Anti-Cas9 immunity: A formidable challenge for muscle genome editing von Lagor, William R.

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Targeting AAV vectors to the central nervous system by engineering capsid-receptor interactions that enable crossing of the blood-brain barrier von Huang, Qin, Chen, Albert T, Chan, Ken Y, Sorensen, Hikari, Barry, Andrew J, Azari, Bahar, Zheng, Qingxia, Beddow, Thomas, Zhao, Binhui, Tobey, Isabelle G, Moncada-Reid, Cynthia, Eid, Fatma-Elzahraa, Walkey, Christopher J, Ljungberg, M Cecilia, Lagor, William R, Heaney, Jason D, Chan, Yujia A, Deverman, Benjamin E

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Less is more: Allele-specific removal of dysfunctional RYR1 channel subunits von Sun, Derek, Lagor, William R.

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Adeno-Associated virus 8 delivers an immunomodulatory peptide to mouse liver more efficiently than to rat liver von Wang, Yuqing, Hurley, Ayrea, De Giorgi, Marco, Tanner, Mark R, Hu, Rong-Chi, Pennington, Michael W, Lagor, William R, Beeton, Christine

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Liver directed adeno‐associated viral vectors to treat metabolic disease von Chuecos, Marcel A., Lagor, William R.

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AAV-CRISPR Gene Editing Is Negated by Pre-existing Immunity to Cas9 von Li, Ang, Tanner, Mark R., Lee, Ciaran M., Hurley, Ayrea E., De Giorgi, Marco, Jarrett, Kelsey E., Davis, Timothy H., Doerfler, Alexandria M., Bao, Gang, Beeton, Christine, Lagor, William R.

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Treating Cardiovascular Disease with Liver Genome Engineering von Hurley, Ayrea, Lagor, William R.

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TAp63 contributes to sexual dimorphism in POMC neuron functions and energy homeostasis von Wang, Chunmei, He, Yanlin, Xu, Pingwen, Yang, Yongjie, Saito, Kenji, Xia, Yan, Yan, Xiaofeng, Hinton Jr, Antentor, Yan, Chunling, Ding, Hongfang, Yu, Likai, Shu, Gang, Gupta, Rajat, Wu, Qi, Tong, Qingchun, Lagor, William R., Flores, Elsa R., Xu, Yong

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Somatic Editing of Ldlr With Adeno-Associated Viral-CRISPR Is an Efficient Tool for Atherosclerosis Research von Jarrett, Kelsey E, Lee, Ciaran, De Giorgi, Marco, Hurley, Ayrea, Gillard, Baiba K, Doerfler, Alexandria M, Li, Ang, Pownall, Henry J, Bao, Gang, Lagor, William R

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CRISPR/Cas9: at the cutting edge of hepatology von Pankowicz, Francis P, Jarrett, Kelsey E, Lagor, William R, Bissig, Karl-Dimiter

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A Self-Deleting AAV-CRISPR System for In Vivo Genome Editing von Li, Ang, Lee, Ciaran M, Hurley, Ayrea E, Jarrett, Kelsey E, De Giorgi, Marco, Lu, Weiqi, Balderrama, Karol S, Doerfler, Alexandria M, Deshmukh, Harshavardhan, Ray, Anirban, Bao, Gang, Lagor, William R

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TFEB regulates murine liver cell fate during development and regeneration von Pastore, Nunzia, Huynh, Tuong, Herz, Niculin J., Calcagni’, Alessia, Klisch, Tiemo J., Brunetti, Lorenzo, Kim, Kangho Ho, De Giorgi, Marco, Hurley, Ayrea, Carissimo, Annamaria, Mutarelli, Margherita, Aleksieva, Niya, D’Orsi, Luca, Lagor, William R., Moore, David D., Settembre, Carmine, Finegold, Milton J., Forbes, Stuart J., Ballabio, Andrea

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In Vivo Ryr2 Editing Corrects Catecholaminergic Polymorphic Ventricular Tachycardia von Pan, Xiaolu, Philippen, Leonne, Lahiri, Satadru K, Lee, Ciaran, Park, So Hyun, Word, Tarah A, Li, Na, Jarrett, Kelsey E, Gupta, Rajat, Reynolds, Julia O, Lin, Jean, Bao, Gang, Lagor, William R, Wehrens, Xander H.T

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Simple improvements in vector design afford substantial gains in AAV delivery of aggregation-slowing Aβ variants von Borgenheimer, Ella, Trueblood, Cameron, Nguyen, Bryan L., Lagor, William R., Jankowsky, Joanna L.

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A chemical chaperone improves muscle function in mice with a RyR1 mutation von Lee, Chang Seok, Hanna, Amy D., Wang, Hui, Dagnino-Acosta, Adan, Joshi, Aditya D., Knoblauch, Mark, Xia, Yan, Georgiou, Dimitra K., Xu, Jianjun, Long, Cheng, Amano, Hisayuki, Reynolds, Corey, Dong, Keke, Martin, John C., Lagor, William R., Rodney, George G., Sahin, Ergun, Sewry, Caroline, Hamilton, Susan L.

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AAV5 delivery of CRISPR-Cas9 supports effective genome editing in mouse lung airway von Liang, Shun-Qing, Walkey, Christopher J., Martinez, Alexa E., Su, Qin, Dickinson, Mary E., Wang, Dan, Lagor, William R., Heaney, Jason D., Gao, Guangping, Xue, Wen

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Temporospatial regulation of intraflagellar transport is required for the endochondral ossification in mice von Yamaguchi, Hiroyuki, Kitami, Megumi, Uchima Koecklin, Karin H., He, Li, Wang, Jianbo, Lagor, William R., Perrien, Daniel S., Komatsu, Yoshihiro

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Atrial-Specific Gene Delivery Using an Adeno-Associated Viral Vector von Ni, Li, Scott, Larry, Campbell, Hannah M, Pan, Xiaolu, Alsina, Katherina M, Reynolds, Julia, Philippen, Leonne E, Hulsurkar, Mohit, Lagor, William R, Li, Na, Wehrens, Xander H.T

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Depletion of Endothelial Prolyl Hydroxylase Domain Protein 2 and 3 Promotes Cardiomyocyte Proliferation and Prevents Ventricular Failure Induced by Myocardial Infarction von Fan, Qiying, Mao, Hua, Angelini, Aude, Coarfa, Cristian, Robertson, Matthew J, Lagor, William R, Wehrens, Xander H.T, Martin, James F, Pi, Xinchun, Xie, Liang

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Proteomic Analysis of Defined HDL Subpopulations Reveals Particle-Specific Protein Clusters: Relevance to Antioxidative Function von Davidson, W Sean, Silva, R A. Gangani D, Chantepie, Sandrine, Lagor, William R, Chapman, M John, Kontush, Anatol

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