Randomized trial of bilateral gene therapy injection for m.11778G>A MT-ND4 Leber optic neuropathy von Newman, Nancy J, Yu-Wai-Man, Patrick, Subramanian, Prem S, Moster, Mark L, Wang, An-Guor, Donahue, Sean P, Leroy, Bart P, Carelli, Valerio, Biousse, Valerie, Vignal-Clermont, Catherine, Sergott, Robert C, Sadun, Alfredo A, Rebolleda Fernández, Gema, Chwalisz, Bart K, Banik, Rudrani, Bazin, Fabienne, Roux, Michel, Cox, Eric D, Taiel, Magali, Sahel, José-Alain

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Five-Year Outcomes of Lenadogene Nolparvovec Gene Therapy in Leber Hereditary Optic Neuropathy von Yu-Wai-Man, Patrick, Newman, Nancy J, Biousse, Valérie, Carelli, Valerio, Moster, Mark L, Vignal-Clermont, Catherine, Klopstock, Thomas, Sadun, Alfredo A, Sergott, Robert C, Hage, Rabih, Degli Esposti, Simona, La Morgia, Chiara, Priglinger, Claudia, Karanja, Rustum, Taiel, Magali, Sahel, José-Alain

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Indirect Comparison of Lenadogene Nolparvovec Gene Therapy Versus Natural History in Patients with Leber Hereditary Optic Neuropathy Carrying the m.11778G>A MT-ND4 Mutation von Carelli, Valerio, Newman, Nancy J., Yu-Wai-Man, Patrick, Biousse, Valerie, Moster, Mark L., Subramanian, Prem S., Vignal-Clermont, Catherine, Wang, An-Guor, Donahue, Sean P., Leroy, Bart P., Sergott, Robert C., Klopstock, Thomas, Sadun, Alfredo A., Rebolleda Fernández, Gema, Chwalisz, Bart K., Banik, Rudrani, Girmens, Jean François, La Morgia, Chiara, DeBusk, Adam A., Jurkute, Neringa, Priglinger, Claudia, Karanjia, Rustum, Josse, Constant, Salzmann, Julie, Montestruc, François, Roux, Michel, Taiel, Magali, Sahel, José-Alain

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Five-Year Outcomes of Lenadogene Nolparvovec Gene Therapy in Leber Hereditary Optic Neuropathy von Yu-Wai-Man, Patrick, Newman, Nancy J, Biousse, Valérie, Carelli, Valerio, Moster, Mark L, Vignal-Clermont, Catherine, Klopstock, Thomas, Sadun, Alfredo A, Sergott, Robert C, Hage, Rabih, Degli Esposti, Simona, La Morgia, Chiara, Priglinger, Claudia, Karanja, Rustum, Taiel, Magali, Sahel, José-Alain, Barboni, Piero, Carbonelli, Michele, Di Vito, Lidia, Amore, Giulia, Contin, Manuela, Mohamed, Susan, Silvestri, Sara, Baker Hubbard, George, Hendrick, Andrew M, Dattilo, Michael, Peragallo, Jason H, Hawy, Eman, DuBois, Lindreth, Gibbs, Deborah, Fernandes Filho, Alcides, Dobbs, Jannah, Aung, Andre, Acheson, James, Boston, Hayley, Eleftheriadou, Maria, Gemenetzi, Maria, Leitch-Devlin, Lauren, Tucker, William R, Jurkute, Neringa, Burale, Asma, DeBusk, Adam A, Haller, Julia A, Massini, Maria, SantaMaria, Melissa, Tollis, Heather, Girmens, Jean-François, Plaine, Lise, Khemliche, Wahiba, Catarino, Claudia B, Priglinger, Siegfried, Rudolph, Günther, Thurau, Stephan R, Livonius, Bettina von, Muth, Daniel, Wolf, Armin, Al-Tamami, Jasmina, Pressler, Angelika, Schertler, Cosima, Hildebrandt, Martin, Neuenhahn, Michael, Heilweil, Gad, Tsui, Irena

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