Prevalence and pharmacological modulation of humoral immunity to AAV vectors in gene transfer to synovial tissue von Mingozzi, F, Chen, Y, Edmonson, S C, Zhou, S, Thurlings, R M, Tak, P P, High, K A, Vervoordeldonk, M J

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High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency von Ayuso, E, Mingozzi, F, Montane, J, Leon, X, Anguela, X M, Haurigot, V, Edmonson, S A, Africa, L, Zhou, S, High, K A, Bosch, F, Wright, J F

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AAV-mediated gene transfer for the treatment of hemophilia B: problems and prospects von Hasbrouck, N C, High, K A

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Gene therapy for haemophilia: a long and winding road von HIGH, K. A.

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Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector von High, Katherine A, Kay, Mark A, Manno, Catherine S, Ragni, Margaret V, Larson, Peter J, Couto, Linda B, McClelland, Alan, Glader, Bertil, Chew, Amy J, J Tai, Shing, Herzog, Roland W, Arruda, Valder, Johnson, Fred, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W

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A viable mouse model of factor X deficiency provides evidence for maternal transfer of factor X von Tai, S J, Herzog, R W, Margaritis, P, Arruda, V R, Chu, K, Golden, J A, Labosky, P A, High, K A

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Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A von Bi, L, Lawler, A.M, Antonarakis, S.E, High, K.A, Gearhart, J.D, Kazazian, H.H

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Progress in the molecular biology of inherited bleeding disorders von PIPE, S. W., HIGH, K. A., OHASHI, K., URAL, A. U., LILLICRAP, D.

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Prevalence of the factor V Leiden mutation in children and neonates with thromboembolic disease von Hagstrom, J.Nathan, Walter, Johannes, Bluebond-Langner, Rachel, Amatniek, Joan C., Manno, Catherine S., High, Katherine A.

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Gene Transfer as an Approach to Treating Hemophilia von High, Katherine A

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Enhanced γ-Carboxylation of Recombinant Factor X Using a Chimeric Construct Containing the Prothrombin Propeptide von Camire, Rodney M, Larson, Peter J, Stafford, Darrel W, High, Katherine A

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Gene therapy in haemophilia - going for cure? von MARGARITIS, P., HIGH, K. A.

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Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice von FIELDS, P. A, ARMSTRONG, E, HAGSTROM, J. N, ARRUDA, V. R, MURPHY, M. L, FARRELL, J. P, HIGH, K. A, HERZOG, R. W

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Canine Hemophilia B Resulting from a Point Mutation with Unusual Consequences von Evans, James P., Brinkhous, Kenneth M., Brayer, Gary D., Reisner, Howard M., High, Katherine A.

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AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B von Manno, Catherine S., Chew, Amy J., Hutchison, Sylvia, Larson, Peter J., Herzog, Roland W., Arruda, Valder R., Tai, Shing Jen, Ragni, Margaret V., Thompson, Arthur, Ozelo, Margareth, Couto, Linda B., Leonard, Debra G.B., Johnson, Frederick A., McClelland, Alan, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W., Kay, Mark A., High, Katherine A., Glader, Bertil

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Progress and Prospects: Gene Therapy Clinical Trials (Part 2) von Griesenbach, U

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Successful Expression of Human Factor IX Following Repeat Administration of an Adenoviral Vector in Mice von Walter, Johannes, You, Qimin, Hagstrom, J. Nathan, Sands, Mark, High, Katherine A.

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A mutation in the propeptide of Factor IX leads to warfarin sensitivity by a novel mechanism von Chu, K, Wu, S M, Stanley, T, Stafford, D W, High, K A

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Special lectures in haemophilia management von BATOROVA, A., HIGH, K. A., GRINGERI, A.

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Gene therapy: a 2001 perspective von High, K.A.

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