3D Printed Functional and Biological Materials on Moving Freeform Surfaces von Zhu, Zhijie, Guo, Shuang‐Zhuang, Hirdler, Tessa, Eide, Cindy, Fan, Xiaoxiao, Tolar, Jakub, McAlpine, Michael C.

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Incorporation of Immune Checkpoint Blockade into Chimeric Antigen Receptor T Cells (CAR-Ts): Combination or Built-In CAR-T von Yoon, Dok Hyun, Osborn, Mark J, Tolar, Jakub, Kim, Chong Jai

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Allogeneic blood and bone marrow cells for the treatment of severe epidermolysis bullosa: repair of the extracellular matrix von Tolar, Jakub, MD, Wagner, John E, Prof

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Phase I/II Trial of StemRegenin-1 Expanded Umbilical Cord Blood Hematopoietic Stem Cells Supports Testing as a Stand-Alone Graft von Wagner, John E., Brunstein, Claudio G., Boitano, Anthony E., DeFor, Todd E., McKenna, David, Sumstad, Darin, Blazar, Bruce R., Tolar, Jakub, Le, Chap, Jones, Julie, Cooke, Michael P., Bleul, Conrad C.

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Rapid DNA replication origin licensing protects stem cell pluripotency von Matson, Jacob Peter, Dumitru, Raluca, Coryell, Philip, Baxley, Ryan M, Chen, Weili, Twaroski, Kirk, Webber, Beau R, Tolar, Jakub, Bielinsky, Anja-Katrin, Purvis, Jeremy E, Cook, Jeanette Gowen

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Base Editor Correction of COL7A1 in Recessive Dystrophic Epidermolysis Bullosa Patient-Derived Fibroblasts and iPSCs von Osborn, Mark J., Newby, Gregory A., McElroy, Amber N., Knipping, Friederike, Nielsen, Sarah C., Riddle, Megan J., Xia, Lily, Chen, Weili, Eide, Cindy R., Webber, Beau R., Wandall, Hans H., Dabelsteen, Sally, Blazar, Bruce R., Liu, David R., Tolar, Jakub

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A Biologic Velcro Patch von Tolar, Jakub, Wagner, John E

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Rapid Induction of Cerebral Organoids From Human Induced Pluripotent Stem Cells Using a Chemically Defined Hydrogel and Defined Cell Culture Medium von Lindborg, Beth A., Brekke, John H., Vegoe, Amanda L., Ulrich, Connor B., Haider, Kerri T., Subramaniam, Sandhya, Venhuizen, Scott L., Eide, Cindy R., Orchard, Paul J., Chen, Weili, Wang, Qi, Pelaez, Francisco, Scott, Carolyn M., Kokkoli, Efrosini, Keirstead, Susan A., Dutton, James R., Tolar, Jakub, O'Brien, Timothy D.

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Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases von Osborn, Mark J, Webber, Beau R, Knipping, Friederike, Lonetree, Cara-lin, Tennis, Nicole, DeFeo, Anthony P, McElroy, Amber N, Starker, Colby G, Lee, Catherine, Merkel, Sarah, Lund, Troy C, Kelly-Spratt, Karen S, Jensen, Michael C, Voytas, Daniel F, von Kalle, Christof, Schmidt, Manfred, Gabriel, Richard, Hippen, Keli L, Miller, Jeffrey S, Scharenberg, Andrew M, Tolar, Jakub, Blazar, Bruce R

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Phenotype categorization of neurofibromatosis type I and correlation to NF1 mutation types von Kang, Eungu, Kim, Yoon-Myung, Seo, Go Hun, Oh, Arum, Yoon, Hee Mang, Ra, Young-Shin, Kim, Eun Key, Kim, Heyry, Heo, Sun-Hee, Kim, Gu-Hwan, Osborn, Mark J, Tolar, Jakub, Yoo, Han-Wook, Lee, Beom Hee

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Outcomes after allogeneic hematopoietic cell transplantation for childhood cerebral adrenoleukodystrophy: the largest single-institution cohort report von Miller, Weston P., Rothman, Steven M., Nascene, David, Kivisto, Teresa, DeFor, Todd E., Ziegler, Richard S., Eisengart, Julie, Leiser, Kara, Raymond, Gerald, Lund, Troy C., Tolar, Jakub, Orchard, Paul J.

