AAVrh10 Vector Corrects Disease Pathology in MPS IIIA Mice and Achieves Widespread Distribution of SGSH in Large Animal Brains von Hocquemiller, Michaël, Hemsley, Kim M., Douglass, Meghan L., Tamang, Sarah J., Neumann, Daniel, King, Barbara M., Beard, Helen, Trim, Paul J., Winner, Leanne K., Lau, Adeline A., Snel, Marten F., Gomila, Cathy, Ausseil, Jérôme, Mei, Xin, Giersch, Laura, Plavsic, Mark, Laufer, Ralph

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Filipin complex‐reactive brain lesions: A cautionary tale von Lau, Adeline A., Trim, Paul J., King, Barbara M., Hassiotis, Sofia, Hung, Ya Hui, Bush, Ashley I., Snel, Marten F., Hemsley, Kim M.

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Synthetic Disaccharide Standards Enable Quantitative Analysis of Stored Heparan Sulfate in MPS IIIA Murine Brain Regions von He, Qi Qi, Trim, Paul J, Lau, Adeline A, King, Barbara M, Hopwood, John J, Hemsley, Kim M, Snel, Marten F, Ferro, Vito

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MUCOPOLYSACCHARIDOSIS II (MPS II) IN A FREE-LIVING KAKA (NESTOR MERIDIONALIS) IN NEW ZEALAND von Jolly, Robert D., Hunter, Stuart A., Alley, Maurice R., King, Barbara M., Lau, Adeline A., Trim, Paul J., Snel, Marten F., Hemsley, Kim M.

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A novel conditional Sgsh knockout mouse model recapitulates phenotypic and neuropathic deficits of Sanfilippo syndrome von Lau, Adeline A., King, Barbara M., Thorsen, Carly L., Hassiotis, Sofia, Beard, Helen, Trim, Paul J., Whyte, Lauren S., Tamang, Sarah J., Duplock, Stephen K., Snel, Marten F., Hopwood, John J., Hemsley, Kim M.

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Characterization of a C57BL/6 congenic mouse strain of mucopolysaccharidosis type IIIA von Crawley, Allison C., Gliddon, Briony L., Auclair, Dyane, Brodie, Suzanne L., Hirte, Craig, King, Barbara M., Fuller, Maria, Hemsley, Kim M., Hopwood, John J.

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Treatment of canine fucosidosis by intracisternal enzyme infusion von Kondagari, Gauthami S., King, Barbara M., Thomson, Peter C., Williamson, Peter, Clements, Peter R., Fuller, Maria, Hemsley, Kim M., Hopwood, John J., Taylor, Rosanne M.

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Enzyme replacement therapy in Mucopolysaccharidosis VI: evidence for immune responses and altered efficacy of treatment in animal models von Brooks, Doug A, King, Barbara M, C. Crawley, Allison, Byers, Sharon, Hopwood, John J

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Neonatal Bone Marrow Transplantation in MPS IIIA Mice von Lau, Adeline A, Shamsani, N. Jannah, Winner, Leanne K., Hassiotis, Sofia, King, Barbara M., Hopwood, John J., Hemsley, Kim M.

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Recombinant caprine 3H-[N-acetylglucosamine-6-sulfatase] and human 3H-[N-acetylgalactosamine-4-sulfatase]: plasma clearance, tissue distribution, and cellular uptake in the rat von Jones, M Z, Brumfield, L K, King, B M, Hopwood, J J, Byers, S

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Enzyme replacement therapy in a feline model of Maroteaux-Lamy syndrome von Crawley, A C, Brooks, D A, Muller, V J, Petersen, B A, Isaac, E L, Bielicki, J, King, B M, Boulter, C D, Moore, A J, Fazzalari, N L, Anson, D S, Byers, S, Hopwood, J J

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Lead in the Placenta, Membranes, and Umbilical Cord in Relation to Pregnancy Outcome in a Lead-Smelter Community von Baghurst, Peter A., Robertson, Evelyn F., Oldfield, Robert K., King, Barbara M., McMichael, Anthony J., Vimpani, Graham V., Wigg, Neil R.

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Immune response to enzyme replacement therapy: clinical signs of hypersensitivity reactions and altered enzyme distribution in a high titre rat model von Brooks, Doug A., Hopwood, John J., King, Barbara M.

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Lead in the Placenta, Membranes, and Umbilical Cord in Relation to Pregnancy Outcome in a Lead-Smelter Community von Baghurst, Peter A., Robertson, Evelyn F., Oldfield, Robert K., King, Barbara M., McMichael, Anthony J., Vimpani, Graham V., Wigg, Neil R.

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Sulfate transport in normal and cystic fibrosis fibroblasts von King, Barbara M., Rozaklis, Tina, Hopwood, John J., Harper, Gregory S.

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Diabetic Microvascular Disease: An Endocrine Society Scientific Statement von Barrett, Eugene J, Liu, Zhenqi, Khamaisi, Mogher, King, George L, Klein, Ronald, Klein, Barbara E K, Hughes, Timothy M, Craft, Suzanne, Freedman, Barry I, Bowden, Donald W, Vinik, Aaron I, Casellini, Carolina M

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Circulating Sphingolipids, Insulin, HOMA-IR, and HOMA-B: The Strong Heart Family Study von Lemaitre, Rozenn N, Yu, Chaoyu, Hoofnagle, Andrew, Hari, Nair, Jensen, Paul N, Fretts, Amanda M, Umans, Jason G, Howard, Barbara V, Sitlani, Colleen M, Siscovick, David S, King, Irena B, Sotoodehnia, Nona, McKnight, Barbara

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Presymptomatic SARS-CoV-2 Infections and Transmission in a Skilled Nursing Facility von Arons, Melissa M, Hatfield, Kelly M, Reddy, Sujan C, Kimball, Anne, James, Allison, Jacobs, Jesica R, Taylor, Joanne, Spicer, Kevin, Bardossy, Ana C, Oakley, Lisa P, Tanwar, Sukarma, Dyal, Jonathan W, Harney, Josh, Chisty, Zeshan, Bell, Jeneita M, Methner, Mark, Paul, Prabasaj, Carlson, Christina M, McLaughlin, Heather P, Thornburg, Natalie, Tong, Suxiang, Tamin, Azaibi, Tao, Ying, Uehara, Anna, Harcourt, Jennifer, Clark, Shauna, Brostrom-Smith, Claire, Page, Libby C, Kay, Meagan, Lewis, James, Montgomery, Patty, Stone, Nimalie D, Clark, Thomas A, Honein, Margaret A, Duchin, Jeffrey S, Jernigan, John A

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Do Online Parenting Programs Create Change?: A Meta-Analysis von Spencer, Chelsea M., Topham, Glade L., King, Erika L.

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Plasma ceramides containing saturated fatty acids are associated with risk of type 2 diabetes von Fretts, Amanda M., Jensen, Paul N., Hoofnagle, Andrew N., McKnight, Barbara, Howard, Barbara V., Umans, Jason, Sitlani, Colleen M., Siscovick, David S., King, Irena B., Djousse, Luc, Sotoodehnia, Nona, Lemaitre, Rozenn N.

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