Quantitative and correlative biodistribution analysis of 89 Zr-labeled mesoporous silica nanoparticles intravenously injected into tumor-bearing mice von Kramer, Larissa, Winter, Gordon, Baur, Benjamin, Kuntz, Andrea J, Kull, Thomas, Solbach, Christoph, Beer, Ambros J, Lindén, Mika

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Quantitative and correlative biodistribution analysis of 89Zr-labeled mesoporous silica nanoparticles intravenously injected into tumor-bearing miceElectronic supplementary informa... von Kramer, Larissa, Winter, Gordon, Baur, Benjamin, Kuntz, Andrea J, Kull, Thomas, Solbach, Christoph, Beer, Ambros J, Lindén, Mika

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Quantitative and correlative biodistribution analysis of 89Zr-labeled mesoporous silica nanoparticles intravenously injected into tumor-bearing mice von Kramer, Larissa, Winter, Gordon, Baur, Benjamin, Kuntz, Andrea J, Kull, Thomas, Solbach, Christoph, Beer, Ambros J, Lindén, Mika

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Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy von Finkel, Richard S, Mercuri, Eugenio, Darras, Basil T, Connolly, Anne M, Kuntz, Nancy L, Kirschner, Janbernd, Chiriboga, Claudia A, Saito, Kayoko, Servais, Laurent, Tizzano, Eduardo, Topaloglu, Haluk, Tulinius, Már, Montes, Jacqueline, Glanzman, Allan M, Bishop, Kathie, Zhong, Z. John, Gheuens, Sarah, Bennett, C. Frank, Schneider, Eugene, Farwell, Wildon, De Vivo, Darryl C

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Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function von Hoffman, Eric P, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Smith, Edward C, Castro, Diana, Mah, Jean K, McDonald, Craig M, Kuntz, Nancy L, Finkel, Richard S, Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Smith, Andrea L, Morgenroth, Lauren P, Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M, Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S, Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M, Clemens, Paula R

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Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial von Guglieri, Michela, Bushby, Kate, McDermott, Michael P, Hart, Kimberly A, Tawil, Rabi, Martens, William B, Herr, Barbara E, McColl, Elaine, Speed, Chris, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michelle, Brown, Mary W, Willis, Tracey, Griggs, Robert C, Straub, Volker, van Ruiten, Henriette, Childs, Anne-Marie, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Maggi, Lorenzo, Baranello, Giovanni, Butterfield, Russell J, Horrocks, I. A, Roper, Helen, Alhaswani, Zoya, Flanigan, Kevin M, Kuntz, Nancy L, Manzur, Adnan, Darras, Basil T, Kang, Peter B, Morrison, Leslie, Krzesniak-Swinarska, Monika, Mah, Jean K, Mongini, Tiziana E, Ricci, Federica, von der Hagen, Maja, Finkel, Richard S, O’Reardon, Kathleen, Wicklund, Matthew, Kumar, Ashutosh, McDonald, Craig M, Han, Jay J, Joyce, Nanette, Henricson, Erik K, Schara-Schmidt, Ulrike, Gangfuss, Andrea, Wilichowski, Ekkehard, Barohn, Richard J, Statland, Jeffrey M, Campbell, Craig, Vita, Giuseppe, Vita, Gian Luca, Howard, James F, Hughes, Imelda, McMillan, Hugh J, Pegoraro, Elena, Bello, Luca, Burnette, W. Bryan, Thangarajh, Mathula, Chang, Taeun

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Functional and structural characterization of allosteric activation of phospholipase Cε by Rap1A von Sieng, Monita, Selvia, Arielle F., Garland-Kuntz, Elisabeth E., Hopkins, Jesse B., Fisher, Isaac J., Marti, Andrea T., Lyon, Angeline M.

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Phase IIa trial in Duchenne muscular dystrophy shows vamorolone is a first-in-class dissociative steroidal anti-inflammatory drug von Conklin, Laurie S., Damsker, Jesse M., Hoffman, Eric P., Jusko, William J., Mavroudis, Panteleimon D., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., Smith, Edward C., Mah, Jean K., Guglieri, Michela, Nevo, Yoram, Kuntz, Nancy, McDonald, Craig M., Tulinius, Mar, Ryan, Monique M., Webster, Richard, Castro, Diana, Finkel, Richard S., Smith, Andrea L., Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, McCall, John M., Hathout, Yetrib, Nagaraju, Kanneboyina, van den Anker, John, Ward, Leanne M., Ahmet, Alexandra, Cornish, Michaelyn R., Clemens, Paula R.

