Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation von Corti, Manuela, Byrne, Barry J., Gessler, Dominic J., Thompson, Grace, Norman, Samantha, Lammers, Jenna, Coleman, Kirsten E., Liberati, Cristina, Elder, Melissa E., Escolar, Maria L., Tuna, Ibrahim S., Mesaros, Clementina, Kleiner, Gary I., Barbouth, Deborah S., Gray-Edwards, Heather L., Clement, Nathalie, Cleaver, Brian D., Gao, Guangping

Volltext

A Review of Non-IgE Immune-Mediated Allergic Disorders of the Gastrointestinal Tract von Pundit, Valishti Artee, Makkoukdji, Nadia, Banegas Carballo, Krisia Maria, Stone, Farrah, Satnarine, Travis, Kuhn, Jessica, Kleiner, Gary I., Gans, Melissa D.

Volltext

Successful Utilization of Costimulatory Blockade in a Refractory Pediatric Autoimmune Enteropathy Patient von Kleiner, Gary I., MD, PhD, FAAAAI, Langshaw, Amber H., MD, Rivera, Edgardo Rivera, MD, Gebbia, Jennifer, ARNP, Rodriguez, Maria, RN, Simon, Nancy, PharmD

Volltext

Successful Utilization of an Immunosuppressive B Cell Depleting Regimen in an Adolescent Male with Recalcitrant Non-Infectious Colitis and X-Linked Hyper IgM Syndrome von Cino, Vivian E., MSN, ARNP-BC, PNP, Shenderov, Faina, PharmD, Spiro, Joan, PharmD, Reid, Robert, MD, Sigua, Jerome, MD, FAAAAI, Kleiner, Gary I., MD, PhD, FAAAAI

Volltext

A Novel Immunoablative Regimen Utilized In The Successful Remission Of Pulmonary Hemorrhage In An Adolescent Female With Systemic Lupus Erythematosus von Cino, Vivian E., Ms, Constantinescu, Alexander, MD, Deeter, Kristina, MD, Shenderov, Faina, PharmD, Spiro, Joan, PharmD, Kleiner, Gary I., Dr

Volltext

Blood citrulline level is an exclusionary marker for significant acute rejection after intestinal transplantation von DAVID, Andre I, SELVAGGI, Gennaro, WEPPLER, Debbie, ESQUENAZI, Violet, LEVI, David M, KATO, Tomoaki, TZAKIS, Andreas G, RUIZ, Phillip, GAYNOR, Jeffrey J, TRYPHONOPOULOS, Panagiotis, KLEINER, Gary I, MOON, Jang I, NISHIDA, Seigo, PAPPAS, Peter A, CONANAN, Lobelia

Volltext

Allergies, Allergic Comorbidities and the Home Environment in Pediatric Asthma in Southern Florida von Saif, Nadia T, Kleiner, Gary I, Forster, Lourdes Q, Hershorin, Eugene R, Colin, Andrew A, Mirsaeidi, Mehdi, Kumar, Naresh

Volltext

Screening for Wiskott-Aldrich syndrome by flow cytometry von Chiang, Samuel C.C., Vergamini, Sue M., Husami, Ammar, Neumeier, Lisa, Quinn, Kathryn, Ellerhorst, Teresa, Sheppard, Linda, Gifford, Carrie, Buchbinder, David, Joshi, Avni, Ifversen, Marianne, Kleiner, Gary I., Bussel, James B., Chandrakasan, Shanmuganathan, Pesek, Robert D., Pozos, Tamara C., Rose, Melissa J., Scurlock, Amy M., Zhang, Kejian, Bryceson, Yenan T., Bleesing, Jack, Marsh, Rebecca A.

Volltext

Targeted treatments for immune dysregulation in inborn errors of immunity von Makkoukdji, Nadia, Pundit, Valishti, Wyke, Matthew, Giraldo, Jheison, Satnarine, Travis, Kleiner, Gary I., Gans, Melissa

Volltext

Pharmacokinetics, Safety, and Tolerability of Subcutaneous Immune Globulin Injection (Human), 10 % Caprylate/Chromatography Purified (GAMUNEX®-C) in Pediatric Patients with Primary... von Heimall, Jennifer, Chen, Junliang, Church, Joseph A., Griffin, Rhonda, Melamed, Isaac, Kleiner, Gary I.

