The discovery of dystrophin, the protein product of the Duchenne muscular dystrophy gene von Hoffman, Eric P.

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Is it time for genetic modifiers to predict prognosis in Duchenne muscular dystrophy? von Bello, Luca, Hoffman, Eric P., Pegoraro, Elena

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A fleeting glimpse of functional benefit of the complete DMD gene in a large animal model of Duchenne muscular dystrophy von Hoffman, Eric P.

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Large-scale serum protein biomarker discovery in Duchenne muscular dystrophy von Hathout, Yetrib, Brody, Edward, Clemens, Paula R., Cripe, Linda, DeLisle, Robert Kirk, Furlong, Pat, Gordish-Dressman, Heather, Hache, Lauren, Henricson, Erik, Hoffman, Eric P., Kobayashi, Yvonne Monique, Lorts, Angela, Mah, Jean K., McDonald, Craig, Mehler, Bob, Nelson, Sally, Nikrad, Malti, Singer, Britta, Steele, Fintan, Sterling, David, Sweeney, H. Lee, Williams, Steve, Gold, Larry

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Glucose Restriction Inhibits Skeletal Myoblast Differentiation by Activating SIRT1 through AMPK-Mediated Regulation of Nampt von Fulco, Marcella, Cen, Yana, Zhao, Po, Hoffman, Eric P., McBurney, Michael W., Sauve, Anthony A., Sartorelli, Vittorio

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Genetic Modifiers of Duchenne Muscular Dystrophy and Dilated Cardiomyopathy von Barp, Andrea, Bello, Luca, Politano, Luisa, Melacini, Paola, Calore, Chiara, Polo, Angela, Vianello, Sara, Sorarù, Gianni, Semplicini, Claudio, Pantic, Boris, Taglia, Antonella, Picillo, Ester, Magri, Francesca, Gorni, Ksenija, Messina, Sonia, Vita, Gian Luca, Vita, Giuseppe, Comi, Giacomo P, Ermani, Mario, Calvo, Vincenzo, Angelini, Corrado, Hoffman, Eric P, Pegoraro, Elena

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Exon-Skipping in Duchenne Muscular Dystrophy von Takeda, Shin’ichi, Clemens, Paula R., Hoffman, Eric P.

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Genetic modifiers of ambulation in the cooperative international Neuromuscular research group Duchenne natural history study von Bello, Luca, Kesari, Akanchha, Gordish-Dressman, Heather, Cnaan, Avital, Morgenroth, Lauren P., Punetha, Jaya, Duong, Tina, Henricson, Erik K., Pegoraro, Elena, McDonald, Craig M., Hoffman, Eric P.

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Biomarker-focused multi-drug combination therapy and repurposing trial in mdx mice von Ziemba, Michael, Barkhouse, Molly, Uaesoontrachoon, Kitipong, Giri, Mamta, Hathout, Yetrib, Dang, Utkarsh J., Gordish-Dressman, Heather, Nagaraju, Kanneboyina, Hoffman, Eric P.

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Asynchronous remodeling is a driver of failed regeneration in Duchenne muscular dystrophy von Dadgar, Sherry, Wang, Zuyi, Johnston, Helen, Kesari, Akanchha, Nagaraju, Kanneboyina, Chen, Yi-Wen, Hill, D Ashley, Partridge, Terence A, Giri, Mamta, Freishtat, Robert J, Nazarian, Javad, Xuan, Jianhua, Wang, Yue, Hoffman, Eric P

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Bodywide skipping of exons 45–55 in dystrophic mdx52 mice by systemic antisense delivery von Aoki, Yoshitsugu, Yokota, Toshifumi, Nagata, Tetsuya, Nakamura, Akinori, Tanihata, Jun, Saito, Takashi, Duguez, Stephanie M. R, Nagaraju, Kanneboyina, Hoffman, Eric P, Partridge, Terence, Takeda, Shin'ichi

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Muscle Weakness in Myositis: MicroRNA‐Mediated Dystrophin Reduction in a Myositis Mouse Model and Human Muscle Biopsies von Kinder, Travis B., Heier, Christopher R., Tully, Christopher B., Van der Muelen, Jack H., Hoffman, Eric P., Nagaraju, Kanneboyina, Fiorillo, Alyson A.