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Inheritance of somatic mutations by animal offspring von Vasquez Kuntz, Kate L, Kitchen, Sheila A, Conn, Trinity L, Vohsen, Samuel A, Chan, Andrea N, Vermeij, Mark J A, Page, Christopher, Marhaver, Kristen L, Baums, Iliana B

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Physician adjudication of angioedema diagnosis codes in a population of patients with heart failure prescribed angiotensin‐converting enzyme inhibitor therapy von Mansi, Elizabeth T., Johnson, Eric S., Thorp, Micah L., Go, Alan S., Lee, Ming‐Sum, Shen, Albert Yuh‐Jer, Park, Ken J., Budzynska, Katarzyna, Markin, Abraham, Sung, Sue Hee, Thompson, Jamie H., Slaughter, Matthew T., Luong, Tiffany Q., An, Jaejin, Reynolds, Kristi, Roblin, Douglas W., Cassidy‐Bushrow, Andrea E., Kuntz, Jennifer L., Schlienger, Raymond G., Behr, Sigrid, Smith, David H.

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Protection with a Third Dose of mRNA Vaccine against SARS-CoV-2 Variants in Frontline Workers von Yoon, Sarang K., Hegmann, Kurt T., Thiese, Matthew S., Burgess, Jefferey L., Ellingson, Katherine, Lutrick, Karen, Olsho, Lauren E.W., Edwards, Laura J., Sokol, Brian, Caban-Martinez, Alberto J., Schaefer-Solle, Natasha, Jones, John M., Tyner, Harmony, Hunt, Angela, Respet, Karley, Gaglani, Manjusha, Dunnigan, Kayan, Rose, Spencer, Naleway, Allison, Groom, Holly, Kuntz, Jennifer, Fowlkes, Ashley L., Thompson, Mark G., Yoo, Young M.

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Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy: A Randomized Controlled Trial von Dang, Utkarsh J, Damsker, Jesse M, Guglieri, Michela, Clemens, Paula R, Perlman, Seth J, Smith, Edward C, Horrocks, Iain, Finkel, Richard S, Mah, Jean K, Deconinck, Nicolas, Goemans, Nathalie M, Haberlová, Jana, Straub, Volker, Mengle-Gaw, Laurel, Schwartz, Benjamin D, Harper, Amy, Shieh, Perry B, De Waele, Liesbeth, Castro, Diana, Yang, Michele L, Ryan, Monique M, McDonald, Craig M, Tulinius, Mar, Webster, Richard I, Mcmillan, Hugh J, Kuntz, Nancy, Rao, Vamshi K, Baranello, Giovanni, Spinty, Stefan, Childs, Anne-Marie, Sbrocchi, Annie M, Selby, Kathryn A, Monduy, Migvis, Nevo, Yoram, Vilchez, Juan J, Nascimento-Osorio, Andres, Niks, Erik H, De Groot, Imelda J M, Katsalouli, Marina, Van Den Anker, John N, Ward, Leanne M, Leinonen, Mika, D'Alessandro, Andrea L, Hoffman, Eric P

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Age at Diagnosis of Autism Spectrum Disorders in Four Regions of Canada von Ouellette-Kuntz, Hélène M.J., Coo, Helen, Lam, Miu, Yu, C.T., Breitenbach, Marlene M., Hennessey, Paula E., Holden, Jeanette J.A., Brown, Hilary K., Noonan, Andrea L., Gauthier, Robert B., Crews, Lori R.

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Efficacy and Safety of Vamorolone Over 48 Weeks in Boys With Duchenne Muscular Dystrophy von Dang, Utkarsh J, Damsker, Jesse M, Guglieri, Michela, Clemens, Paula R, Perlman, Seth J, Smith, Edward C, Horrocks, Iain, Finkel, Richard S, Mah, Jean K, Deconinck, Nicolas, Goemans, Nathalie M, Haberlova, Jana, Straub, Volker, Mengle-Gaw, Laurel, Schwartz, Benjamin D, Harper, Amy, Shieh, Perry B, De Waele, Liesbeth, Castro, Diana, Yang, Michele L, Ryan, Monique M, McDonald, Craig M, Tulinius, Mar, Webster, Richard I, Mcmillan, Hugh J, Kuntz, Nancy, Rao, Vamshi K, Baranello, Giovanni, Spinty, Stefan, Childs, Anne-Marie, Sbrocchi, Annie M, Selby, Kathryn A, Monduy, Migvis, Nevo, Yoram, Vilchez, Juan J, Nascimento-Osorio, Andres, Niks, Erik H, De Groot, Imelda J.M, Katsalouli, Marina, van den Anker, John N, Ward, Leanne M, Leinonen, Mika, D'Alessandro, Andrea L, Hoffman, Eric P

