A Modified γ-Retrovirus Vector for X-Linked Severe Combined Immunodeficiency von Hacein-Bey-Abina, Salima, Pai, Sung-Yun, Gaspar, H. Bobby, Armant, Myriam, Berry, Charles C, Blanche, Stephane, Bleesing, Jack, Blondeau, Johanna, de Boer, Helen, Buckland, Karen F, Caccavelli, Laure, Cros, Guilhem, De Oliveira, Satiro, Fernández, Karen S, Guo, Dongjing, Harris, Chad E, Hopkins, Gregory, Lehmann, Leslie E, Lim, Annick, London, Wendy B, van der Loo, Johannes C.M, Malani, Nirav, Male, Frances, Malik, Punam, Marinovic, M. Angélica, McNicol, Anne-Marie, Moshous, Despina, Neven, Benedicte, Oleastro, Matías, Picard, Capucine, Ritz, Jerome, Rivat, Christine, Schambach, Axel, Shaw, Kit L, Sherman, Eric A, Silberstein, Leslie E, Six, Emmanuelle, Touzot, Fabien, Tsytsykova, Alla, Xu-Bayford, Jinhua, Baum, Christopher, Bushman, Frederic D, Fischer, Alain, Kohn, Donald B, Filipovich, Alexandra H, Notarangelo, Luigi D, Cavazzana, Marina, Williams, David A, Thrasher, Adrian J

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Preclinical correction of human Fanconi anemia complementation group A bone marrow cells using a safety-modified lentiviral vector von Becker, P S, Taylor, J A, Trobridge, G D, Zhao, X, Beard, B C, Chien, S, Adair, J, Kohn, D B, Wagner, J E, Shimamura, A, Kiem, H-P

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The woodchuck hepatitis virus post-transcriptional regulatory element reduces readthrough transcription from retroviral vectors von HIGASHIMOTO, T, URBINATI, F, PERUMBETI, A, JIANG, G, ZARZUELA, A, CHANG, L.-J, KOHN, D. B, MALIK, P

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Time Course of Bioluminescent Signal in Orthotopic and Heterotopic Brain Tumors in Nude Mice von Burgos, J.S, Rosol, M, Moats, R.A, Khankaldyyan, V, Kohn, D.B, Nelson, M.D, Laug, W.E

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Lack of Expression from a Retroviral Vector After Transduction of Murine Hematopoietic Stem Cells is Associated with Methylation in vivo von Challita, Pia-Maria, Kohn, Donald B.

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HIV-1-derived lentiviral vectors and fetal route of administration on transgene biodistribution and expression in rhesus monkeys von JIMENEZ, D. F, LEE, C. I, O'SHEA, C. E, KOHN, D. B, TARANTAL, A. F

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Immune response to green fluorescent protein : implications for gene therapy von STRIPECKE, R, DEL CARMEN VILLACRES, M, SKELTON, D. C, SATAKE, N, HALENE, S, KOHN, D. B

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Gene therapy for genetic haematological disorders and immunodeficiencies von Kohn, D. B.

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The enhanced green fluorescent protein (eGFP) is minimally immunogenic in C57BL/6 mice von Skelton, D, Satake, N, Kohn, D B

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Improved Expression in Hematopoietic and Lymphoid Cells in Mice After Transplantation of Bone Marrow Transduced With a Modified Retroviral Vector von Halene, Stephanie, Wang, Lijun, Cooper, Robert M., Bockstoce, David C., Robbins, Paul B., Kohn, Donald B.

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Tissue-specific restriction of cyclophilin A-independent HIV-1- and SIV-derived lentiviral vectors von Kahl, C A, Cannon, P M, Oldenburg, J, Tarantal, A F, Kohn, D B

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A clinical trial of retroviral-mediated transfer of a rev-responsive element decoy gene into CD34+ cells from the bone marrow of human immunodeficiency virus-1-infected children von KOHN, D. B, BAUER, G, BRODY, K, FOX, S, HADEN, E, WILSON, K, SALATA, C, DOLAN, C, WETTER, C, AGUILAR-CORDOVA, E, CHURCH, J, RICE, C. R, ROTHSCHILD, J. C, CARBONARO, D. A, VALDEZ, P, HAO, Q.-L, CHEN ZHOU, BAHNER, I, KEARNS, K

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Lentiviral vectors with amplified β cell-specific gene expression von Shaw, K L, Pais, E, Ge, S, Hardee, C, Skelton, D, Hollis, R P, Crooks, G M, Kohn, D B

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Transduction of Pluripotent Human Hematopoietic Stem Cells Demonstrated by Clonal Analysis after Engraftment in Immune-Deficient Mice von Nolta, Jan A., Dao, Mo A., Wells, Susie, Smogorzewska, E. Monika, Kohn, Donald B.

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Occurrence of leukaemia following gene therapy of X-linked SCID von Kohn, Donald B, Sadelain, Michel, Glorioso, Joseph C

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Analysis of Optimal Conditions for Retroviral-Mediated Transduction of Primitive Human Hematopoietic Cells von Nolta, Jan A., Smogorzewska, Elzbieta M., Kohn, Donald B.

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Comparison of Gene Transfer Efficiencies and Gene Expression Levels Achieved with Equine Infectious Anemia Virus- and Human Immunodeficiency Virus Type 1-Derived Lentivirus Vectors von O'Rourke, J P, Newbound, G C, Kohn, D B, Olsen, J C, Bunnell, B A

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Gene therapy for childhood immunological diseases von Kohn, D B

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Sustained human hematopoiesis in immunodeficient mice by cotransplantation of marrow stroma expressing human interleukin-3 : analysis of gene transduction of long-lived progenitors von NOLTA, J. A, HANLEY, M. B, KOHN, D. B

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Gene therapy to inhibit xenoantibody production using lentiviral vectors in non-human primates von FISCHER-LOUGHEED, J. Y, TARANTAL, A. F, SHULKIN, I, MITSUHASHI, N, KOHN, D. B, LEE, C. C. I, KEARNS-IONKER, M

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