Small impacts on the giant planet Jupiter von Hueso, R., Delcroix, M., Sánchez-Lavega, A., Pedranghelu, S., Kernbauer, G., McKeon, J., Fleckstein, A., Wesley, A., Gómez-Forrellad, J. M., Rojas, J. F., Juaristi, J.

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Small impacts on the giant planet Jupiter von Hueso, R, Delcroix, M, Sánchez-Lavega, A, Pedranghelu, S, Kernbauer, G, McKeon, J, Fleckstein, A, Wesley, A, Gómez-Forrellad, J M, Rojas, J F, Juaristi, J

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Fasting metabolism modulates the interleukin-12/interleukin-10 cytokine axis von Kovarik, Johannes J, Kernbauer, Elisabeth, Hölzl, Markus A, Hofer, Johannes, Gualdoni, Guido A, Schmetterer, Klaus G, Miftari, Fitore, Sobanov, Yury, Meshcheryakova, Anastasia, Mechtcheriakova, Diana, Witzeneder, Nadine, Greiner, Georg, Ohradanova-Repic, Anna, Waidhofer-Söllner, Petra, Säemann, Marcus D, Decker, Thomas, Zlabinger, Gerhard J

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Gene-Replacement Therapy in Spinal Muscular Atrophy Type 1: Long-Term Follow-Up From the Onasemnogene Abeparvovec-xioi Phase 1/2a Clinical Trial (1808) von Mendell, Jerry R., Shell, Richard, Lehman, Kelly J., McColly, Markus, Lowes, Linda P., Alfano, Lindsay N., Miller, Natalie F., Iammarino, Megan A., Church, Kathleen, Ogrinc, Francis G., Ouyang, Haojun, Kernbauer, Elaine, Joshi, Shivani, Sproule, Douglas M., Meriggioli, Matthew, Feltner, Douglas E., Al-Zaidy, Samiah

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One-Time Intrathecal (IT) Administration of AVXS-101 IT Gene-Replacement Therapy for Spinal Muscular Atrophy: Phase 1 Study (STRONG) (2493) von Finkel, Richard S., Day, John W., Darras, Basil T., Kuntz, Nancy L., Connolly, Anne M., Crawford, Thomas, Butterfield, Russell J., Shieh, Perry B., Tennekoon, Gihan, Iannaccone, Susan T., Meriggioli, Matthew, Tauscher-Wisniewski, Sitra, Shoffner, John, Ogrinc, Francis G., Kavanagh, Sarah, Kernbauer, Elaine, Whittle, JoAnn, Sproule, Douglas M., Feltner, Douglas E., Mendell, Jerry R.

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Onasemnogene Abeparvovec-xioi Gene-Replacement Therapy for Spinal Muscular Atrophy Type 1 (SMA1): Phase 3 US Study (STR1VE) Update (1828) von Day, John W., Chiriboga, Claudia A., Crawford, Thomas O., Darras, Basil T., Finkel, Richard S., Connolly, Anne M., Iannaccone, Susan T., Kuntz, Nancy L., Peña, Loren D.M., Shieh, Perry B., Smith, Edward C., Schultz, Meredith, Feltner, Douglas E., Tauscher-Wisniewski, Sitra, Ogrinc, Francis G., Shah, Ankita, Ouyang, Haojun, Macek, Thomas, Kernbauer, Elaine, Sproule, Douglas M., Mendell, Jerry R.

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Onasemnogene Abeparvovec-xioi Gene-Replacement Therapy in Presymptomatic Spinal Muscular Atrophy: SPR1NT Study Update (2384) von Strauss, Kevin A., Farrar, Michelle A., Swoboda, Kathryn J., Saito, Kayoko, Chiriboga, Claudia A., Finkel, Richard S., Iannaccone, Susan T., Krueger, Jena M., Kwon, Jennifer M., McMillan, Hugh J., Servais, Laurent, Mendell, Jerry R., Parsons, Julie, Scoto, Mariacristina, Shieh, Perry B., Zaidman, Craig, Schultz, Meredith, Kernbauer, Elaine, Joshi, Shivani, Ogrinc, Francis G., Kavanagh, Sarah, Feltner, Douglas E., Tauscher-Wisniewski, Sitra, McGill, Bryan E., Sproule, Douglas M., Muntoni, Francesco

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O.40Intrathecal administration of onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 2 (SMA2): phase 1/2a study (STRONG) von Finkel, R., Day, J., Darras, B., Kuntz, N., Connolly, A., Crawford, T., Butterfield, R., Shieh, P., Tennekoon, G., Iannaccone, S., Ogrinc, F., Kavanagh, S., Kernbauer, E., Whittle, J., L'Italien, J., Kaspar, B., Sproule, D., Spector, S., Feltner, D., Mendell, J.

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Intrathecal administration of AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 2 (SMA2): Phase 1/2A study (strong) von Finkel, R.S., Day, J.W., Darras, B.T., Kuntz, N.L., Connolly, A.M., Crawford, T.O., Butterfield, R.J., Shieh, P.B., Tennekoon, G., Iannaccone, S.T., Meriggioli, M., Ogrinc, F.G., Kavanagh, S., Kernbauer, E., Whittle, J., L'Italien, J., Kaspar, B., Sproule, D.M., Spector, S.A., Feltner, D.E., Mendell, J.R.

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S61 Onasemnogene abeparvovec gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): preliminary pulmonary and ventilatory findings from the phase 3 study (STR1VE... von Shell, R, Day, JW, Chiriboga, CA, Crawford, TO, Darras, BT, Finkel, RS, Connolly, AM, Iannaccone, ST, Kuntz, NL, Peña, LDM, Shieh, PB, Smith, EC, Kausar, I, Schultz, M, Feltner, DE, Ogrinc, FG, Macek, TA, Kernbauer, E, L’Italien, J, Sproule, DM, Kaspar, BK, Mendell, JR

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Associations among visual acuity and vision- and health-related quality of life among patients in the multicenter uveitis steroid treatment trial von Frick, Kevin D, Drye, Lea T, Kempen, John H, Dunn, James P, Holland, Gary N, Latkany, Paul, Rao, Narsing A, Sen, H Nida, Sugar, Elizabeth A, Thorne, Jennifer E, Wang, Robert C, Holbrook, Janet T

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P.066 AVXS-101 gene-replacement therapy (GRT) in spinal muscular atrophy type 1 (SMA1): long-term follow-up from the phase 1 clinical trial von Mendell, JR, Lehman, KJ, McColly, M, Lowes, LP, Alfano, LN, Miller, NF, Iammarino, MA, Church, K, Schultz, M, Ogrinc, FG, L’Italien, J, Kernbauer, E, Shah, S, Sproule, DM, Feltner, DE

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B.01 AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 1 (SMA1): pivotal phase 3 study (STR1VE) update von Day, JW, Chiriboga, CA, Crawford, TO, Darras, BT, Finkel, RS, Connolly, AM, Iannaccone, ST, Kuntz, NL, Pena, LD, Schultz, M, Shieh, PB, Smith, EC, Feltner, DE, Ogrinc, FG, Macek, TA, Kernbauer, E, Muehring, LM, L’Italien, J, Sproule, DM, Kaspar, BK, Mendell, JR

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