Significance of Oligomeric and Fibrillar Species in Amyloidosis: Insights into Pathophysiology and Treatment von Koike, Haruki, Iguchi, Yohei, Sahashi, Kentaro, Katsuno, Masahisa

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A rapid and easy-to-use spinal muscular atrophy screening tool based on primers with high specificity and amplification efficiency for SMN1 combined with single-stranded tag hybrid... von Hirano, Masaki, Sahashi, Kentaro, Ichikawa, Yuki, Katsuno, Masahisa, Natsume, Atsushi

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Peripheral SMN restoration is essential for long-term rescue of a severe spinal muscular atrophy mouse model von Hua, Yimin, Sahashi, Kentaro, Rigo, Frank, Hung, Gene, Horev, Guy, Bennett, C. Frank, Krainer, Adrian R.

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Preclinical progression of neurodegenerative diseases von Katsuno, Masahisa, Sahashi, Kentaro, Iguchi, Yohei, Hashizume, Atsushi

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Motor neuron cell-nonautonomous rescue of spinal muscular atrophy phenotypes in mild and severe transgenic mouse models von Hua, Yimin, Liu, Ying Hsiu, Sahashi, Kentaro, Rigo, Frank, Bennett, C Frank, Krainer, Adrian R

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Antisense correction of SMN2 splicing in the CNS rescues necrosis in a type III SMA mouse model von Hua, Yimin, Sahashi, Kentaro, Hung, Gene, Rigo, Frank, Passini, Marco A, Bennett, C Frank, Krainer, Adrian R

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Mid1 is associated with androgen-dependent axonal vulnerability of motor neurons in spinal and bulbar muscular atrophy von Ogura, Yosuke, Sahashi, Kentaro, Hirunagi, Tomoki, Iida, Madoka, Miyata, Takaki, Katsuno, Masahisa

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Neutrophil extracellular traps: from antimicrobial innate immunity to the development of chemotherapy-induced peripheral neuropathy von Koike, Haruki, Iguchi, Yohei, Sahashi, Kentaro, Katsuno, Masahisa

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Src inhibition attenuates polyglutamine-mediated neuromuscular degeneration in spinal and bulbar muscular atrophy von Iida, Madoka, Sahashi, Kentaro, Kondo, Naohide, Nakatsuji, Hideaki, Tohnai, Genki, Tsutsumi, Yutaka, Noda, Seiya, Murakami, Ayuka, Onodera, Kazunari, Okada, Yohei, Nakatochi, Masahiro, Tsukagoshi Okabe, Yuka, Shimizu, Shinobu, Mizuno, Masaaki, Adachi, Hiroaki, Okano, Hideyuki, Sobue, Gen, Katsuno, Masahisa

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Nucleic Acid-Based Therapeutic Approach for Spinal and Bulbar Muscular Atrophy and Related Neurological Disorders von Hirunagi, Tomoki, Sahashi, Kentaro, Meilleur, Katherine G, Katsuno, Masahisa

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Exercise attenuates polyglutamine‐mediated neuromuscular degeneration in a mouse model of spinal and bulbar muscular atrophy von Hirunagi, Tomoki, Nakatsuji, Hideaki, Sahashi, Kentaro, Yamamoto, Mikiyasu, Iida, Madoka, Tohnai, Genki, Kondo, Naohide, Yamada, Shinichiro, Murakami, Ayuka, Noda, Seiya, Adachi, Hiroaki, Sobue, Gen, Katsuno, Masahisa

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Sustained therapeutic benefits by transient reduction of TDP-43 using ENA-modified antisense oligonucleotides in ALS/FTD mice von Takeuchi, Toshihide, Maeta, Kazuhiro, Ding, Xin, Oe, Yukako, Takeda, Akiko, Inoue, Mana, Nagano, Seiichi, Fujihara, Tsuyoshi, Matsuda, Seiji, Ishigaki, Shinsuke, Sahashi, Kentaro, Minakawa, Eiko N., Mochizuki, Hideki, Neya, Masahiro, Sobue, Gen, Nagai, Yoshitaka

