P1345: IMMUNE RECONSTITUTION AFTER BMT FOR NON‐MALIGNANT HEMATOLOGICAL CONDITIONS FOR RELATED, UNRELATED AND HAPLOIDENTICAL DONORS. A STUDY IN THE PEDIATRIC DEPARTMENT AT ST MARY'S... von Khoder, A., Gassas, A., Bremathas, S., Rabanal, O., Hennesy, K., Loaiza, S., Lund, K., Petterson, T., Karnik, L., Josu de la Fuente, J.

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P1345: IMMUNE RECONSTITUTION AFTER BMT FOR NON-MALIGNANT HEMATOLOGICAL CONDITIONS FOR RELATED, UNRELATED AND HAPLOIDENTICAL DONORS. A STUDY IN THE PEDIATRIC DEPARTMENT AT ST MARY’S... von A. Khoder, A. Gassas, S. Bremathas, O. Rabanal, K. Hennesy, S. Loaiza, K. Lund, T. Petterson, L. Karnik, J. Josu de la Fuente

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Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia von Locatelli, Franco, Lang, Peter, Wall, Donna, Meisel, Roland, Corbacioglu, Selim, Li, Amanda M., de la Fuente, Josu, Shah, Ami J., Carpenter, Ben, Kwiatkowski, Janet L., Mapara, Markus, Liem, Robert I., Cappellini, Maria Domenica, Algeri, Mattia, Kattamis, Antonis, Sheth, Sujit, Grupp, Stephan, Handgretinger, Rupert, Kohli, Puja, Shi, Daoyuan, Ross, Leorah, Bobruff, Yael, Simard, Christopher, Zhang, Lanju, Morrow, Phuong Khanh, Hobbs, William E., Frangoul, Haydar

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CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia von Frangoul, Haydar, Altshuler, David, Cappellini, M. Domenica, Chen, Yi-Shan, Domm, Jennifer, Eustace, Brenda K, Foell, Juergen, de la Fuente, Josu, Grupp, Stephan, Handgretinger, Rupert, Ho, Tony W, Kattamis, Antonis, Kernytsky, Andrew, Lekstrom-Himes, Julie, Li, Amanda M, Locatelli, Franco, Mapara, Markus Y, de Montalembert, Mariane, Rondelli, Damiano, Sharma, Akshay, Sheth, Sujit, Soni, Sandeep, Steinberg, Martin H, Wall, Donna, Yen, Angela, Corbacioglu, Selim

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Azathioprine/hydroxyurea preconditioning prior to nonmyeloablative matched sibling donor hematopoietic stem cell transplantation in adults with sickle cell disease: A prospective o... von Dovern, Elisabeth, Aydin, Mesire, Hazenberg, Mette D., Tang, Man Wai, Suijk, Elisabeth M., Hoogendoorn, Gerianne M., Van Tuijn, Charlotte F. J., Kerkhoffs, Jean‐Louis, Rutten, Caroline E., Zeerleder, Sacha S., Fuente, Josu, Biemond, Bart J., Nur, Erfan

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Similar outcome of upfront‐unrelated and matched sibling stem cell transplantation in idiopathic paediatric aplastic anaemia. A study on behalf of the UK Paediatric BMT Working Par... von Dufour, Carlo, Veys, Paul, Carraro, Elisa, Bhatnagar, Neha, Pillon, Marta, Wynn, Rob, Gibson, Brenda, Vora, Ajay J., Steward, Colin G., Ewins, Anna M., Hough, Rachael E., Fuente, Josu, Velangi, Mark, Amrolia, Persis J., Skinner, Roderick, Bacigalupo, Andrea, Risitano, Antonio M., Socie, Gerard, Peffault de Latour, Regis, Passweg, Jakob, Rovo, Alicia, Tichelli, André, Schrezenmeier, Hubert, Hochsmann, Britta, Bader, Peter, Biezen, Anja, Aljurf, Mahmoud D., Kulasekararaj, Austin, Marsh, Judith C., Samarasinghe, Sujith

