Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system von DeRosa, F, Guild, B, Karve, S, Smith, L, Love, K, Dorkin, J R, Kauffman, K J, Zhang, J, Yahalom, B, Anderson, D G, Heartlein, M W

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Long-Term Production and Delivery of Human Growth Hormone In vivo von Heartlein, Michael W., Roman, Victoria A., Jiang, Ji-Lei, Sellers, Joan W., Zuliani, Antoinette M., Treco, Douglas A., Selden, Richard F.

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Chromosome instability associated with human alphoid DNA transfected into the Chinese hamster genome von HEARTLEIN, M. W, KNOLL, J. H. M, LATT, S. A

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5-Bromodeoxyuridine-dependent increase in sister chromatid exchange formation in Bloom's syndrome is associated with reduction in topoisomerase II activity von Heartlein, .W., Tsuji, H., Latt, S.A.

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Optimization of a degradable polymer−lipid nanoparticle for potent systemic delivery of mRNA to the lung endothelium and immune cells von Kaczmarek, J, Kauffman, K, Fenton, O, Sadtler, K, Patel, AK, Heartlein, MW, DeRosa, F, Anderson, D

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Inhaled nanoformulated mRNA polyplexes for protein production in lung epithelium von Patel, AK, Kaczmarek, JC, Bose, S, Kauffman, KJ, Mir, F, Heartlein, MW, DeRosa, F, Langer, R, Anderson, DG

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Amplified inverted duplications within and adjacent to heterologous selectable DNA von HEARTLEIN, M. W, LATT, S. A

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Polymer-lipid nanoparticles for systemic delivery of mRNA to the lungs von Kaczmarek, JC, Patel, AK, Kauffman, KJ, Fenton, OS, Webber, MJ, Heartlein, MW, DeRosa, F, Anderson, DG

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Mutagenicity of municipal water obtained from an agricultural area von Heartlein, M. W., Demarini, D. M., Katz, A. J., Brockman, H. E., Means, J. C., Plewa, M. J.

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Amplified inverted duplications within and adjacent to heterologous selectable DNAS von Heartlein, M.W., Latt, S.A.

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Breakage of the human Y-chromosome short arm between two blocks of tandemly repeated DNA sequences von Müller, Ulrich, Lalande, Marc, Donlon, Timothy A., Heartlein, Michael W.

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Chromosome Instability Associated with Human Alphoid DNA Transfected into the Chinese Hamster Genome von Heartlein, M. W., Knoll, J. H., Latt, S. A.

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COMPOSITIONS AND METHODS FOR TREATING GAUCHER DISEASE von DANIEL, PETER, F. PF, HEARTLEIN, MICHAEL, W. MW

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Human Sulfatase 2 inhibits in vivo tumor growth of MDA-MB-231 human breast cancer xenografts von Peterson, Sarah M, Iskenderian, Andrea, Cook, Lynette, Romashko, Alla, Tobin, Kristen, Jones, Michael, Norton, Angela, Gómez-Yafal, Alicia, Heartlein, Michael W, Concino, Michael F, Liaw, Lucy, Martini, Paolo G V

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Erythropoietin Produced in a Human Cell Line (Dynepo) Has Significant Differences in Glycosylation Compared with Erythropoietins Produced in CHO Cell Lines von Shahrokh, Zahra, Royle, Louise, Saldova, Radka, Bones, Jonathan, Abrahams, Jodie L, Artemenko, Natalia V, Flatman, Steve, Davies, Mike, Baycroft, Alison, Sehgal, Surinder, Heartlein, Michael W, Harvey, David J, Rudd, Pauline M

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TRANSFEKTION VON VERTEBRATENZELLEN BEISPIELSWEISE DURCH HOMOLOGE REKOMBINATION von HEARTLEIN, MICHAEL, W., BOXBOROUGH, MA 01719, US, TRECO, DOUGLAS, A., ARLINGTON, MA 02174, US, SELDEN, RICHARD, F., WELLESLEY, MA 02181, US

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Recombinant human complement component C2 produced in a human cell line restores the classical complement pathway activity in-vitro: an alternative treatment for C2 deficiency dise... von Martini, Paolo G V, Cook, Lynette C, Alderucci, Scott, Norton, Angela W, Lundberg, Dianna M, Fish, Susan M, Langsetmo, Knut, Jönsson, Göran, Lood, Christian, Gullstrand, Birgitta, Zaleski, Kate J, Savioli, Nancy, Lottherand, Jason, Bedard, Charles, Gill, John, Concino, Michael F, Heartlein, Michael W, Truedsson, Lennart, Powell, Jan L, Tzianabos, Arthur O

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TARGETED GENE EXPRESSION OF THROMBOPOIETEIN, DNASE I AND B-INTERFERON von HEARTLEIN, MICHAEL W, TRECO, DOUGLAS A, HAUGE, BRIAN M, SELDEN, RICHARD F

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TRANSKARYOTIC DELIVERY OF THERAPEUTIC PRODUCTS von HEARTLEIN MICHAEL W, SELDON RICHARD F, TRECO DOUGLAS A, HAUGE BRIAN M

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TRANSKARYOTIC DELIVERY OF THERAPEUTIC PRODUCTS von HEARTLEIN, MICHAEL W, TRECO, DOUGLAS A, HAUGE, BRIAN M, SELDON, RICHARD F

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