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DNA methylation inhibitor attenuates polyglutamine‐induced neurodegeneration by regulating Hes5 von Kondo, Naohide, Tohnai, Genki, Sahashi, Kentaro, Iida, Madoka, Kataoka, Mayumi, Nakatsuji, Hideaki, Tsutsumi, Yutaka, Hashizume, Atsushi, Adachi, Hiroaki, Koike, Haruki, Shinjo, Keiko, Kondo, Yutaka, Sobue, Gen, Katsuno, Masahisa

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BIIB021, a synthetic Hsp90 inhibitor, induces mutant ataxin-1 degradation through the activation of heat shock factor 1 von Ding, Ying, Adachi, Hiroaki, Katsuno, Masahisa, Sahashi, Kentaro, Kondo, Naohide, Iida, Madoka, Tohnai, Genki, Nakatsuji, Hideaki, Sobue, Gen

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Selective suppression of polyglutamine-expanded protein by lipid nanoparticle-delivered siRNA targeting CAG expansions in the mouse CNS von Hirunagi, Tomoki, Sahashi, Kentaro, Tachikawa, Kiyoshi, Leu, Angel I., Nguyen, Michelle, Mukthavaram, Rajesh, Karmali, Priya P., Chivukula, Padmanabh, Tohnai, Genki, Iida, Madoka, Onodera, Kazunari, Ohyama, Manabu, Okada, Yohei, Okano, Hideyuki, Katsuno, Masahisa

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The Japan Registry for Adult Subjects of Spinal Muscular Atrophy (jREACT-SMA): Protocol for a Longitudinal Observational Study von Sahashi, Kentaro, Hashizume, Atsushi, Kuwatsuka, Yachiyo, Chinen, Madoka, Saotome-Nakamura, Ai, Ando, Masahiko, Katsuno, Masahisa

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HMGCR antibody-associated myopathy as a paraneoplastic manifestation of esophageal carcinoma von Tsujikawa, Koyo, Hara, Kazuhiro, Muro, Yoshinao, Nakanishi, Hirotaka, Niwa, Yukiko, Koike, Masahiko, Noda, Seiya, Riku, Yuichi, Sahashi, Kentaro, Atsuta, Naoki, Ito, Mizuki, Shimoyama, Yoshie, Akiyama, Masashi, Katsuno, Masahisa

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Clinicopathological features of graft versus host disease‐associated myositis von Kazuta, Tomoyuki, Murakami, Ayuka, Noda, Seiya, Hirano, Satoko, Kito, Hiroshi, Tsujikawa, Koyo, Nakanishi, Hirotaka, Kimura, Seigo, Sahashi, Kentaro, Koike, Haruki, Katsuno, Masahisa

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Actin-binding protein filamin-A drives tau aggregation and contributes to progressive supranuclear palsy pathology von Tsujikawa, Koyo, Hamanaka, Kohei, Riku, Yuichi, Hattori, Yuki, Hara, Norikazu, Iguchi, Yohei, Ishigaki, Shinsuke, Hashizume, Atsushi, Miyatake, Satoko, Mitsuhashi, Satomi, Miyazaki, Yu, Kataoka, Mayumi, Jiayi, Li, Yasui, Keizo, Kuru, Satoshi, Koike, Haruki, Kobayashi, Kenta, Sahara, Naruhiko, Ozaki, Norio, Yoshida, Mari, Kakita, Akiyoshi, Saito, Yuko, Iwasaki, Yasushi, Miyashita, Akinori, Iwatsubo, Takeshi, Ikeuchi, Takeshi, Miyata, Takaki, Sobue, Gen, Matsumoto, Naomichi, Sahashi, Kentaro, Katsuno, Masahisa

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TSUNAMI: an antisense method to phenocopy splicing-associated diseases in animals von Sahashi, Kentaro, Hua, Yimin, Ling, Karen K Y, Hung, Gene, Rigo, Frank, Horev, Guy, Katsuno, Masahisa, Sobue, Gen, Ko, Chien-Ping, Bennett, C Frank, Krainer, Adrian R

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