The TREAT-NMD DMD Global Database: Analysis of More than 7,000 Duchenne Muscular Dystrophy Mutations von Bladen, Catherine L., Salgado, David, Monges, Soledad, Foncuberta, Maria E., Kekou, Kyriaki, Kosma, Konstantina, Dawkins, Hugh, Lamont, Leanne, Roy, Anna J., Chamova, Teodora, Guergueltcheva, Velina, Chan, Sophelia, Korngut, Lawrence, Campbell, Craig, Dai, Yi, Wang, Jen, Barišić, Nina, Brabec, Petr, Lahdetie, Jaana, Walter, Maggie C., Schreiber-Katz, Olivia, Karcagi, Veronika, Garami, Marta, Viswanathan, Venkatarman, Bayat, Farhad, Buccella, Filippo, Kimura, En, Koeks, Zaïda, van den Bergen, Janneke C., Rodrigues, Miriam, Roxburgh, Richard, Lusakowska, Anna, Kostera-Pruszczyk, Anna, Zimowski, Janusz, Santos, Rosário, Neagu, Elena, Artemieva, Svetlana, Rasic, Vedrana Milic, Vojinovic, Dina, Posada, Manuel, Bloetzer, Clemens, Jeannet, Pierre-Yves, Joncourt, Franziska, Díaz-Manera, Jordi, Gallardo, Eduard, Karaduman, A. Ayşe, Topaloğlu, Haluk, El Sherif, Rasha, Stringer, Angela, Shatillo, Andriy V., Martin, Ann S., Peay, Holly L., Bellgard, Matthew I., Kirschner, Jan, Flanigan, Kevin M., Straub, Volker, Bushby, Kate, Verschuuren, Jan, Aartsma-Rus, Annemieke, Béroud, Christophe, Lochmüller, Hanns

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Longitudinal Assessment of Creatine Kinase, Creatine/Creatinineratio and Myostatin as Monitoring Biomarkers in Becker Muscular Dystrophy von van de Velde, Nienke M., Koeks, Zaïda, Signorelli, Mirko, Verwey, Nisha, Overzier, Maurice, Bakker, Jaap A., Sajeev, Gautam, Signorovitch, James, Ricotti, Valeria, Verschuuren, Jan, Brown, Kristy, Spitali, Pietro, Niks, Erik H.

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Selection Approach to Identify the Optimal Biomarker Using Quantitative Muscle MRI and Functional Assessments in Becker Muscular Dystrophy von van de Velde, Nienke M., Hooijmans, Melissa T., Sardjoe Mishre, Aashley S.D., Keene, Kevin R., Koeks, Zaïda, Veeger, Thom T.J., Alleman, Iris, van Zwet, Erik W., Beenakker, Jan-Willem M., Verschuuren, Jan J.G.M., Kan, Hermien E., Niks, Erik H.

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Tracking disease progression non‐invasively in Duchenne and Becker muscular dystrophies von Spitali, Pietro, Hettne, Kristina, Tsonaka, Roula, Charrout, Mohammed, Bergen, Janneke, Koeks, Zaïda, Kan, Hermien E., Hooijmans, Melissa T., Roos, Andreas, Straub, Volker, Muntoni, Francesco, Al‐Khalili‐Szigyarto, Cristina, Koel‐Simmelink, Marleen J.A., Teunissen, Charlotte E., Lochmüller, Hanns, Niks, Erik H., Aartsma‐Rus, Annemieke

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Value of Global Longitudinal Strain for Identification and Monitoring of Left Ventricular Dysfunction in Becker Muscular Dystrophy von van de Velde, Nienke M., Gegenava, Tea, Koeks, Zaïda, Butcher, Steele C., Roest, Arno Aw, Bax, Jeroen J., Atsma, Douwe E., Spitali, Pietro, Ajmone Marsan, Nina, Niks, Erik H.

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Diffusion‐tensor magnetic resonance imaging captures increased skeletal muscle fibre diameters in Becker muscular dystrophy von Cameron, Donnie, Abbassi‐Daloii, Tooba, Heezen, Laura G.M., Velde, Nienke M., Koeks, Zaïda, Veeger, Thom T.J., Hooijmans, Melissa T., Abdellaoui, Salma, Duinen, Sjoerd G., Verschuuren, Jan J.G.M., Putten, Maaike, Aartsma‐Rus, Annemieke, Raz, Vered, Spitali, Pietro, Niks, Erik H., Kan, Hermien E.

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Decision-Making And Selection Bias in Four Observational Studies on Duchenne and Becker Muscular Dystrophy von Naarding, Karin J., Doorenweerd, Nathalie, Koeks, Zaïda, Hendriksen, Ruben G.F., Chotkan, Kinita A., Krom, Yvonne D., de Groot, Imelda J.M., Straathof, Chiara S., Niks, Erik H., Kan, Hermien E.

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The neurocognitive profile of adults with Becker muscular dystrophy in the Netherlands von Koeks, Zaıda, Hellebrekers, Danique M.J., van de Velde, Nienke M., Alleman, Iris, Spitali, Pietro, van Duyvenvoorde, Hermine A., Verschuuren, Jan J.G.M., Hendriksen, Jos G.M., Niks, Erik H.

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Multi‐parametric MR in Becker muscular dystrophy patients von Hooijmans, Melissa T., Froeling, Martijn, Koeks, Zaida, Verschuuren, Jan J.G.M., Webb, Andrew, Niks, Erik H., Kan, Hermien E.

