Australian comparative field study evaluating the activity of recombinant factor VIII Fc fusion protein (Eloctate®) von Kershaw, Geoffrey, Chen, Vivien M., Cai, Nancy, Khoo, Teh‐Liane

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Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1 von O'Mahony, Brian, Dunn, Amy L, Leavitt, Andrew D, Peyvandi, Flora, Ozelo, Margareth C, Mahlangu, Johnny, Peerlinck, Kathelijne, Wang, Jiaan-Der, Lowe, Gillian C, Tan, Chee Wee, Giermasz, Adam, Tran, Huyen, Khoo, Teh-Liane, Cockrell, Erin, Pepperell, Dominic, Chambost, Hervé, López Fernández, Maria Fernanda, Kazmi, Rashid, Majerus, Elaine, Skinner, Mark W, Klamroth, Robert, Quinn, Jennifer, Yu, Hua, Wong, Wing Yen, Robinson, Tara M, Pipe, Steven W

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The presence of F cells with a fetal phenotype in adults with hemoglobinopathies limits the utility of flow cytometry for quantitation of fetomaternal hemorrhage von Othman, Jad, Orellana, Daniel, Chen, Lin Selina, Russell, Megan, Khoo, Teh‐Liane

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Orchestrated Intron Retention Regulates Normal Granulocyte Differentiation von Wong, Justin J.-L., Ritchie, William, Ebner, Olivia A., Selbach, Matthias, Wong, Jason W.H., Huang, Yizhou, Gao, Dadi, Pinello, Natalia, Gonzalez, Maria, Baidya, Kinsha, Thoeng, Annora, Khoo, Teh-Liane, Bailey, Charles G., Holst, Jeff, Rasko, John E.J.

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Emicizumab assay evaluations and results from an Australian field study of emicizumab measurement von Kershaw, Geoffrey, Dix, Caroline, Chen, Vivien M, Cai, Nancy, Khoo, Teh-Liane

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Combination adefovir-lamivudine prevents emergence of adefovir resistance in lamivudine-resistant hepatitis B von Van Der Poorten, David, Prakoso, Emilia, Khoo, Teh-Liane, Ngu, Meng C, McCaughan, Geoffrey W, Strasser, Simone I, Lee, Alice U

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The antiproliferative ELF2 isoform, ELF2B, induces apoptosis in vitro and perturbs early lymphocytic development in vivo von Guan, Fiona H X, Bailey, Charles G, Metierre, Cynthia, O'Young, Patrick, Gao, Dadi, Khoo, Teh Liane, Holst, Jeff, Rasko, John E J

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Valoctocogene Roxaparvovec Gene Therapy for Hemophilia A von Ozelo, Margareth C, Mahlangu, Johnny, Pasi, K. John, Giermasz, Adam, Leavitt, Andrew D, Laffan, Michael, Symington, Emily, Quon, Doris V, Wang, Jiaan-Der, Peerlinck, Kathelijne, Pipe, Steven W, Madan, Bella, Key, Nigel S, Pierce, Glenn F, O’Mahony, Brian, Kaczmarek, Radoslaw, Henshaw, Joshua, Lawal, Adebayo, Jayaram, Kala, Huang, Mei, Yang, Xinqun, Wong, Wing Y, Kim, Benjamin

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A Phase 3 Trial of Luspatercept in Patients with Transfusion-Dependent β-Thalassemia von Cappellini, M. Domenica, Viprakasit, Vip, Taher, Ali T, Georgiev, Pencho, Kuo, Kevin H.M, Coates, Thomas, Voskaridou, Ersi, Liew, Hong-Keng, Pazgal-Kobrowski, Idit, Forni, G.L, Perrotta, Silverio, Khelif, Abderrahim, Lal, Ashutosh, Kattamis, Antonis, Vlachaki, Efthymia, Origa, Raffaella, Aydinok, Yesim, Bejaoui, Mohamed, Ho, P. Joy, Chew, Lee-Ping, Bee, Ping-Chong, Lim, Soo-Min, Lu, Meng-Yao, Tantiworawit, Adisak, Ganeva, Penka, Gercheva, Liana, Shah, Farrukh, Neufeld, Ellis J, Thompson, Alexis, Laadem, Abderrahmane, Shetty, Jeevan K, Zou, Jun, Zhang, Jennie, Miteva, Dimana, Zinger, Tatiana, Linde, Peter G, Sherman, Matthew L, Hermine, Olivier, Porter, John, Piga, Antonio

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Efanesoctocog Alfa Prophylaxis for Patients with Severe Hemophilia A von von Drygalski, Annette, Chowdary, Pratima, Kulkarni, Roshni, Susen, Sophie, Konkle, Barbara A., Oldenburg, Johannes, Matino, Davide, Klamroth, Robert, Weyand, Angela C., Jimenez-Yuste, Victor, Nogami, Keiji, Poloskey, Stacey, Winding, Bent, Willemze, Annemieke, Knobe, Karin

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Two-Year Outcomes of Valoctocogene Roxaparvovec Therapy for Hemophilia A von Mahlangu, Johnny, Kaczmarek, Radoslaw, von Drygalski, Annette, Shapiro, Susan, Chou, Sheng-Chieh, Ozelo, Margareth C., Kenet, Gili, Peyvandi, Flora, Wang, Michael, Madan, Bella, Key, Nigel S., Laffan, Michael, Dunn, Amy L., Mason, Jane, Quon, Doris V., Symington, Emily, Leavitt, Andrew D., Oldenburg, Johannes, Chambost, Hervé, Reding, Mark T., Jayaram, Kala, Yu, Hua, Mahajan, Reena, Chavele, Konstantia-Maria, Reddy, Divya B., Henshaw, Joshua, Robinson, Tara M., Wong, Wing Yen, Pipe, Steven W.

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Management of a rare red cell antibody in pregnancy von Van, Kim Linh, Bruce, Hayley, Dennington, Peta, Hull, Sue, Yin Kwok, Alice Chi, Partridge, James, Ackerman, Lynette, Khoo, Teh-Liane

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Health-Related Quality of Life Following Valoctocogene Roxaparvovec Gene Therapy for Severe Hemophilia A in the Phase 3 Trial GENEr8-1 von O'Mahony, Brian, Mahlangu, Johnny, Peerlinck, Kathelijne, Wang, Jiaan-Der, Lowe, Gillian, Tan, Chee Wee, Giermasz, Adam, Tran, Huyen A, Khoo, Teh-Liane, Cockrell, Erin, Pepperell, Dominic, Chambost, Hervé, López Fernández, María Fernanda, Kazmi, Rashid, Majerus, Elaine, Skinner, Mark W, Klamroth, Robert, Quinn, Jennifer, Yu, Hua, Wong, Wing Yen, Lawal, Adebayo, Robinson, Tara M, Kim, Benjamin

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Intron Retention Coupled with Nonsense-Mediated Decay Determines Protein Expression and Nuclear Morphology in Granulopoiesis von Rasko, John, Wong, Justin, Ritchie, William, Olivia, Ebner, Matthias, Selbach, Wong, Jason WH, Huang, Yizhou, Gao, Dadi, Gonzalez, Maria, Baidya, Kinsha, Theong, Annora, Khoo, Teh-Liane, Bailey, Charles G, Holst, Jeff

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