Randomized and non-randomized designs for causal inference with longitudinal data in rare disorders von Izem, Rima, McCarter, Robert

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FDA Initiative for Drug Facts Label for Over-the-Counter Naloxone von Cohen, Barbara R, Mahoney, Karen M, Baro, Elande, Squire, Claudia, Beck, Melissa, Travis, Sara, Pike-McCrudden, Amanda, Izem, Rima, Woodcock, Janet

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Plasmodium falciparum clearance time in Malawian children with cerebral malaria: a retrospective cohort study von Saidi, Alexuse M., Guenther, Geoffrey, Izem, Rima, Chen, Xiaojun, Seydel, Karl, Postels, Douglas

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Real-World Data as External Controls: Practical Experience from Notable Marketing Applications of New Therapies von Izem, Rima, Buenconsejo, Joan, Davi, Ruthanna, Luan, Jingyu Julia, Tracy, LaRee, Gamalo, Margaret

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Decentralized Clinical Trials: Scientific Considerations Through the Lens of the Estimand Framework von Izem, Rima, Zuber, Emmanuel, Daizadeh, Nadia, Bretz, Frank, Sverdlov, Oleksandr, Edrich, Pascal, Branson, Janice, Degtyarev, Evgeny, Sfikas, Nikolaos, Hemmings, Robert

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Unlocking the Potential: A Systematic Review of Master Protocol in Pediatrics von Li, Yimei, Nelson, Robert, Izem, Rima, Broglio, Kristine, Mundayat, Rajiv, Gamalo, Margaret, Wen, Yansong, Pan, Haitao, Sun, Hengrui, Ye, Jingjing

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Validation of a computational phenotype for finding patients eligible for genetic testing for pathogenic PTEN variants across three centers von Kothari, Cartik, Srivastava, Siddharth, Kousa, Youssef, Izem, Rima, Gierdalski, Marcin, Kim, Dongkyu, Good, Amy, Dies, Kira A, Geisel, Gregory, Morizono, Hiroki, Gallo, Vittorio, Pomeroy, Scott L, Garden, Gwenn A, Guay-Woodford, Lisa, Sahin, Mustafa, Avillach, Paul

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Are asymptomatic carriers of OTC deficiency always asymptomatic? A multicentric retrospective study of risk using the UCDC longitudinal study database von Sen, Kuntal, Izem, Rima, Long, Yuelin, Jiang, Jiji, Konczal, Laura L., McCarter, Robert J., Mew, Nicholas Ah, Baumgartner, Matthias R., Berry, Gerard, Berry, Susan A., Burgard, Peter, Burrage, Lindsay C., Cederbaum, Stephen, Coughlin, Curtis, Diaz, George A., Enns, Gregory, Gallagher, Renata C., Harding, Cary O., Hoffmann, Georg F., Le Mons, Cynthia, McCandless, Shawn E., Merritt, J. Lawrence, Nagamani, Sandesh C. S., Schulze, Andreas, Seminara, Jennifer, Stricker, Tamar, Tuchman, Mendel, Waisbren, Susan, Weisfeld‐Adams, James D., Wong, Derek, Yudkoff, Marc, Gropman, Andrea L., Bedoyan, Jirair K.

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Novel clinical trial design and analytic methods to tackle challenges in therapeutic development in rare diseases von Li, Yimei, Izem, Rima

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The genetic basis of thermal reaction norm evolution in lab and natural phage populations von Knies, Jennifer L, Izem, Rima, Supler, Katie L, Kingsolver, Joel G, Burch, Christina L

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The role of quantitative safety evaluation in regulatory decision making of drugs von Chakravarty, Aloka G., Izem, Rima, Keeton, Stephine, Kim, Clara Y., Levenson, Mark S., Soukup, Mat

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Sample size estimation for case‐crossover studies von Dharmarajan, Sai, Lee, Joo‐Yeon, Izem, Rima

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Stroke, Bleeding, and Mortality Risks in Elderly Medicare Beneficiaries Treated With Dabigatran or Rivaroxaban for Nonvalvular Atrial Fibrillation von Graham, David J, Reichman, Marsha E, Wernecke, Michael, Hsueh, Ya-Hui, Izem, Rima, Southworth, Mary Ross, Wei, Yuqin, Liao, Jiemin, Goulding, Margie R, Mott, Katrina, Chillarige, Yoganand, MaCurdy, Thomas E, Worrall, Chris, Kelman, Jeffrey A

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Are asymptomatic carriers of OTC always asymptomatic? A multicentric retrospective study of risk using the UCDC longitudinal study database von Sen, Kuntal, Izem, Rima, Long, Yuelin, Jiang, Jiji, Konczal, Laura, McCarter, Robert, Gropman, Andrea, Bedoyan, Jirair

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Sample size estimation for case‐crossover studies von Dharmarajan, Sai, Lee, Joo‐Yeon, Izem, Rima

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Using EEG in Resource-Limited Areas: Comparing Qualitative and Quantitative Interpretation Methods in Cerebral Malaria von Andrews, Alexander, Zelleke, Tesfaye, Izem, Rima, Gai, Jiaxiang, Harrar, Dana, Mvula, Jessica, Postels, Douglas G.

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Post-Malaria Anemia Is Rare in Malawian Children with Cerebral Malaria von Guenther, Geoffrey, Saidi, Alexuse M., Izem, Rima, Seydel, Karl, Postels, Douglas G.

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11: Post-malarial Hemolysis is Rare in Malawian Children with Cerebral Malaria von Guenther, Geoffrey, Izem, Rima, Saidi, Alexuse, Seydel, Karl, Postels, Douglas

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Comparison of propensity score methods for pre-specified subgroup analysis with survival data von Izem, Rima, Liao, Jiemin, Hu, Mao, Wei, Yuqin, Akhtar, Sandia, Wernecke, Michael, MaCurdy, Thomas E., Kelman, Jeffrey, Graham, David J

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Variation in Continuous Reaction Norms: Quantifying Directions of Biological Interest von Izem, Rima, Kingsolver, Joel G.

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