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Busulfan-fludarabine- or treosulfan-fludarabine-based conditioning before allogeneic HSCT from matched sibling donors in paediatric patients with sickle cell disease: A study on be... von Cseh, Annamária, Galimard, Jacques-Emmanuel, de la Fuente, Josu, Isgro, Antonella, Zecca, Marco, Garwer, Birgit, Biffi, Alexandra, Aljurf, Mahmoud, Sundin, Mikael, Belendez, Cristina, Locatelli, Franco, Balduzzi, Adriana, Lawson, Sarah, Sengeloev, Henrik, Ifversen, Marianne, Saccardi, Riccardo, Wynn, Robert, Lankester, Arjan C, Corbacioglu, Selim, Peters, Christina

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Exagamglogene Autotemcel for Severe Sickle Cell Disease von Frangoul, Haydar, Locatelli, Franco, Sharma, Akshay, Bhatia, Monica, Mapara, Markus, Molinari, Lyndsay, Wall, Donna, Liem, Robert I., Telfer, Paul, Shah, Ami J., Cavazzana, Marina, Corbacioglu, Selim, Rondelli, Damiano, Meisel, Roland, Dedeken, Laurence, Lobitz, Stephan, de Montalembert, Mariane, Steinberg, Martin H., Walters, Mark C., Eckrich, Michael J., Imren, Suzan, Bower, Laura, Simard, Christopher, Zhou, Weiyu, Xuan, Fengjuan, Morrow, Phuong Khanh, Hobbs, William E., Grupp, Stephan A.

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Real-time national survey of COVID-19 in hemoglobinopathy and rare inherited anemia patients von Telfer, Paul, De la Fuente, Josu, Sohal, Mamta, Brown, Ralph, Eleftheriou, Perla, Roy, Noémi, Piel, Frédéric B, Chakravorty, Subarna, Gardner, Kate, Velangi, Mark, Drasar, Emma, Shah, Farrukh, Porter, John B, Trompeter, Sara, Atoyebi, Wale, Szydlo, Richard, Anie, Kofi A, Ryan, Kate, Sharif, Joseph, Wright, Josh, Astwood, Emma, Nicolle, C Sarah, Webster, Amy, Roberts, David J, Lugthart, Sanne, Kaya, Banu, Awogbade, Moji, Rees, David C, Hollingsworth, Rob, Inusa, Baba, Howard, Jo, Layton, D Mark

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Busulfan–fludarabine- or treosulfan–fludarabine-based myeloablative conditioning for children with thalassemia major von Lüftinger, Roswitha, Zubarovskaya, Natalia, Galimard, Jacques-Emmanuel, Cseh, Annamaria, Salzer, Elisabeth, Locatelli, Franco, Algeri, Mattia, Yesilipek, Akif, de la Fuente, Josu, Isgrò, Antonella, Alseraihy, Amal, Angelucci, Emanuele, Smiers, Frans J., La La Nasa, Giorgia, Zecca, Marco, Fisgin, Tunc, Unal, Emel, Kleinschmidt, Katharina, Peters, Christina, Lankester, Arjan, Corbacioglu, Selim

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Impairment of neutrophil oxidative burst in children with sickle cell disease is associated with heme oxygenase-1 von Evans, Ceri, Orf, Katharine, Horvath, Erzsebet, Levin, Michael, De La Fuente, Josu, Chakravorty, Subarna, Cunnington, Aubrey J

