Novel AAV-mediated genome editing therapy improves health and survival in a mouse model of methylmalonic acidemia von Zhang, Shengwen, Bastille, Amy, Gordo, Susana, Ramesh, Nikhil, Vora, Jenisha, McCarthy, Elizabeth, Zhang, Xiaohan, Frank, Dylan, Ko, Chih-Wei, Wu, Carmen, Walsh, Noel, Amarwani, Shreya, Liao, Jing, Xiong, Qiang, Drouin, Lauren, Hebben, Matthias, Chiang, Kyle, Chau, B. Nelson

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Novel AAV-mediated genome editing therapy improves health and survival in a mouse model of methylmalonic acidemia von Shengwen Zhang, Amy Bastille, Susana Gordo, Nikhil Ramesh, Jenisha Vora, Elizabeth McCarthy, Xiaohan Zhang, Dylan Frank, Chih-Wei Ko, Carmen Wu, Noel Walsh, Shreya Amarwani, Jing Liao, Qiang Xiong, Lauren Drouin, Matthias Hebben, Kyle Chiang, B Nelson Chau

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