In vivo genome editing with a small Cas9 orthologue derived from Campylobacter jejuni von Kim, Eunji, Koo, Taeyoung, Park, Sung Wook, Kim, Daesik, Kim, Kyoungmi, Cho, Hee-Yeon, Song, Dong Woo, Lee, Kyu Jun, Jung, Min Hee, Kim, Seokjoong, Kim, Jin Hyoung, Kim, Jeong Hun, Kim, Jin-Soo

Volltext

Targeted chromosomal duplications and inversions in the human genome using zinc finger nucleases von Lee, Hyung Joo, Kweon, Jiyeon, Kim, Eunji, Kim, Seokjoong, Kim, Jin-Soo

Volltext

Targeted dual base editing with Campylobacter jejuni Cas9 by single AAV-mediated delivery von Kweon, Jiyeon, Jang, An-Hee, Kwon, Eunji, Kim, Ungi, Shin, Ha Rim, See, Jieun, Jang, Gayoung, Lee, Chaeyeon, Koo, Taeyoung, Kim, Seokjoong, Kim, Yongsub

Volltext

In vivo delivery of CRISPR-Cas9 using lipid nanoparticles enables antithrombin gene editing for sustainable hemophilia A and B therapy von Han, Jeong Pil, Kim, MinJeong, Choi, Beom Seok, Lee, Jeong Hyeon, Lee, Geon Seong, Jeong, Michaela, Lee, Yeji, Kim, Eun-Ah, Oh, Hye-Kyung, Go, Nanyeong, Lee, Hyerim, Lee, Kyu Jun, Kim, Un Gi, Lee, Jae Young, Kim, Seokjoong, Chang, Jun, Lee, Hyukjin, Song, Dong Woo, Yeom, Su Cheong

Volltext

Statins suppress cell-to-cell propagation of α-synuclein by lowering cholesterol von Min, Joo-Ok, Ho, Hoang-Anh, Lee, Wonjae, Jung, Byung Chul, Park, Sung Jun, Kim, Seokjoong, Lee, Seung-Jae

Volltext

SUPT4H1-edited stem cell therapy rescues neuronal dysfunction in a mouse model for Huntington’s disease von Park, Hyun Jung, Han, Areum, Kim, Ji Yeon, Choi, Jiwoo, Bae, Hee Sook, Cho, Gyu-bon, Shin, Hyejung, Shin, Eun ji, Lee, Kang-in, Kim, Seokjoong, Lee, Jae Young, Song, Jihwan

Volltext

Mediator Modulates Gli3-Dependent Sonic Hedgehog Signaling von Zhou, Haiying, Kim, Seokjoong, Ishii, Shunsuke, Boyer, Thomas G.

Volltext

Apancreatic pigs cloned using Pdx1-disrupted fibroblasts created via TALEN-mediated mutagenesis von Kang, Jin-Dan, Kim, Hyojin, Jin, Long, Guo, Qing, Cui, Cheng-Du, Li, Wen-Xue, Kim, Seokjoong, Kim, Jin-Soo, Yin, Xi-Jun

Volltext

Efficient and specific generation of knockout mice using Campylobacter jejuni CRISPR/Cas9 system von Lee, Jae Young, Jang, Yoo Jin, Bae, Ji Hyun, Lee, Yoon Hoo, Bae, Hee Sook, Kim, Seokjoong, Park, Sin-Gi, Koo, Ok Jae, Yeom, Su Cheong

Volltext

Genotyping with CRISPR-Cas-derived RNA-guided endonucleases von Kim, Jong Min, Kim, Daesik, Kim, Seokjoong, Kim, Jin-Soo

Volltext

Programmable Nuclease-Based Integration into Novel Extragenic Genomic Safe Harbor Identified from Korean Population-Based CNV Analysis von Lee, Eun-Seo, Moon, Sanghoon, Abu-Bonsrah, Kwaku Dad, Kim, Yun Kyoung, Hwang, Mi Yeong, Kim, Young Jin, Kim, Seokjoong, Hwang, Nathaniel S., Kim, Hyongbum Henry, Kim, Bong-Jo

Volltext

Targeted genome engineering via zinc finger nucleases von Kim, Seokjoong, Kim, Jin-Soo

Volltext

Leakage-aware redundancy for reliable sub-threshold memories von Kim, Seokjoong, Guthaus, Matthew

Volltext

Targeted PMP22 TATA-box editing by CRISPR/Cas9 reduces demyelinating neuropathy of Charcot-Marie-Tooth disease type 1A in mice von Lee, Ji-Su, Lee, Jae Y, Song, Dong W, Bae, Hee S, Doo, Hyun M, Yu, Ho S, Lee, Kyu J, Kim, Hee K, Hwang, Hyun, Kwak, Geon, Kim, Daesik, Kim, Seokjoong, Hong, Young B, Lee, Jung M, Choi, Byung-Ok

Volltext

CRISPR/Cas9-mediated gene knockout screens and target identification via whole-genome sequencing uncover host genes required for picornavirus infection von Kim, Heon Seok, Lee, Kyungjin, Bae, Sangsu, Park, Jeongbin, Lee, Chong-Kyo, Kim, Meehyein, Kim, Eunji, Kim, Minju, Kim, Seokjoong, Kim, Chonsaeng, Kim, Jin-Soo

Volltext

Loss of glucocerebrosidase 1 activity causes lysosomal dysfunction and α-synuclein aggregation von Bae, Eun-Jin, Yang, Na Young, Lee, Cheolsoon, Lee, He-Jin, Kim, Seokjoong, Sardi, Sergio Pablo, Lee, Seung-Jae

Volltext

CRISPR-Cas9-mediated therapeutic editing of Rpe65 ameliorates the disease phenotypes in a mouse model of Leber congenital amaurosis von Jo, Dong Hyun, Song, Dong Woo, Cho, Chang Sik, Kim, Un Gi, Lee, Kyu Jun, Lee, Kihwang, Park, Sung Wook, Kim, Daesik, Kim, Jin Hyoung, Kim, Jin-Soo, Kim, Seokjoong, Kim, Jeong Hun, Lee, Jung Min

Volltext

Tetrameric Oligomerization Mediates Transcriptional Repression by the BRCA1-dependent Kruppel-associated Box-Zinc Finger Protein ZBRK1 von Tan, Wei, Kim, Seokjoong, Boyer, Thomas G.

Volltext

Correction: Corrigendum: Genotyping with CRISPR-Cas-derived RNA-guided endonucleases von Kim, Jong Min, Kim, Daesik, Kim, Seokjoong, Kim, Jin-Soo

Volltext

Proposed Motor Scoring System in a Porcine Model of Parkinson's Disease induced by Chronic Subcutaneous Injection of MPTP von Moon, Joon Ho, Kim, Ji Ho, Im, Hyung-Jun, Lee, Dong Soo, Park, Eun Jung, Song, Kilyoung, Oh, Hyun Ju, Hyun, Su Bin, Kang, Sang Chul, Kim, Hyunil, Moon, Hyo Eun, Park, Hyung Woo, Lee, Hong Jae, Kim, Eun Ji, Kim, Seokjoong, Lee, Byeong Chun, Paek, Sun Ha

Volltext