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Multi-parametric MR in Becker muscular dystrophy patients von Hooijmans, Melissa T, Froeling, Martijn, Koeks, Zaida, Verschuuren, Jan J G M, Webb, Andrew, Niks, Erik H, Kan, Hermien E

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Longitudinal Assessment of Creatine Kinase, Creatine/Creatinine ratio , and Myostatin as Monitoring Biomarkers in Becker Muscular Dystrophy von van de Velde, Nienke M., Koeks, Zaïda, Signorelli, Mirko, Verwey, Nisha, Overzier, Maurice, Bakker, Jaap A., Sajeev, Gautam, Signorovitch, James, Ricotti, Valeria, Verschuuren, Jan, Brown, Kristy, Spitali, Pietro, Niks, Erik H.

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TCTEX1D1 is a genetic modifier of disease progression in Duchenne muscular dystrophy von Spitali, Pietro, Zaharieva, Irina, Bohringer, Stefan, Hiller, Monika, Chaouch, Amina, Roos, Andreas, Scotton, Chiara, Claustres, Mireille, Bello, Luca, McDonald, Craig M, Hoffman, Eric P, Koeks, Zaida, Eka Suchiman, H, Cirak, Sebahattin, Scoto, Mariacristina, Reza, Mojgan, 't Hoen, Peter A C, Niks, Erik H, Tuffery-Giraud, Sylvie, Lochmüller, Hanns, Ferlini, Alessandra, Muntoni, Francesco, Aartsma-Rus, Annemieke

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Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database von Koeks, Zaïda, Bladen, Catherine L., Salgado, David, van Zwet, Erik, Pogoryelova, Oksana, McMacken, Grace, Monges, Soledad, Foncuberta, Maria E., Kekou, Kyriaki, Kosma, Konstantina, Dawkins, Hugh, Lamont, Leanne, Bellgard, Matthew I., Roy, Anna J., Chamova, Teodora, Guergueltcheva, Velina, Chan, Sophelia, Korngut, Lawrence, Campbell, Craig, Dai, Yi, Wang, Jen, Barišić, Nina, Brabec, Petr, Lähdetie, Jaana, Walter, Maggie C., Schreiber-Katz, Olivia, Karcagi, Veronika, Garami, Marta, Herczegfalvi, Agnes, Viswanathan, Venkatarman, Bayat, Farhad, Buccella, Filippo, Ferlini, Alessandra, Kimura, En, van den Bergen, Janneke C., Rodrigues, Miriam, Roxburgh, Richard, Lusakowska, Anna, Kostera-Pruszczyk, Anna, Santos, Rosário, Neagu, Elena, Artemieva, Svetlana, Rasic, Vedrana Milic, Vojinovic, Dina, Posada, Manuel, Bloetzer, Clemens, Klein, Andrea, Díaz-Manera, Jordi, Gallardo, Eduard, Karaduman, A. Ayşe, Oznur, Tunca, Topaloğlu, Haluk, El Sherif, Rasha, Stringer, Angela, Shatillo, Andriy V., Martin, Ann S., Peay, Holly L., Kirschner, Jan, Flanigan, Kevin M., Straub, Volker, Bushby, Kate, Béroud, Christophe, Verschuuren, Jan J., Lochmüller, Hanns

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Clinical Outcomes in Duchenne Muscular Dystrophy: A Study of 5345 Patients from the TREAT-NMD DMD Global Database von Koeks, Zaïda, Bladen, Catherine, Salgado, En, van Zwet, Erik, Pogoryelova, Oksana, Mcmacken, Grace, Monges, Soledad, Foncuberta, Maria, Kekou, Kyriaki, Kosma, Konstantina, Dawkins, Hugh, Lamont, Leanne, Bellgard, Matthew M., Roy, Ann, Chamova, Teodora, Guergueltcheva, Velina, Chan, Sophelia, Korngut, Lawrence, Campbell, Craig, Dai, Yi, Wang, Jen, Barišić, Nina, Brabec, Petr, Lähdetie, Jaana, Walter, Maggie C., Schreiber-Katz, Olivia, Karcagi, Veronika, Garami, Marta, Herczegfalvi, Agnes, Viswanathan, Venkatarman, Bayat, Farhad, Buccella, Filippo, Ferlini, Alessandra, Kimura, En, van den Bergen, Jan, Rodrigues, Miriam, Roxburgh, Richard, Lusakowska, Ann, Kostera-Pruszczyk, Ann, Santos, Rosário, Neagu, Elena, Artemieva, Svetlana, Rasic, Vedrana Milic, Vojinovic, Dina, Posada, Manuel, Bloetzer, Clemens, Klein, Andrea, Díaz-Manera, Jordi, Gallardo, Eduard, Karaduman, A. Ayşe, Oznur, Tunca, Topaloğlu, Haluk, El Sherif, Rasha, Stringer, Angela, Shatillo, Andriy, Martin, Ann, Peay, Holly, Kirschner, Jan, Flanigan, Kevin, Straub, Volker, Bushby, Kate, Béroud, Christophe, Verschuuren, Jan, Lochmuller, Hanns

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Identification of Gene‐Therapy Responsive Blood Biomarkers in mdx Mouse Model von Johansson, Camilla, Boehler, Jessica F., Brown, Kristy J., Koeks, Zaïda, Schrama, Esther J., Velde, Nienke, Verschuuren, Jan J. G. M., Niks, Erik H., Spitali, Pietro, Al‐Khalili Szigyarto, Cristina

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