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ATXN1-CIC Complex Is the Primary Driver of Cerebellar Pathology in Spinocerebellar Ataxia Type 1 through a Gain-of-Function Mechanism von Rousseaux, Maxime W.C., Tschumperlin, Tyler, Lu, Hsiang-Chih, Lackey, Elizabeth P., Bondar, Vitaliy V., Wan, Ying-Wooi, Tan, Qiumin, Adamski, Carolyn J., Friedrich, Jillian, Twaroski, Kirk, Chen, Weili, Tolar, Jakub, Henzler, Christine, Sharma, Ajay, Bajić, Aleksandar, Lin, Tao, Duvick, Lisa, Liu, Zhandong, Sillitoe, Roy V., Zoghbi, Huda Y., Orr, Harry T.

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Bone Marrow Transplantation for Recessive Dystrophic Epidermolysis Bullosa von Wagner, John E, Ishida-Yamamoto, Akemi, McGrath, John A, Hordinsky, Maria, Keene, Douglas R, Woodley, David T, Chen, Mei, Riddle, Megan J, Osborn, Mark J, Lund, Troy, Dolan, Michelle, Blazar, Bruce R, Tolar, Jakub

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Creation and characterization of novel rat model for recessive dystrophic epidermolysis bullosa: Frameshift mutation of the Col7a1 gene leads to severe blistered phenotype von Stone, William, Strege, Chloe, Miller, William, Geurts, Aron M, Grzybowski, Michael, Riddle, Megan, Lees, Christopher, Eide, Cindy, Keene, Douglas R, Tufa, Sara F, Seelig, Davis, McGrath, John, Tolar, Jakub

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latent human herpesvirus-6A genome specifically integrates in telomeres of human chromosomes in vivo and in vitro von Arbuckle, Jesse H, Medveczky, Maria M, Luka, Janos, Hadley, Stephen H, Luegmayr, Andrea, Ablashi, Dharam, Lund, Troy C, Tolar, Jakub, De Meirleir, Kenny, Montoya, Jose G, Komaroff, Anthony L, Ambros, Peter F, Medveczky, Peter G

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Retinoblastoma tumor cell proliferation is negatively associated with an immune gene expression signature and increased immune cells von Sarver, Aaron L., Xie, Chencheng, Riddle, Megan J., Forster, Colleen L., Wang, Xiaohong, Lu, Huarui, Wagner, Wyatt, Tolar, Jakub, Hallstrom, Timothy C.

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Accumulation of senescence observed in spinocerebellar ataxia type 7 mouse model von Miller, William, Pruett, Charles Lewis Humphrey, Stone, William, Eide, Cindy, Riddle, Megan, Popp, Courtney, Yousefzadeh, Matthew, Lees, Christopher, Seelig, Davis, Thompson, Elizabeth, Orr, Harry, Niedernhofer, Laura, Tolar, Jakub

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A multitask clustering approach for single-cell RNA-seq analysis in Recessive Dystrophic Epidermolysis Bullosa von Zhang, Huanan, Lee, Catherine A A, Li, Zhuliu, Garbe, John R, Eide, Cindy R, Petegrosso, Raphael, Kuang, Rui, Tolar, Jakub

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Derivation and high engraftment of patient-specific cardiomyocyte sheet using induced pluripotent stem cells generated from adult cardiac fibroblast von Zhang, Liying, Guo, Jing, Zhang, Pengyuan, Xiong, Qiang, Wu, Steven C, Xia, Lily, Roy, Samit Sunny, Tolar, Jakub, O'Connell, Timothy D, Kyba, Michael, Liao, Kenneth, Zhang, Jianyi

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Intrathecal enzyme replacement for Hurler syndrome: biomarker association with neurocognitive outcomes von Eisengart, Julie B., Pierpont, Elizabeth I., Kaizer, Alexander M., Rudser, Kyle D., King, Kelly E., Pasquali, Marzia, Polgreen, Lynda E., Dickson, Patricia I., Le, Steven Q., Miller, Weston P., Tolar, Jakub, Orchard, Paul J., Lund, Troy C.

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