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Discovery of serum protein biomarkers in the mdx mouse model and cross-species comparison to Duchenne muscular dystrophy patients von Hathout, Yetrib, Marathi, Ramya L, Rayavarapu, Sree, Zhang, Aiping, Brown, Kristy J, Seol, Haeri, Gordish-Dressman, Heather, Cirak, Sebahattin, Bello, Luca, Nagaraju, Kanneboyina, Partridge, Terry, Hoffman, Eric P, Takeda, Shin'ichi, Mah, Jean K, Henricson, Erik, McDonald, Craig

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Microtubules underlie dysfunction in duchenne muscular dystrophy von Khairallah, Ramzi J, Shi, Guoli, Sbrana, Francesca, Prosser, Benjamin L, Borroto, Carlos, Mazaitis, Mark J, Hoffman, Eric P, Mahurkar, Anup, Sachs, Fredrick, Sun, Yezhou, Chen, Yi-Wen, Raiteri, Roberto, Lederer, W Jonathan, Dorsey, Susan G, Ward, Christopher W

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TNF-α-Induced microRNAs Control Dystrophin Expression in Becker Muscular Dystrophy von Fiorillo, Alyson A., Heier, Christopher R., Novak, James S., Tully, Christopher B., Brown, Kristy J., Uaesoontrachoon, Kitipong, Vila, Maria C., Ngheim, Peter P., Bello, Luca, Kornegay, Joe N., Angelini, Corrado, Partridge, Terence A., Nagaraju, Kanneboyina, Hoffman, Eric P.

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Sphingosine-1-phosphate enhances satellite cell activation in dystrophic muscles through a S1PR2/STAT3 signaling pathway von Loh, Kenneth C, Leong, Weng-In, Carlson, Morgan E, Oskouian, Babak, Kumar, Ashok, Fyrst, Henrik, Zhang, Meng, Proia, Richard L, Hoffman, Eric P, Saba, Julie D

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Myoblasts and macrophages are required for therapeutic morpholino antisense oligonucleotide delivery to dystrophic muscle von Novak, James S., Hogarth, Marshall W., Boehler, Jessica F., Nearing, Marie, Vila, Maria C., Heredia, Raul, Fiorillo, Alyson A., Zhang, Aiping, Hathout, Yetrib, Hoffman, Eric P., Jaiswal, Jyoti K., Nagaraju, Kanneboyina, Cirak, Sebahattin, Partridge, Terence A.

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A Dystrophin Exon-52 Deleted Miniature Pig Model of Duchenne Muscular Dystrophy and Evaluation of Exon Skipping von Echigoya, Yusuke, Trieu, Nhu, Duddy, William, Moulton, Hong M., Yin, HaiFang, Partridge, Terence A., Hoffman, Eric P., Kornegay, Joe N., Rohret, Frank A., Rogers, Christopher S., Yokota, Toshifumi

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Natural progression of childhood asthma symptoms and strong influence of sex and puberty von Fu, Liang, Freishtat, Robert J, Gordish-Dressman, Heather, Teach, Stephen J, Resca, Lorenzo, Hoffman, Eric P, Wang, Zuyi

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Identification of Disease Specific Pathways Using in Vivo SILAC Proteomics in Dystrophin Deficient mdx Mouse von Rayavarapu, Sree, Coley, William, Cakir, Erdinc, Jahnke, Vanessa, Takeda, Shin'ichi, Aoki, Yoshitsugu, Grodish-Dressman, Heather, Jaiswal, Jyoti K., Hoffman, Eric P., Brown, Kristy J., Hathout, Yetrib, Nagaraju, Kanneboyina

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