P-21 Activated Kinase 1 (Pak1) Is Critical for Normal Mast Cell Degranulation and Cytokine Production in Response to Antigen Stimulation of the High Affinity IgE Receptor von Allen, Jayme D., Hoffman, Clemens, Derr-Yellin, Ethel, Bessler, Waylan, Yang, Fen-Chun, Ingram, David A., Jaffer, Zahra, Tipton, Amanda, Chernoff, Johnathan, Clapp, D. Wade

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Large-scale serum protein biomarker discovery in Duchenne muscular dystrophy von Hathout, Yetrib, Brody, Edward, Clemens, Paula R., Cripe, Linda, DeLisle, Robert Kirk, Furlong, Pat, Gordish-Dressman, Heather, Hache, Lauren, Henricson, Erik, Hoffman, Eric P., Kobayashi, Yvonne Monique, Lorts, Angela, Mah, Jean K., McDonald, Craig, Mehler, Bob, Nelson, Sally, Nikrad, Malti, Singer, Britta, Steele, Fintan, Sterling, David, Sweeney, H. Lee, Williams, Steve, Gold, Larry

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Safety, Tolerability, and Efficacy of Viltolarsen in Boys With Duchenne Muscular Dystrophy Amenable to Exon 53 Skipping: A Phase 2 Randomized Clinical Trial von Clemens, Paula R, Rao, Vamshi K, Connolly, Anne M, Harper, Amy D, Mah, Jean K, Smith, Edward C, McDonald, Craig M, Zaidman, Craig M, Morgenroth, Lauren P, Osaki, Hironori, Satou, Youhei, Yamashita, Taishi, Hoffman, Eric P

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Exon-Skipping in Duchenne Muscular Dystrophy von Takeda, Shin’ichi, Clemens, Paula R., Hoffman, Eric P.

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Demographic causes of adult sex ratio variation and their consequences for parental cooperation von Eberhart-Phillips, Luke J., Küpper, Clemens, Carmona-Isunza, María Cristina, Vincze, Orsolya, Zefania, Sama, Cruz-López, Medardo, Kosztolányi, András, Miller, Tom E. X., Barta, Zoltán, Cuthill, Innes C., Burke, Terry, Székely, Tamás, Hoffman, Joseph I., Krüger, Oliver

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Sex-specific early survival drives adult sex ratio bias in snowy plovers and impacts mating system and population growth von Eberhart-Phillips, Luke J., Küpper, Clemens, Miller, Tom E. X., Cruz-López, Medardo, Maher, Kathryn H., dos Remedios, Natalie, Stoffel, Martin A., Hoffman, Joseph I., Krüger, Oliver, Székely, Tamás

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Concerns Regarding Therapeutic Implications of Very Low‐Level Dystrophin von Hoffman, Eric P., Clemens, Paula R.

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Efficacy and safety of vamorolone in Duchenne muscular dystrophy: An 18-month interim analysis of a non-randomized open-label extension study von Smith, Edward C., Conklin, Laurie S., Hoffman, Eric P., Clemens, Paula R., Mah, Jean K., Finkel, Richard S., Guglieri, Michela, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M., Webster, Richard, Castro, Diana, Kuntz, Nancy L., Kerchner, Laurie, Morgenroth, Lauren P., Arrieta, Adrienne, Shimony, Maya, Jaros, Mark, Shale, Phil, Gordish-Dressman, Heather, Hagerty, Laura, Dang, Utkarsh J., Damsker, Jesse M., Schwartz, Benjamin D., Mengle-Gaw, Laurel J., McDonald, Craig M.

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Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study von Boca, Simina M, Nishida, Maki, Harris, Michael, Rao, Shruti, Cheema, Amrita K, Gill, Kirandeep, Seol, Haeri, Morgenroth, Lauren P, Henricson, Erik, McDonald, Craig, Mah, Jean K, Clemens, Paula R, Hoffman, Eric P, Hathout, Yetrib, Madhavan, Subha

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Regulation of Dendritic Excitability by Activity-Dependent Trafficking of the A-Type K + Channel Subunit Kv4.2 in Hippocampal Neurons von Kim, Jinhyun, Jung, Sung-Cherl, Clemens, Ann M., Petralia, Ronald S., Hoffman, Dax A.

