motor Function Measure Using the Microsoft Kinect von Vincent-Genod, Dominique, Rippert, Pascal, Coton, Justine, Le Goff, Laure, Barriere, Aurélie, Berruyer, Anne, Bernard, Marjorie, Garde, Camille, Gutierrez-Garcia, Marta, Gilabert, Stéphanie, Gomes-Lisboade-Souza, Adriana, Daron, Aurore, Servais, Laurent, Thomann, Guillaume, Vuillerot, Carole

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Real-world multidisciplinary outcomes of onasemnogene abeparvovec monotherapy in patients with spinal muscular atrophy type 1: experience of the French cohort in the first three ye... von Desguerre, Isabelle, Barrois, Rémi, Audic, Frédérique, Barnerias, Christine, Chabrol, Brigitte, Davion, Jean Baptiste, Durigneux, Julien, Espil-Taris, Caroline, Gomez-Garcia de la Banda, Marta, Guichard, Marine, Isapof, Arnaud, Nougues, Marie Christine, Laugel, Vincent, Le Goff, Laure, Mercier, Sandra, Pervillé, Anne, Richelme, Christian, Thibaud, Marie, Sarret, Catherine, Schweitzer, Cyril, Testard, Hervé, Trommsdorff, Valérie, Vanhulle, Catherine, Walther-Louvier, Ulrike, Altuzarra, Cécilia, Chouchane, Mondher, Ropars, Juliette, Quijano-Roy, Susana, Cances, Claude

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Scoring People With Spinal Muscular Atrophy on the Motor Function Measure Using the Microsoft Kinect von Vincent-Genod, Dominique, Rippert, Pascal, Coton, Justine, Le Goff, Laure, Barriere, Aurélie, Berruyer, Anne, Bernard, Marjorie, Garde, Camille, Gutierrez-Garcia, Marta, Gilabert, Stéphanie, Gomes-Lisboade-Souza, Adriana, Daron, Aurore, Servais, Laurent, Thomann, Guillaume, Vuillerot, Carole

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Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study von Chiriboga, Claudia A., Bruno, Claudio, Duong, Tina, Fischer, Dirk, Mercuri, Eugenio, Kirschner, Janbernd, Kostera-Pruszczyk, Anna, Jaber, Birgit, Gorni, Ksenija, Kletzl, Heidemarie, Carruthers, Imogen, Martin, Carmen, Warren, Francis, Scalco, Renata S., Wagner, Kathryn R., Muntoni, Francesco

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Psychometric Characteristics of the Motor Function Measure in Neuromuscular Diseases: A Systematic Review1 von Ribault, Shams, Rippert, Pascal, Jain, Minal, Le Goff, Laure, Genod, Dominique Vincent, Barriere, Aurélie, Berruyer, Anne, Garde, Camille, Tinat, Marie, Pons, Christelle, Vuillerot, Carole

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Assessment of the validity and reliability of the 32-item Motor Function Measure in individuals with Type 2 or non-ambulant Type 3 spinal muscular atrophy von Dylan Trundell, Stephanie Le Scouiller, Laure Le Goff, Ksenija Gorni, Carole Vuillerot, Andrea Martinuzzi

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Correction to: Risdiplam in Patients Previously Treated with Other Therapies for Spinal Muscular Atrophy: An Interim Analysis from the JEWELFISH Study von Chiriboga, Claudia A., Bruno, Claudio, Duong, Tina, Fischer, Dirk, Mercuri, Eugenio, Kirschner, Janbernd, Kostera-Pruszczyk, Anna, Jaber, Birgit, Gorni, Ksenija, Kletzl, Heidemarie, Carruthers, Imogen, Martin, Carmen, Warren, Francis, Scalco, Renata S., Wagner, Kathryn R., Muntoni, Francesco

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Psychometric Characteristics of the Motor Function Measure in Neuromuscular Diseases: A Systematic Review 1 von Ribault, Shams, Rippert, Pascal, Jain, Minal, Le Goff, Laure, Genod, Dominique Vincent, Barriere, Aurélie, Berruyer, Anne, Garde, Camille, Tinat, Marie, Pons, Christelle, Vuillerot, Carole

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COVID‐19–Related IgA Vasculitis von Allez, Matthieu, Denis, Blandine, Bouaziz, Jean‐David, Battistella, Maxime, Zagdanski, Anne‐Marie, Bayart, Jules, Lazaridou, Ingrid, Gatey, Caroline, Pillebout, Evangeline, Chaix Baudier, Marie‐Laure, Delaugerre, Constance, Molina, Jean‐Michel, Le Goff, Jérôme

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Prevention of SARS-CoV-2 transmission during a large, live, indoor gathering (SPRING): a non-inferiority, randomised, controlled trial von Delaugerre, Constance, Foissac, Frantz, Abdoul, Hendy, Masson, Guillaume, Choupeaux, Laure, Dufour, Eric, Gastli, Nabil, Delarue, Severine Mercier, Néré, Marie Laure, Minier, Marine, Gabassi, Audrey, Salmona, Maud, Seguineau, Malika, Schmitt, Sarah, Tonglet, Sébastien, Olivier, Alexis, Poyart, Claire, Le Goff, Jerôme, Lescure, Xavier, Kernéis, Solen, Tréluyer, Jean-Marc

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Baseline circulating tumour DNA and total metabolic tumour volume as early outcome predictors in aggressive large B‐cell lymphoma. A real‐world 112‐patient cohort von Le Goff, Enora, Blanc‐Durand, Paul, Roulin, Louise, Lafont, Charlotte, Loyaux, Romain, MBoumbae, Diana‐Laure, Benmaad, Ichrafe, Claudel, Alexis, Poullot, Elsa, Robe, Cyrielle, Gricourt, Guillaume, Aissat, Abdelrazak, Copie‐Bergman, Christiane, Lemonnier, François, Gaulard, Philippe, Itti, Emmanuel, Haioun, Corinne, Delfau‐Larue, Marie‐Helene

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Evaluation of the COVID-19 IgG/IgM Rapid Test from Orient Gene Biotech von Dellière, Sarah, Salmona, Maud, Minier, Marine, Gabassi, Audrey, Alanio, Alexandre, Le Goff, Jérôme, Delaugerre, Constance, Chaix, Marie-Laure

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White matter tracts lesions and decline of verbal fluency after deep brain stimulation in Parkinson's disease von Costentin, Guillaume, Derrey, Stéphane, Gérardin, Emmanuel, Cruypeninck, Yohann, Pressat‐Laffouilhere, Thibaut, Anouar, Youssef, Wallon, David, Le Goff, Floriane, Welter, Marie‐Laure, Maltête, David

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