Lentivirus Mediated Correction of Artemis-Deficient Severe Combined Immunodeficiency von Punwani, Divya, Kawahara, Misako, Yu, Jason, Sanford, Ukina, Roy, Sushmita, Patel, Kiran, Carbonaro, Denise A, Karlen, Andrea D, Khan, Sara, Cornetta, Kenneth, Rothe, Michael, Schambach, Axel, Kohn, Donald B, Malech, Harry L, McIvor, R Scott, Puck, Jennifer M, Cowan, Morton J

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Comparative dose effectiveness of intravenous and intrathecal AAV9.CB7.hIDS, RGX-121, in mucopolysaccharidosis type II mice von Smith, Miles C., Belur, Lalitha R., Karlen, Andrea D., Erlanson, Olivia, Furcich, Justin, Lund, Troy C., Seelig, Davis, Kitto, Kelley F., Fairbanks, Carolyn A., Kim, Kwi Hye, Buss, Nick, McIvor, R. Scott

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Phenotypic Correction of Murine Mucopolysaccharidosis Type II by Engraftment of Ex Vivo Lentiviral Vector-Transduced Hematopoietic Stem and Progenitor Cells von Smith, Miles C, Belur, Lalitha R, Karlen, Andrea D, Erlanson, Olivia, Podetz-Pedersen, Kelly M, McKenzie, Jessica, Detellis, Jenn, Gagnidze, Khatuna, Parsons, Geoffrey, Robinson, Nicholas, Labarre, Shelby, Shah, Saumil, Furcich, Justin, Lund, Troy C, Tsai, Hsing-Chen, McIvor, R Scott, Bonner, Melissa

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Generation and characterization of an immunodeficient mouse model of mucopolysaccharidosis type II von Smith, Miles C., Belur, Lalitha R., Karlen, Andrea D., Podetz-Pedersen, Kelly, Erlanson, Olivia, Laoharawee, Kanut, Furcich, Justin, Lund, Troy C., You, Yun, Seelig, Davis, Webber, Beau R., McIvor, R. Scott

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Intrathecal or intravenous AAV9-IDUA/RGX-111 at minimal effective dose prevents cardiac, skeletal and neurologic manifestations of murine MPS I von Belur, Lalitha R., Huber, Avery K., Mantone, Hillary, Robertson, Mason, Smith, Miles C., Karlen, Andrea D., Kitto, Kelley F., Ou, Li, Whitley, Chester B., Braunlin, Elizabeth, Furcich, Justin, Lund, Troy C., Seelig, Davis, Fairbanks, Carolyn A., Buss, Nicholas, Kim, Kwi Hye, McIvor, R. Scott

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Role of transgene regulation in ex vivo lentiviral correction of artemis deficiency von Multhaup, Megan M, Podetz-Pedersen, Kelly M, Karlen, Andrea D, Olson, Erik R, Gunther, Roland, Somia, Nikunj V, Blazar, Bruce R, Cowan, Morton J, McIvor, R Scott

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Cytotoxicity Associated with Artemis Overexpression After Lentiviral Vector-Mediated Gene Transfer von MULTHAUP, Megan, KARLEN, Andrea D, SWANSON, Debra L, WILBER, Andrew, SOMIA, Nikunj V, COWAN, Morton J, MCLVOR, R. Scott

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Characterization of the human artemis promoter by heterologous gene expression in vitro and in vivo von Multhaup, Megan M, Gurram, Sweta, Podetz-Pedersen, Kelly M, Karlen, Andrea D, Swanson, Debra L, Somia, Nikunj V, Hackett, Perry B, Cowan, Morton J, McIvor, R Scott

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Comparative effectiveness of intravenous and intrathecal AAV9.CB7.hIDS (RGX-121) in a murine model of mucopolysaccharidosis type II von Smith, Miles C., Belur, Lalitha, Erlanson, Olivia L., Furcich, Justin W., Karlen, Andrea D., Lund, Troy C., Buss, Nicholas, McIvor, R. Scott

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Prevention of Cardiac, Neurologic, and Skeletal Manifestations of Murine MPS I by Either Systemic or CSF-Directed AAV9-IDUA/RGX-111 Administered at Minimal Effective Dose von Belur, Lalitha R., Huber, Avery K., Mantone, Hillary, Robertson, Mason, Smith, Miles C., Karlen, Andrea D., Kitto, Kelley F., Ou, Li, Whitley, Chester B., Braunlin, Elizabeth, Furcich, Justin, Lund, Troy C., Seelig, Davis, Fairbanks, Carolyn A., Buss, Nicholas, Kim, Kwi Hye, McIvor, R. Scott