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Adrenal suppression from vamorolone and prednisone in Duchenne muscular dystrophy: results from the phase 2b clinical trial von Ahmet, Alexandra, Tobin, Rebecca, Dang, Utkarsh J, Rooman, Raoul, Guglieri, Michela, Clemens, Paula R, Hoffman, Eric P, Ward, Leanne M

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Asprosin-neutralizing antibodies as a treatment for metabolic syndrome von Mishra, Ila, Duerrschmid, Clemens, Ku, Zhiqiang, He, Yang, Xie, Wei, Silva, Elizabeth Sabath, Hoffman, Jennifer, Xin, Wei, Zhang, Ningyan, Xu, Yong, An, Zhiqiang, Chopra, Atul R

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Vamorolone trial in Duchenne muscular dystrophy shows dose-related improvement of muscle function von Hoffman, Eric P, Schwartz, Benjamin D, Mengle-Gaw, Laurel J, Smith, Edward C, Castro, Diana, Mah, Jean K, McDonald, Craig M, Kuntz, Nancy L, Finkel, Richard S, Guglieri, Michela, Bushby, Katharine, Tulinius, Mar, Nevo, Yoram, Ryan, Monique M, Webster, Richard, Smith, Andrea L, Morgenroth, Lauren P, Arrieta, Adrienne, Shimony, Maya, Siener, Catherine, Jaros, Mark, Shale, Phil, McCall, John M, Nagaraju, Kanneboyina, van den Anker, John, Conklin, Laurie S, Cnaan, Avital, Gordish-Dressman, Heather, Damsker, Jesse M, Clemens, Paula R

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Serum pharmacodynamic biomarkers for chronic corticosteroid treatment of children von Hathout, Yetrib, Conklin, Laurie S., Seol, Haeri, Gordish-Dressman, Heather, Brown, Kristy J., Morgenroth, Lauren P., Nagaraju, Kanneboyina, Heier, Christopher R., Damsker, Jesse M., van den Anker, John N., Henricson, Erik, Clemens, Paula R., Mah, Jean K., McDonald, Craig, Hoffman, Eric P.

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Dissecting p53 tumor suppressor functions in vivo von Schmitt, Clemens A, Fridman, Jordan S, Yang, Meng, Baranov, Eugene, Hoffman, Robert M, Lowe, Scott W

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Correction: Discovery of Metabolic Biomarkers for Duchenne Muscular Dystrophy within a Natural History Study von Boca, Simina M, Nishida, Maki, Harris, Michael, Rao, Shruti, Cheema, Amrita K, Gill, Kirandeep, Wang, Difei, An, Lin, Gauba, Robinder, Seol, Haeri, Morgenroth, Lauren P, Henricson, Erik, McDonald, Craig, Mah, Jean K, Clemens, Paula R, Hoffman, Eric P, Hathout, Yetrib, Madhavan, Subha

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High fidelity: extra-pair fertilisations in eight Charadrius plover species are not associated with parental relatedness or social mating system von Kathryn H. Maher, Luke J. Eberhart-Phillips, András Kosztolányi, Natalie dos Remedios, María Cristina Carmona-Isunza, Medardo Cruz-López, Sama Zefania, James J. H. St Clair, Monif Alrashidi, Michael A. Weston, Martín A. Serrano-Meneses, Oliver Krüger, Joseph I. Hoffman, Tamás Székely, Terry Burke, Clemens Küpper

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Long-term effects of glucocorticoids on function, quality of life, and survival in patients with Duchenne muscular dystrophy: a prospective cohort study von McDonald, Craig M, Henricson, Erik K, Abresch, Richard T, Duong, Tina, Joyce, Nanette C, Hu, Fengming, Clemens, Paula R, Hoffman, Eric P, Cnaan, Avital, Gordish-Dressman, Heather, Vishwanathan, Vijay, Chidambaranathan, S, Biggar, W. Douglas, McAdam, Laura C., Mah, Jean K., Tulinius, Mar, Cnaan, Avital, Morgenroth, Lauren P., Leshner, Robert, Tesi-Rocha, Carolina, Thangarajh, Mathula, Duong, Tina, Kornberg, Andrew, Ryan, Monique, Nevo, Yoram, Dubrovsky, Alberto, Clemens, Paula R., Abdel-Hamid, Hoda, Connolly, Anne M., Pestronk, Alan, Teasley, Jean, Bertorin, Tulio E., Webster, Richard, Kolski, Hanna, Kuntz, Nancy, Driscoll, Sherilyn, Bodensteiner, John B., Carlo, Jose, Gorni, Ksenija, Lotze, Timothy, Day, John W., Karachunski, Peter, Henricson, Erik K., Abresch, Richard T., Joyce, Nanette C., McDonald, Craig M.

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Serum biomarkers associated with baseline clinical severity in young steroid-naïve Duchenne muscular dystrophy boys von Dang, Utkarsh J, Ziemba, Michael, Clemens, Paula R, Hathout, Yetrib, Conklin, Laurie S, Hoffman, Eric P

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Exposure‐Response Analysis of Vamorolone (VBP15) in Boys With Duchenne Muscular Dystrophy von Li, Xiaonan, Conklin, Laurie S., den Anker, John, Hoffman, Eric P., Clemens, Paula R., Jusko, William J.

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