Postnatal genome editing partially restores dystrophin expression in a mouse model of muscular dystrophy von Long, Chengzu, Amoasii, Leonela, Mireault, Alex A., McAnally, John R., Li, Hui, Sanchez-Ortiz, Efrain, Bhattacharyya, Samadrita, Shelton, John M., Bassel-Duby, Rhonda, Olson, Eric N.

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Generation of a Hutchinson-Gilford progeria syndrome monkey model by base editing von Wang, Fang, Zhang, Weiqi, Yang, Qiaoyan, Kang, Yu, Fan, Yanling, Wei, Jingkuan, Liu, Zunpeng, Dai, Shaoxing, Li, Hao, Li, Zifan, Xu, Lizhu, Chu, Chu, Qu, Jing, Si, Chenyang, Ji, Weizhi, Liu, Guang-Hui, Long, Chengzu, Niu, Yuyu

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A Pseudomonas syringae effector inactivates MAPKs to suppress PAMP-induced immunity in plants von Zhang, Jie, Shao, Feng, Li, Yan, Cui, Haitao, Chen, Linjie, Li, Hongtao, Zou, Yan, Long, Chengzu, Lan, Lefu, Chai, Jijie, Chen, She, Tang, Xiaoyan, Zhou, Jian-Min

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Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing von Long, Chengzu, Li, Hui, Tiburcy, Malte, Rodriguez-Caycedo, Cristina, Kyrychenko, Viktoriia, Zhou, Huanyu, Zhang, Yu, Min, Yi-Li, Shelton, John M, Mammen, Pradeep P A, Liaw, Norman Y, Zimmermann, Wolfram-Hubertus, Bassel-Duby, Rhonda, Schneider, Jay W, Olson, Eric N

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Functional correction of dystrophin actin binding domain mutations by genome editing von Kyrychenko, Viktoriia, Kyrychenko, Sergii, Tiburcy, Malte, Shelton, John M, Long, Chengzu, Schneider, Jay W, Zimmermann, Wolfram-Hubertus, Bassel-Duby, Rhonda, Olson, Eric N

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Setting the pace of the Neurospora circadian clock by multiple independent FRQ phosphorylation events von Tang, Chi-Tai, Li, Shaojie, Long, Chengzu, Cha, Joonseok, Huang, Guocun, Li, Lily, Chen, She, Liu, Yi

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Ataxia and Purkinje cell degeneration in mice lacking the CAMTA1 transcription factor von Long, Chengzu, Grueter, Chad E., Song, Kunhua, Qin, Song, Qi, Xiaoxia, Kong, Y. Megan, Shelton, John M., Richardson, James A., Zhang, Chun-Li, Bassel-Duby, Rhonda, Olsona, Eric N.

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Heterogeneous Nuclear Ribonucleoprotein L Is a Subunit of Human KMT3a/Set2 Complex Required for H3 Lys-36 Trimethylation Activity in Vivo von Yuan, Wen, Xie, Jingwei, Long, Chengzu, Erdjument-Bromage, Hediye, Ding, Xiaojun, Zheng, Yong, Tempst, Paul, Chen, She, Zhu, Bing, Reinberg, Danny

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bacterial type III effector family uses the papain-like hydrolytic activity to arrest the host cell cycle von Yao, Qing, Cui, Jixin, Zhu, Yongqun, Wang, Guolun, Hu, Liyan, Long, Chengzu, Cao, Ran, Liu, Xinqi, Huang, Niu, Chen, She, Liu, Liping, Shao, Feng

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Progress and challenges in CRISPR-mediated therapeutic genome editing for monogenic diseases von Konishi, Colin T., Long, Chengzu

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Genome Editing of Monogenic Neuromuscular Diseases: A Systematic Review von Long, Chengzu, Amoasii, Leonela, Bassel-Duby, Rhonda, Olson, Eric N

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Progress and challenges in CRISPR-mediated therapeutic genome editing for monogenic diseases von Konishi, Colin T, Long, Chengzu

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KLHL40 deficiency destabilizes thin filament proteins and promotes nemaline myopathy von Garg, Ankit, O'Rourke, Jason, Long, Chengzu, Doering, Jonathan, Ravenscroft, Gianina, Bezprozvannaya, Svetlana, Nelson, Benjamin R, Beetz, Nadine, Li, Lin, Chen, She, Laing, Nigel G, Grange, Robert W, Bassel-Duby, Rhonda, Olson, Eric N

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Structural Insights into the Enzymatic Mechanism of the Pathogenic MAPK Phosphothreonine Lyase von Zhu, Yongqun, Li, Hongtao, Long, Chengzu, Hu, Liyan, Xu, Hao, Liu, Liping, Chen, She, Wang, Da-Cheng, Shao, Feng

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Primate Model Carrying LMNA Mutation Develops Dilated Cardiomyopathy von Luo, Xiang, Jia, Hao, Wang, Fang, Mo, Han, Kang, Yu, Zhang, Ningning, Zhao, Lu, Xu, Lizhu, Yang, Zhengsheng, Yang, Qiaoyan, Chang, Yuan, Li, Shulin, Bian, Ning, Hua, Xiumeng, Cui, Hao, Cao, Yu, Chu, Chu, Zeng, Yuqiang, Chen, Xinglong, Chen, Zhigang, Ji, Weizhi, Long, Chengzu, Song, Jiangping, Niu, Yuyu

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730. Permanent Correction of Diverse Muscular Dystrophy Mutations in Human Cardiomyocytes by Myoediting von Long, Chengzu, Li, Hui, Kyrychenko, Viktoriia, Zhou, Huayu, Bhattacharyya, Samadrita, Rodriguez, Cristina E., Shelton, John M., Mammen, Pradeep, Schneider, Jay, Bassel-Duby, Rhonda, Olson, Eric N.

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ENHANCEMENT OF PREDICTABLE AND TEMPLATE-FREE GENE EDITING BY THE ASSOCIATION OF CAS WITH DNA POLYMERASE von LONG, Chengzu, YANG, Qiaoyan

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ENHANCEMENT OF PREDICTABLE AND TEMPLATE-FREE GENE EDITING BY THE ASSOCIATION OF CAS WITH DNA POLYMERASE von LONG, Chengzu, YANG, Qiaoyan

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ENHANCEMENT OF PREDICTABLE AND TEMPLATE-FREE GENE EDITING BY THE ASSOCIATION OF CAS WITH DNA POLYMERASE von LONG, CHENGZU, YANG, QIAOYAN

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ENHANCEMENT OF PREDICTABLE AND TEMPLATE-FREE GENE EDITING BY THE ASSOCIATION OF CAS WITH DNA POLYMERASE von LONG, Chengzu, YANG, Qiaoyan

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