Volltext

Efficacy and Safety of Ex Vivo Cultured Adult Human Mesenchymal Stem Cells (Prochymal™) in Pediatric Patients with Severe Refractory Acute Graft-Versus-Host Disease in a Compassion... von Prasad, Vinod K, Lucas, Kenneth G, Kleiner, Gary I, Talano, Julie An M, Jacobsohn, David, Broadwater, Gloria, Monroy, Rod, Kurtzberg, Joanne

Volltext

A progressive, fatal dystonia-Parkinsonism syndrome in a patient with primary immunodeficiency receiving chronic IVIG therapy von Papapetropoulos, Spiridon, Friedman, Jennifer, Blackstone, Craig, Kleiner, Gary I., Bowen, Brian C., Singer, Carlos

Volltext

Utilization of dried blood spot citrulline level as a noninvasive method for monitoring graft function following intestinal transplantation von HEE CHUL YU, TUTEJA, Sony, GANDIA, Carlos, WEPPLER, Debbie, ESQUENAZI, Violet, RUIZ, Phillip, MILLER, Joshua, TZAKIS, Andreas G, JANG IL MOON, KLEINER, Gary I, CONANAN, Lobelia, GAYNOR, Jeffrey J, KATO, Tomoaki, LEVI, David M, NISHIDA, Seigo, SELVAGGI, Gennaro

Volltext

Unmasking of acquired autoimmune C1-inhibitor deficiency by an angiotensin-converting enzyme inhibitor von Kleiner, Gary I., Giclas, Patricia, Stadtmauer, Gary, Cunningham-Rundles, Charlotte

Volltext

Combined immunodeficiency in the United States and Kuwait: Comparison of patients' characteristics and molecular diagnosis von Al-Herz, Waleed, Notarangelo, Luigi D, Sadek, Ali, Buckley, Rebecca

Volltext

A murine model of IgE-mediated cow’s milk hypersensitivity von Li, Xiu-min, Schofield, Brian H., Huang, Chih-Kang, Kleiner, Gary I., Sampson, Hugh A.

Volltext

Morbidity, Mortality, and Therapeutics in Combined Immunodeficiency: Data From the USIDNET Registry von Durkee-Shock, Jessica, Zhang, Anqing, Liang, Hua, Wright, Hannah, Magnusson, Julieann, Garabedian, Elizabeth, Marsh, Rebecca A., Sullivan, Kathleen E., Keller, Michael D., Puck, Jennifer, Secord, Elizabeth, Akhter, Javeed, Pozos, Tamara, Fuleihan, Ramsay, Chen, Karin, Buckley, Rebecca, Patel, Niraj, Suez, Daniel, Cooper, Megan, Butte, Manish, Bonilla, Francisco, Walkovich, Kelly, Haddad, Elie, Cunningham-Rundles, Charlotte, Kleiner, Gary, Chong, Hey, Ballas, Zuhair, Uygungil, Burcin, Hernandez-Trujillo, Vivian, Secord, Elizabeth A., Hartog, Nicholas, Dorsey, Morna, Shapiro, Ralph, Schuval, Susan, Notarangelo, Luigi, Routes, John, Knight, Adina, Bennett, Nicholas, Khan, Fatima, Walter, Jolan, Seroogy, Christine, Ochs, Hans, Haines, Kathleen, Muskat, Mica, Costa Reis, Patricia, Cheng, Laurence

Volltext

Esophageal obstruction after incomplete removal of a percutaneous endoscopic gastrostomy tube von KLEINER, GARY I, VERGARA, THERESA M

Volltext

Use of Mesenchymal Stem Cells To Treat Pediatric Patients with Severe (Grade III–IV) Acute Graft Versus Host Disease Refractory to Steroid and Other Agents on a Compassionate Use B... von Prasad, Vinod K., Lucas, Kenneth G., Kleiner, Gary I., Talano, July-An M., Jacobsohn, David, Szabolcs, Paul, Monroy, Rod, Kurtzberg, Joanne

Volltext

Unmasking of acquired autoimmune C1-inhibotor deficiency by an angiotensin-converting enzyme inhibitor von Kleiner, Gary I, Giclas, Patricia, Stadtmauer, Gary, Cunningham-Rundles, Charlotte

Volltext