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Special issues related to the diagnosis and management of acquired aplastic anemia in countries with restricted resources, a report on behalf of the Eastern Mediterranean blood and... von Iftikhar, Raheel, Ahmad, Parvez, de Latour, Regis, Dufour, Carlo, Risitano, Antonio, Chaudhri, Naeem, Bazarbachi, Ali, De La Fuente, Josu, Höchsmann, Britta, Osman Ahmed, Syed, Gergis, Usama, Elhaddad, Alaa, Halkes, Constantijn, Albeirouti, Bassim, Alotaibi, Sultan, Kulasekararaj, Austin, Alzahrani, Hazzaa, Ben Othman, Tarek, Cesaro, Simone, Alahmari, Ali, Rihani, Rawad, Alshemmari, Salem, Hamidieh, Amir Ali, Bekadja, Mohamed-Amine, Passweg, Jakob, Al-Khabori, Murtadha, Rasheed, Walid, Bacigalupo, Andrea, Chaudhry, Qamar-Un-Nisa, Ljungman, Per, Marsh, Judith, El Fakih, Riad, Aljurf, Mahmoud

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Haploidentical Allogeneic Stem Cell Transplantation in Sickle Cell Disease: A Systematic Review and Meta-Analysis von Aydin, Mesire, Dovern, Elisabeth, Leeflang, Mariska M.G., de la Fuente, Josu, Kassim, Adetola A., Biemond, Bart J., Nur, Erfan

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Harmonizing definitions for hematopoietic recovery, graft rejection, graft failure, poor graft function, and donor chimerism in allogeneic hematopoietic cell transplantation: a rep... von Sureda, Anna, Carpenter, Paul A., Bacigalupo, Andrea, Bhatt, Vijaya Raj, de la Fuente, Josu, Ho, Aloysius, Kean, Leslie, Lee, Jong Wook, Sánchez-Ortega, Isabel, Savani, Bipin N., Schetelig, Johannes, Stadtmauer, Edward A., Takahashi, Yoshiyuki, Atsuta, Yoshiko, Koreth, John, Kröger, Nicolaus, Ljungman, Per, Okamoto, Shinichiro, Popat, Uday, Soiffer, Robert, Stefanski, Heather E., Kharfan-Dabaja, Mohamed A.

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Macrophage activation syndrome and post‐transplant microangiopathy following haploidentical bone marrow transplantation for sickle cell anemia von Davies, James O. J., Hart, Alice C., De La Fuente, Josu, Bain, Barbara J.

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Dyskeratosis congenita: Advances in the understanding of the telomerase defect and the role of stem cell transplantation von De La Fuente, Josu, Dokal, Inderjeet

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Microchimerism in female bone marrow and bone decades after fetal mesenchymal stem-cell trafficking in pregnancy von O'Donoghue, Keelin, Chan, Jerry, de la Fuente, Josu, Kennea, Nigel, Sandison, Ann, Anderson, Jonathan R, Roberts, Irene AG, Fisk, Nicholas M

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Exome sequencing identifies MPL as a causative gene in familial aplastic anemia von WALNE, Amanda J, DOKAL, Arran, PLAGNOL, Vincent, BESWICK, Richard, KIRWAN, Michael, DE LA FUENTE, Josu, VULLIAMY, Tom, DOKAL, Inderjeet

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Heterogeneous disease-propagating stem cells in juvenile myelomonocytic leukemia von Louka, Eleni, Povinelli, Benjamin, Rodriguez-Meira, Alba, Buck, Gemma, Wen, Wei Xiong, Wang, Guanlin, Sousos, Nikolaos, Ashley, Neil, Hamblin, Angela, Booth, Christopher A G, Roy, Anindita, Elliott, Natalina, Iskander, Deena, de la Fuente, Josu, Fordham, Nicholas, O'Byrne, Sorcha, Inglott, Sarah, Norfo, Ruggiero, Salio, Mariolina, Thongjuea, Supat, Rao, Anupama, Roberts, Irene, Mead, Adam J

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Target enrichment and high‐throughput sequencing of 80 ribosomal protein genes to identify mutations associated with Diamond‐Blackfan anaemia von Gerrard, Gareth, Valgañón, Mikel, Foong, Hui En, Kasperaviciute, Dalia, Iskander, Deena, Game, Laurence, Müller, Michael, Aitman, Timothy J., Roberts, Irene, Fuente, Josu, Foroni, Letizia, Karadimitris, Anastasios

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