Corticosteroids in Duchenne muscular dystrophy: Major variations in practice von Griggs, Robert C., Herr, Barbara E., Reha, Allen, Elfring, Gary, Atkinson, Leone, Cwik, Valerie, Mccoll, Elaine, Tawil, Rabi, Pandya, Shree, McDermott, Michael P., Bushby, Kate

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Challenges in the Design and Conduct of Therapeutic Trials in Channel Disorders von Venance, Shannon L., Herr, Barbara E., Griggs, Robert C.

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Effect of Different Corticosteroid Dosing Regimens on Clinical Outcomes in Boys With Duchenne Muscular Dystrophy: A Randomized Clinical Trial von Guglieri, Michela, Bushby, Kate, McDermott, Michael P, Hart, Kimberly A, Tawil, Rabi, Martens, William B, Herr, Barbara E, McColl, Elaine, Speed, Chris, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michelle, Brown, Mary W, Willis, Tracey, Griggs, Robert C, Straub, Volker, van Ruiten, Henriette, Childs, Anne-Marie, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Maggi, Lorenzo, Baranello, Giovanni, Butterfield, Russell J, Horrocks, I. A, Roper, Helen, Alhaswani, Zoya, Flanigan, Kevin M, Kuntz, Nancy L, Manzur, Adnan, Darras, Basil T, Kang, Peter B, Morrison, Leslie, Krzesniak-Swinarska, Monika, Mah, Jean K, Mongini, Tiziana E, Ricci, Federica, von der Hagen, Maja, Finkel, Richard S, O’Reardon, Kathleen, Wicklund, Matthew, Kumar, Ashutosh, McDonald, Craig M, Han, Jay J, Joyce, Nanette, Henricson, Erik K, Schara-Schmidt, Ulrike, Gangfuss, Andrea, Wilichowski, Ekkehard, Barohn, Richard J, Statland, Jeffrey M, Campbell, Craig, Vita, Giuseppe, Vita, Gian Luca, Howard, James F, Hughes, Imelda, McMillan, Hugh J, Pegoraro, Elena, Bello, Luca, Burnette, W. Bryan, Thangarajh, Mathula, Chang, Taeun

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A checklist for clinical trials in rare disease: obstacles and anticipatory actions-lessons learned from the FOR-DMD trial von Crow, Rebecca A, Hart, Kimberly A, McDermott, Michael P, Tawil, Rabi, Martens, William B, Herr, Barbara E, McColl, Elaine, Wilkinson, Jennifer, Kirschner, Janbernd, King, Wendy M, Eagle, Michele, Brown, Mary W, Hirtz, Deborah, Lochmuller, Hanns, Straub, Volker, Ciafaloni, Emma, Shieh, Perry B, Spinty, Stefan, Childs, Anne-Marie, Manzur, Adnan Y, Morandi, Lucia, Butterfield, Russell J, Horrocks, Iain, Roper, Helen, Flanigan, Kevin M, Kuntz, Nancy L, Mah, Jean K, Morrison, Leslie, Darras, Basil T, von der Hagen, Maja, Schara, Ulrike, Wilichowski, Ekkehard, Mongini, Tiziana, McDonald, Craig M, Vita, Giuseppe, Barohn, Richard J, Finkel, Richard S, Wicklund, Matthew, McMillan, Jr, Hugh J, Hughes, Imelda, Pegoraro, Elena, Bryan Burnette, W, Howard, James F, Thangarajh, Mathula, Campbell, Craig, Griggs, Robert C, Bushby, Kate, Guglieri, Michela

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Poster Abstract #11: A Research Network for the Experimental Therapeutics of Rare Neurologic Disorders von Herr, Barbara E., Richesson, Rachel, Griggs, Robert C.

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Poster Abstract #2: Surrogate Completion of the Treatment Satisfaction Questionnaire for Medication for a Trial of Corticosteroids in Duchenne Muscular Dystrophy von Herr, Barbara E., Hart, Kimberly A., McDermott, Michael, Griggs, Robert C., Herbelin, Laura, Barohn, Richard

