Alport syndrome: Proteomic analysis identifies early molecular pathway alterations in Col4a3 knock out mice von Nicolaou, O, Kousios, A, Sokratous, K, Potamiti, L, Koniali, L, Neophytou, G, Papacharalampous, R, Zanti, M, Ioannou, K, Hadjisavvas, A, Stingl, C, Luider, TM, Kyriacou, K

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S844 KDM5 INHIBITION OFFERS A NOVEL THERAPEUTIC STRATEGY FOR THE TREATMENT OF KMT2D MUTANT LYMPHOMAS von Heward, J., Koniali, L., D’Avola, A., Close, K., Yeomans, A., Johnson, P., Okosun, J., Neve, R., Gribben, J., Oppermann, U., Packham, G., Fitzgibbon, J.

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Context base editing for splice correction of IVSI-110 β-thalassemia von Naiisseh, Basma, Papasavva, Panayiota L., Papaioannou, Nikoletta Y., Tomazou, Marios, Koniali, Lola, Felekis, Xenia, Constantinou, Constantina G., Sitarou, Maria, Christou, Soteroula, Kleanthous, Marina, Lederer, Carsten W., Patsali, Petros

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Catching Them Early: Framework Parameters and Progress for Prenatal and Childhood Application of Advanced Therapies von Lederer, Carsten W, Koniali, Lola, Buerki-Thurnherr, Tina, Papasavva, Panayiota L, La Grutta, Stefania, Licari, Amelia, Staud, Frantisek, Bonifazi, Donato, Kleanthous, Marina

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Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by HBBAS3 Gene Addition and Mutation-Specific RNA Interference von Koniali, Lola, Flouri, Christina, Kostopoulou, Markela I., Papaioannou, Nikoletta Y., Papasavva, Panayiota L., Naiisseh, Basma, Stephanou, Coralea, Demetriadou, Anthi, Sitarou, Maria, Christou, Soteroula, Antoniou, Michael N., Kleanthous, Marina, Patsali, Petros, Lederer, Carsten W.

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High-efficiency editing in hematopoietic stem cells and the HUDEP-2 cell line based on in vitro mRNA synthesis von Papaioannou, Nikoletta Y, Patsali, Petros, Naiisseh, Basma, Papasavva, Panayiota L, Koniali, Lola, Kurita, Ryo, Nakamura, Yukio, Christou, Soteroula, Sitarou, Maria, Mussolino, Claudio, Cathomen, Toni, Kleanthous, Marina, Lederer, Carsten W

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Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by IHBBAS3/I Gene Addition and Mutation-Specific RNA Interference von Koniali, Lola, Flouri, Christina, Kostopoulou, Markela I, Papaioannou, Nikoletta Y, Papasavva, Panayiota L, Naiisseh, Basma, Stephanou, Coralea, Demetriadou, Anthi, Sitarou, Maria, Christou, Soteroula, Antoniou, Michael N, Kleanthous, Marina, Patsali, Petros, Lederer, Carsten W

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Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by HBB AS3 Gene Addition and Mutation-Specific RNA Interference von Koniali, Lola, Flouri, Christina, Kostopoulou, Markela I, Papaioannou, Nikoletta Y, Papasavva, Panayiota L, Naiisseh, Basma, Stephanou, Coralea, Demetriadou, Anthi, Sitarou, Maria, Christou, Soteroula, Antoniou, Michael N, Kleanthous, Marina, Patsali, Petros, Lederer, Carsten W

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