Effects of miglustat therapy on neurological disorder and survival in early-infantile Niemann-Pick disease type C: A national French retrospective study von Freihuber, Cecile, Dahmani, Bahia, Brassier, Anais, Broue, Pierre, Cances, Claude, Chabrol, Brigitte, Eyer, Didier, Labarthe, Fancois, Latour, Philippe, Levade, Thierry, Pichard, Samia, Sevin, Caroline, Vanier, Marie Therese, Heron, Benedicte

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