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Abstracts from the ASENT 2007 Annual Meeting March 5-8, 2007 von Vandenburgh, Amanda M, Abu-shakra, Susan, Brin, Mitchell F, Beddingfield, Frederick, Lipkovich, Ilya, Houston, John P, Ahl, Jonna, Kollack-walker, Sara, Kinon, Bruce, Stauffer, Virginia, Ascher-svanum, Haya, Keefe, Richard, Byrnes, Kimberly R, Stoica, Bogdan, Faden, Alan I, Tanaka, Kazunori, Okada, Yoshinori, Sakai, Harumi, Otomo, Asako, Hadano, Shinji, Osuga, Hitoshi, Ikeda, Joh-e, Torres, Richard, Vercollone, J, Anderson, K D, Croll, S D, Yancopoulos, G D, Wiegand, S J, Murphy, A J, Kaminski, Rafal M, Runyon, Scott P, Marini, Herbert, Rogawski, Michael A, Stoica, Bogdan A, Kunitz, Selma C, Gropman, Andrea, Hailu, Ayichew, Seltzer, Rebecca, Fricke, Stanley, van Meter, John, Herr, Barbara E, Richesson, Rachel, Griggs, Robert C, Fridman, Esteban, Krimchansky, Ben-zion, Galperin, Tatiana, Gamzu, Elkan, Bonetto, Mariana, Mettu, Krishna, Garewal, Mandeep, Sivaraman, Manjamali, Sahota, Pradeep, Tilley, Barbara C, Mainous, Arch, Smith, Dan, Elm, Jordan, Batshaw, Mark, Tuchman, Mendel, Elliott, Robin, Todaro, Veronica, Robinson, Robert G, Jorge, Ricardo E, Starkstein, Sergio E, Badman, D, Jackson, T, Miller, T

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Abstracts from the ASENT 2008 Annual Meeting March 6–8, 2008 von VanDenburgh, Amanda, Shah, Manasee V., Hua, S., Abu-Shakra, S., Wagg, Jon, Khariton, Tatiana, Beddingfield, F. C., Brin, M. F., Herr, Barbara E., Hart, Kimberly A., McDermott, Michael, Griggs, Robert C., Herbelin, Laura, Barohn, Richard, Loane, David J., Byrnes, Kimberly R., Stoica, Bogdan A., Pajoohesh-Ganji, Ahdeah, Faden, Alan I., Nahab, Fatta, Wittevrongel, Loretta, Hallett, Mark, Li, Ingrid, Brady, Linda, Driscoll, Jamie, Guyer, Mark, Yao, Yong, Almeida, Luis, Maia, Joana, Soares-da-Silva, Patricio, Rocha, Jose Francisco, Lopes, Carlos, Nunes, Teresa, Machado, Rita, Costa, Raquel, Torrão, Leonel, Loureiro, Ana-Isabel, Vaz-da-Silva, Manuel, Wright, Lyndon, Falcão, Amilcar, Coelho, Rui, Albino-Teixeira, Antonio, Cusack, Noel, Hurtt, Mark, Katner, Simon, Torchia, John, Solomon, Bruce, Guinn, Robyn, Rohde, Candace, Thorne, Christine, Cusack, Noel J., Aungst, Bruce, Venkatarangan, Lata, Behrens, Davette, Brown, Foster, Meltzer, Peter, Bakshi, Rohit, Neema, Mohit, Healy, Brian C., Liptak, Zsuzsanna, Betensky, Rebecca A., Buckle, Guy J., Gauthier, Susan A., Stankiewicz, James, Meier, Dominik, Egorova, Svetlana, Arora, Ashish, Guss, Zachary D., Glanz, Bonnie I., Khoury, Samia J., Guttmann, Charles R. G., Weiner, Howard L., Guss, Jason G.

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P113 Investigator-initiated clinical trials: What academicians need to know von Herr, Barbara E., Pelusio, Rita M.

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Mechanism of muscle wasting in myotonic dystrophy von Griggs, Robert C., Jozefowicz, Ralph, Kingston, William, Nair, K. Sreekumaran, Herr, Barbara E., Halliday, David

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Evaluation of exposure–response relationships for health effects of microbial bioaerosols – A systematic review von Walser, Sandra M., Gerstner, Doris G., Brenner, Bernhard, Bünger, Jürgen, Eikmann, Thomas, Janssen, Barbara, Kolb, Stefanie, Kolk, Annette, Nowak, Dennis, Raulf, Monika, Sagunski, Helmut, Sedlmaier, Nadja, Suchenwirth, Roland, Wiesmüller, Gerhard, Wollin, Klaus-Michael, Tesseraux, Irene, Herr, Caroline E.W.