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Association Study of Exon Variants in the NF-κB and TGFβ Pathways Identifies CD40 as a Modifier of Duchenne Muscular Dystrophy von Bello, Luca, Flanigan, Kevin M., Weiss, Robert B., Dunn, Diane M., Swoboda, Kathryn J., Gappmaier, Eduard, Howard, Michael T., Sampson, Jacinda B., Bromberg, Mark B., Butterfield, Russell, Kerr, Lynne, Pestronk, Alan, Florence, Julaine M., Connolly, Anne, Lopate, Glenn, Golumbek, Paul, Schierbecker, Jeanine, Malkus, Betsy, Renna, Renee, Siener, Catherine, Finkel, Richard S., Bonnemann, Carsten G., Medne, Livija, Glanzman, Allan M., Flickinger, Jean, Mendell, Jerry R., King, Wendy M., Lowes, Linda, Alfano, Lindsay, Mathews, Katherine D., Stephan, Carrie, Laubenthal, Karla, Baldwin, Kris, Wong, Brenda, Morehart, Paula, Meyer, Amy, Day, John W., Naughton, Cameron E., Margolis, Marcia, Spitali, Pietro, Aartsma-Rus, Annemieke, Muntoni, Francesco, Zaharieva, Irina, Ferlini, Alessandra, Mercuri, Eugenio, Tuffery-Giraud, Sylvie, Claustres, Mireille, Straub, Volker, Lochmüller, Hanns, Barp, Andrea, Vianello, Sara, Pegoraro, Elena, Punetha, Jaya, Gordish-Dressman, Heather, Giri, Mamta, McDonald, Craig M., Hoffman, Eric P., Cnaan, Avital, Abresch, Richard T., Henricson, Erik K., Morgenroth, Lauren P., Duong, Tina, Chidambaranathan, V. Viswanathan, Biggar, W. Douglas, McAdam, Laura C., Mah, Jean, Tulinius, Mar, Leshner, Robert, Rocha, Carolina Tesi, Thangarajh, Mathula, Kornberg, Andrew, Ryan, Monique, Nevo, Yoram, Dubrovsky, Alberto, Clemens, Paula R., Abdel-Hamid, Hoda, Connolly, Anne M., Teasley, Jean, Bertorini, Tulio E., North, Kathryn, Webster, Richard, Kolski, Hanna, Kuntz, Nancy, Driscoll, Sherilyn, Carlo, Jose, Gorni, Ksenija, Lotze, Timothy, Karachunski, Peter, Bodensteiner, John B.

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Nusinersen versus Sham Control in Later-Onset Spinal Muscular Atrophy von Mercuri, Eugenio, Darras, Basil T, Chiriboga, Claudia A, Day, John W, Campbell, Craig, Connolly, Anne M, Iannaccone, Susan T, Kirschner, Janbernd, Kuntz, Nancy L, Saito, Kayoko, Shieh, Perry B, Tulinius, Már, Mazzone, Elena S, Montes, Jacqueline, Bishop, Kathie M, Yang, Qingqing, Foster, Richard, Gheuens, Sarah, Bennett, C. Frank, Farwell, Wildon, Schneider, Eugene, De Vivo, Darryl C, Finkel, Richard S

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Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial von Mah, Jean K, Clemens, Paula R, Guglieri, Michela, Smith, Edward C, Finkel, Richard S, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Castro, Diana, Kuntz, Nancy L, McDonald, Craig M, Damsker, Jesse M, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Jackowski, Stefan, Stimpson, Georgia, Ridout, Deborah A, Ayyar-Gupta, Vandana, Baranello, Giovanni, Manzur, Adnan Y, Muntoni, Francesco, Gordish-Dressman, Heather, Leinonen, Mika, Ward, Leanne M, Hoffman, Eric P, Dang, Utkarsh J

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Discovery of thiophene inhibitors of polo-like kinase von Emmitte, Kyle A., Andrews, C. Webb, Badiang, Jennifer G., Davis-Ward, Ronda G., Dickson, Hamilton D., Drewry, David H., Emerson, Holly K., Epperly, Andrea H., Hassler, Daniel F., Knick, Victoria B., Kuntz, Kevin W., Lansing, Timothy J., Linn, James A., Mook, Robert A., Nailor, Kristen E., Salovich, James M., Spehar, Glenn M., Cheung, Mui

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Isoprenoid biosynthesis as a target for antibacterial and antiparasitic drugs: phosphonohydroxamic acids as inhibitors of deoxyxylulose phosphate reducto-isomerase von Kuntz, Lionel, Tritsch, Denis, Grosdemange-Billiard, Catherine, Hemmerlin, Andréa, Willem, Audrey, Bach, Thomas J, Rohmer, Michel

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Functional and structural characterization of allosteric activation of phospholipase Cε by Rap1A von Sieng, Monita, Selvia, Arielle F, Garland-Kuntz, Elisabeth E, Hopkins, Jesse B, Fisher, Isaac J, Marti, Andrea T, Lyon, Angeline M

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