Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo von Ibraheim, Raed, Tai, Phillip W. L., Mir, Aamir, Javeed, Nida, Wang, Jiaming, Rodríguez, Tomás C., Namkung, Suk, Nelson, Samantha, Khokhar, Eraj Shafiq, Mintzer, Esther, Maitland, Stacy, Chen, Zexiang, Cao, Yueying, Tsagkaraki, Emmanouela, Wolfe, Scot A., Wang, Dan, Pai, Athma A., Xue, Wen, Gao, Guangping, Sontheimer, Erik J.

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CRISPR-enhanced human adipocyte browning as cell therapy for metabolic disease von Tsagkaraki, Emmanouela, Nicoloro, Sarah M., DeSouza, Tiffany, Solivan-Rivera, Javier, Desai, Anand, Lifshitz, Lawrence M., Shen, Yuefei, Kelly, Mark, Guilherme, Adilson, Henriques, Felipe, Amrani, Nadia, Ibraheim, Raed, Rodriguez, Tomas C., Luk, Kevin, Maitland, Stacy, Friedline, Randall H., Tauer, Lauren, Hu, Xiaodi, Kim, Jason K., Wolfe, Scot A., Sontheimer, Erik J., Corvera, Silvia, Czech, Michael P.

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All-in-one adeno-associated virus delivery and genome editing by Neisseria meningitidis Cas9 in vivo von Ibraheim, Raed, Song, Chun-Qing, Mir, Aamir, Amrani, Nadia, Xue, Wen, Sontheimer, Erik J

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Tissue-restricted genome editing in vivo specified by microRNA-repressible anti-CRISPR proteins von Lee, Jooyoung, Mou, Haiwei, Ibraheim, Raed, Liang, Shun-Qing, Liu, Pengpeng, Xue, Wen, Sontheimer, Erik J

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NmeCas9 is an intrinsically high-fidelity genome-editing platform von Amrani, Nadia, Gao, Xin D, Liu, Pengpeng, Edraki, Alireza, Mir, Aamir, Ibraheim, Raed, Gupta, Ankit, Sasaki, Kanae E, Wu, Tong, Donohoue, Paul D, Settle, Alexander H, Lied, Alexandra M, McGovern, Kyle, Fuller, Chris K, Cameron, Peter, Fazzio, Thomas G, Zhu, Lihua Julie, Wolfe, Scot A, Sontheimer, Erik J

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Potent Cas9 Inhibition in Bacterial and Human Cells by AcrIIC4 and AcrIIC5 Anti-CRISPR Proteins von Lee, Jooyoung, Mir, Aamir, Edraki, Alireza, Garcia, Bianca, Amrani, Nadia, Lou, Hannah E, Gainetdinov, Ildar, Pawluk, April, Ibraheim, Raed, Gao, Xin D, Liu, Pengpeng, Davidson, Alan R, Maxwell, Karen L, Sontheimer, Erik J

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A Compact, High-Accuracy Cas9 with a Dinucleotide PAM for In Vivo Genome Editing von Edraki, Alireza, Mir, Aamir, Ibraheim, Raed, Gainetdinov, Ildar, Yoon, Yeonsoo, Song, Chun-Qing, Cao, Yueying, Gallant, Judith, Xue, Wen, Rivera-Pérez, Jaime A., Sontheimer, Erik J.

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Structures of Neisseria meningitidis Cas9 Complexes in Catalytically Poised and Anti-CRISPR-Inhibited States von Sun, Wei, Yang, Jing, Cheng, Zhi, Amrani, Nadia, Liu, Chao, Wang, Kangkang, Ibraheim, Raed, Edraki, Alireza, Huang, Xue, Wang, Min, Wang, Jiuyu, Liu, Liang, Sheng, Gang, Yang, Yanhua, Lou, Jizhong, Sontheimer, Erik J., Wang, Yanli

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Sleeping Beauty mRNA-LNP enables stable rAAV transgene expression in mouse and NHP hepatocytes and improves vector potency von Zakas, Philip M., Cunningham, Sharon C., Doherty, Ann, van Dijk, Eva B., Ibraheim, Raed, Yu, Stephanie, Mekonnen, Befikadu D., Lang, Brendan, English, Elizabeth J., Sun, Gang, Duncan, Miles C., Benczkowski, Matthew S., Altshuler, Robert C., Singh, Malvenderjit Jagjit, Kibbler, Emily S., Tonga, Gulen Y., Wang, Zi Jun, Wang, Z. Jane, Li, Guangde, An, Ding, Rottman, James B., Bhavsar, Yashvi, Purcell, Cormac, Jain, Rachit, Alberry, Ryan, Roquet, Nathaniel, Fu, Yanfang, Citorik, Robert J., Rubens, Jacob R., Holmes, Michael C., Cotta-Ramusino, Cecilia, Querbes, William, Alexander, Ian E., Salomon, William E.

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A Scalable and Accurate Method for Quantifying Vector Genomes of Recombinant Adeno-Associated Viruses in Crude Lysate von Ai, Jianzhong, Ibraheim, Raed, Tai, Phillip W L, Gao, Guangping

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Targeted CRISPR delivery platforms von ILDAR, Gainetdinov, IBRAHEIM, Raed, SONTHEIMER, Erik Joseph, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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Targeted CRISPR Delivery Platforms von Xue, Wen, Mir, Aamir, Sontheimer, Erik J, Gainetdinov, Ildar, Edraki, Alireza, Ibraheim, Raed

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Targeted CRISPR delivery platforms von ILDAR, Gainetdinov, IBRAHEIM, Raed, SONTHEIMER, Erik Joseph, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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TARGETED CRISPR DELIVERY PLATFORMS von ILDAR, Gainetdinov, SONTHEIMER, Erik, Joseph, IBRAHEIM, Raed, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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TARGETED CRISPR DELIVERY PLATFORMS von ILDAR, Gainetdinov, SONTHEIMER, Erik, Joseph, IBRAHEIM, Raed, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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Targeted crispr delivery platforms von ILDAR Gainetdinov, IBRAHEIM Raed, SONTHEIMER Erik Joseph, MIR Aamir, XUE Wen, EDRAKI Alireza

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TARGETED CRISPR DELIVERY PLATFORMS von ILDAR, Gainetdinov, IBRAHEIM, Raed, SONTHEIMER, Erik, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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Targeted CRISPR delivery platforms von ILDAR, Gainetdinov, IBRAHEIM, Raed, SONTHEIMER, Erik Joseph, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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Targeted CRISPR Delivery Platforms von Xue, Wen, Mir, Aamir, Sontheimer, Erik J, Gainetdinov, Ildar, Edraki, Alireza, Ibraheim, Raed

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TARGETED CRISPR DELIVERY PLATFORMS von ILDAR, Gainetdinov, IBRAHEIM, Raed, SONTHEIMER, Erik, EDRAKI, Alireza, XUE, Wen, MIR, Aamir

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