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Anticipating the perceived risk of nanotechnologies von Satterfield, Terre, Kandlikar, Milind, Beaudrie, Christian E. H, Conti, Joseph, Herr Harthorn, Barbara

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Considerations of Environmentally Relevant Test Conditions for Improved Evaluation of Ecological Hazards of Engineered Nanomaterials von Holden, Patricia A, Gardea-Torresdey, Jorge L, Klaessig, Fred, Turco, Ronald F, Mortimer, Monika, Hund-Rinke, Kerstin, Cohen Hubal, Elaine A, Avery, David, Barceló, Damià, Behra, Renata, Cohen, Yoram, Deydier-Stephan, Laurence, Ferguson, P. Lee, Fernandes, Teresa F, Herr Harthorn, Barbara, Henderson, W. Matthew, Hoke, Robert A, Hristozov, Danail, Johnston, John M, Kane, Agnes B, Kapustka, Larry, Keller, Arturo A, Lenihan, Hunter S, Lovell, Wess, Murphy, Catherine J, Nisbet, Roger M, Petersen, Elijah J, Salinas, Edward R, Scheringer, Martin, Sharma, Monita, Speed, David E, Sultan, Yasir, Westerhoff, Paul, White, Jason C, Wiesner, Mark R, Wong, Eva M, Xing, Baoshan, Steele Horan, Meghan, Godwin, Hilary A, Nel, André E

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LDHA-Associated Lactic Acid Production Blunts Tumor Immunosurveillance by T and NK Cells von Brand, Almut, Singer, Katrin, Koehl, Gudrun E., Kolitzus, Marlene, Schoenhammer, Gabriele, Thiel, Annette, Matos, Carina, Bruss, Christina, Klobuch, Sebastian, Peter, Katrin, Kastenberger, Michael, Bogdan, Christian, Schleicher, Ulrike, Mackensen, Andreas, Ullrich, Evelyn, Fichtner-Feigl, Stefan, Kesselring, Rebecca, Mack, Matthias, Ritter, Uwe, Schmid, Maximilian, Blank, Christian, Dettmer, Katja, Oefner, Peter J., Hoffmann, Petra, Walenta, Stefan, Geissler, Edward K., Pouyssegur, Jacques, Villunger, Andreas, Steven, André, Seliger, Barbara, Schreml, Stephan, Haferkamp, Sebastian, Kohl, Elisabeth, Karrer, Sigrid, Berneburg, Mark, Herr, Wolfgang, Mueller-Klieser, Wolfgang, Renner, Kathrin, Kreutz, Marina

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Moving Assertive Community Treatment Into Standard Practice von Phillips, Susan D., Burns, Barbara J., Edgar, Elizabeth R., Mueser, Kim T., Linkins, Karen W., Rosenheck, Robert A., Drake, Robert E., McDonel Herr, Elizabeth C.

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Potential Role of the PD-1/PD-L1 Axis in the Immune Regulation of Chronic GVHD von Klobuch, Sebastian, Weber, Daniela, Holler, Barbara, Herr, Wolfgang, Holler, Ernst, Wolff, Daniel

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Abatacept as salvage therapy in chronic graft-versus-host disease—a retrospective analysis von Wertheimer, Tobias, Dohse, Marius, Afram, Gabriel, Weber, Daniela, Heidenreich, Martin, Holler, Barbara, Kattner, Anna-Sophia, Neubauer, Andreas, Mielke, Stephan, Ljungman, Per, Holler, Ernst, Herr, Wolfgang, Edinger, Matthias, Martínez, Antonio Pérez, Fante, Matthias, Wolff, Daniel

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An integrated model of multimorbidity and symptom science von Tripp-Reimer, Toni, Williams, Janet K, Gardner, Sue E., Rakel, Barbara, Herr, Keela, McCarthy, Ann Marie, Hand, Linda Liu, Gilbertson-White, Stephanie, Cherwin, Catherine

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Mexiletine for Symptoms and Signs of Myotonia in Nondystrophic Myotonia: A Randomized Controlled Trial von Statland, Jeffrey M, Bundy, Brian N, Wang, Yunxia, Rayan, Dipa Raja, Trivedi, Jaya R, Sansone, Valeria A, Salajegheh, Mohammad K, Venance, Shannon L, Ciafaloni, Emma, Matthews, Emma, Meola, Giovanni, Herbelin, Laura, Griggs, Robert C, Barohn, Richard J, Hanna, Michael G

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Diabetes and Neurodegeneration in Wolfram Syndrome: A multicenter study of phenotype and genotype von Rohayem, Julia, Ehlers, Christian, Wiedemann, Bärbel, Holl, Reinhard, Oexle, Konrad, Kordonouri, Olga, Salzano, Giuseppina, Meissner, Thomas, Burger, Walter, Schober, Edith, Huebner, Angela, Lee-Kirsch, Min Ae

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