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Response-adapted omission of radiotherapy and comparison of consolidation chemotherapy in children and adolescents with intermediate-stage and advanced-stage classical Hodgkin lymp... von Mauz-Körholz, Christine, Landman-Parker, Judith, Balwierz, Walentyna, Ammann, Roland A, Anderson, Richard A, Attarbaschi, Andische, Bartelt, Jörg M, Beishuizen, Auke, Boudjemaa, Sabah, Cepelova, Michaela, Claviez, Alexander, Daw, Stephen, Dieckmann, Karin, Fernández-Teijeiro, Ana, Fosså, Alexander, Gattenlöhner, Stefan, Georgi, Thomas, Hjalgrim, Lisa L, Hraskova, Andrea, Karlén, Jonas, Kluge, Regine, Kurch, Lars, Leblanc, Thiery, Mann, Georg, Montravers, Francoise, Pears, Jean, Pelz, Tanja, Rajić, Vladan, Ramsay, Alan D, Stoevesandt, Dietrich, Uyttebroeck, Anne, Vordermark, Dirk, Körholz, Dieter, Hasenclever, Dirk, Wallace, William Hamish

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Response-adapted omission of radiotherapy in children and adolescents with early-stage classical Hodgkin lymphoma and an adequate response to vincristine, etoposide, prednisone, an... von Mauz-Körholz, Christine, Landman-Parker, Judith, Fernández-Teijeiro, Ana, Attarbaschi, Andishe, Balwierz, Walentyna, Bartelt, Jörg M, Beishuizen, Auke, Boudjemaa, Sabah, Cepelova, Michaela, Ceppi, Francesco, Claviez, Alexander, Daw, Stephen, Dieckmann, Karin, Fosså, Alexander, Gattenlöhner, Stefan, Georgi, Thomas, Hjalgrim, Lisa L, Hraskova, Andrea, Karlén, Jonas, Kurch, Lars, Leblanc, Thierry, Mann, Georg, Montravers, Francoise, Pears, Jane, Pelz, Tanja, Rajić, Vladan, Ramsay, Alan D, Stoevesandt, Dietrich, Uyttebroeck, Anne, Vordermark, Dirk, Körholz, Dieter, Hasenclever, Dirk, Wallace, William H, Kluge, Regine

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Response-adapted omission of radiotherapy in children and adolescents with early-stage classical Hodgkin lymphoma and an adequate response to vincristine, etoposide, prednisone, an... von Mauz-Koerholz, Christine, Landman-Parker, Judith, Fernandez-Teijeiro, Ana, Attarbaschi, Andishe, Balwierz, Walentyna, Bartelt, Joerg M, Beishuizen, Auke, Boudjemaa, Sabah, Cepelova, Michaela, Ceppi, Francesco, Claviez, Alexander, Daw, Stephen, Dieckmann, Karin, Fossa, Alexander, Gattenloehner, Stefan, Georgi, Thomas, Hjalgrim, Lisa L, Hraskova, Andrea, Karlen, Jonas, Kurch, Lars, Leblanc, Thierry, Mann, Georg, Montravers, Francoise, Pears, Jane, Pelz, Tanja, Rajic, Vladan, Ramsay, Alan D, Stoevesandt, Dietrich, Uyttebroeck, Anne, Vordermark, Dirk, Koerholz, Dieter, Hasenclever, Dirk, Wallace, William H, Kluge, Regine

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Response-adapted omission of radiotherapy and comparison of consolidation chemotherapy in children and adolescents with intermediate-stage and advanced-stage classical Hodgkin lymp... von Mauz-Koerholz, Christine, Landman-Parker, Judith, Balwierz, Walentyna, Ammann, Roland A, Anderson, Richard A, Attarbaschi, Andische, Bartelt, Jorg M, Beishuizen, Auke, Boudjemaa, Sabah, Cepelova, Michaela, Claviez, Alexander, Daw, Stephen, Dieckmann, Karin, Fernandez-Teijeiro, Ana, Fossa, Alexander, Gattenloehner, Stefan, Georgi, Thomas, Hjalgrim, Lisa L, Hraskova, Andrea, Karlen, Jonas, Kluge, Regine, Kurch, Lars, Leblanc, Thiery, Mann, Georg, Montravers, Francoise, Pears, Jean, Pelz, Tanja, Rajic, Vladan, Ramsay, Alan D, Stoevesandt, Dietrich, Uyttebroeck, Anne, Vordermark, Dirk, Koerholz, Dieter, Hasenclever, Dirk, Wallace, William Hamish

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De literaire manifesten van het fin de siècle in de Zuidnederlandse periodieken 1878-1914 von Vervliet, Raymond

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