Therapeutic efficacy in a hemophilia B model using a biosynthetic mRNA liver depot system von DeRosa, F, Guild, B, Karve, S, Smith, L, Love, K, Dorkin, J R, Kauffman, K J, Zhang, J, Yahalom, B, Anderson, D G, Heartlein, M W

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Systemic delivery of mRNA and DNA to the lung using polymer-lipid nanoparticles von Kaczmarek, J, Patel, AK, Rhym, L, Capasso Palmiero, U, Bhat, B, Heartlein, M, DeRosa, F, Anderson, DG

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WS09.1 Development of a CFTR mRNA therapy capable of treating lung disease in all CFTR patients von Smith, L., Karve, S., De Rosa, F., Kaza, N., Shei, R.-J., Stanford, D., Askew, K., Heartlein, M., Rowe, S., Mccauley, T.

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Long-Term Production and Delivery of Human Growth Hormone In vivo von Heartlein, Michael W., Roman, Victoria A., Jiang, Ji-Lei, Sellers, Joan W., Zuliani, Antoinette M., Treco, Douglas A., Selden, Richard F.

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Optimization of a degradable polymer−lipid nanoparticle for potent systemic delivery of mRNA to the lung endothelium and immune cells von Kaczmarek, J, Kauffman, K, Fenton, O, Sadtler, K, Patel, AK, Heartlein, MW, DeRosa, F, Anderson, D

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Inhaled nanoformulated mRNA polyplexes for protein production in lung epithelium von Patel, AK, Kaczmarek, JC, Bose, S, Kauffman, KJ, Mir, F, Heartlein, MW, DeRosa, F, Langer, R, Anderson, DG

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Chromosome instability associated with human alphoid DNA transfected into the Chinese hamster genome von HEARTLEIN, M. W, KNOLL, J. H. M, LATT, S. A

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5-Bromodeoxyuridine-dependent increase in sister chromatid exchange formation in Bloom's syndrome is associated with reduction in topoisomerase II activity von Heartlein, .W., Tsuji, H., Latt, S.A.

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Molecular Characterization and Pharmacology of Epoetin Delta − The Only Erythropoietin Produced in a Human Cell Line von Pratt, Raymond D., Dowell, J., Shahrokh, Z., Flatman, S., Davies, M., Baycroft, A., Heartlein, M.

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Amplified inverted duplications within and adjacent to heterologous selectable DNA von HEARTLEIN, M. W, LATT, S. A

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Polymer-lipid nanoparticles for systemic delivery of mRNA to the lungs von Kaczmarek, JC, Patel, AK, Kauffman, KJ, Fenton, OS, Webber, MJ, Heartlein, MW, DeRosa, F, Anderson, DG

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Samuel A. Latt, 1938-1988: in memoriam von Allen, J, Disteche, C, Heartlein, M, Loveday, K, Schreck, R, Stetten, G

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Amplified inverted duplications within and adjacent to heterologous selectable DNAS von Heartlein, M.W., Latt, S.A.

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CELLS FOR PRODUCING RECOMBINANT IDURONATE-2-SULFATASE -2 von HEARTLEIN, MICHAEL M, BOLDOG, FERENC F

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Mutagenicity of municipal water obtained from an agricultural area von Heartlein, M. W., Demarini, D. M., Katz, A. J., Brockman, H. E., Means, J. C., Plewa, M. J.

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Breakage of the human Y-chromosome short arm between two blocks of tandemly repeated DNA sequences von Müller, Ulrich, Lalande, Marc, Donlon, Timothy A., Heartlein, Michael W.

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LIPID NANOPARTICLE COMPOSITIONS AND METHODS FOR MRNA DELIVERY MRNA von HEARTLEIN, MICHAEL M, DEROSA, FRANK F, GUILD, BRAYDON, CHARLES BC

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PULMONARY DELIVERY OF MRNA TO NON-LUNG TARGET CELLS MRNA von HEARTLEIN, MICHAEL M, DEROSA, FRANK F, GUILD, BRAYDON CHARLES BC, RUDOLPH, CARSTEN C, PLANK, CHRISTIAN C

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CFTR MRNA COMPOSITIONS AND RELATED METHODS AND USES CFTR MRNA von Michael HEARTLEIN M, Braydon Charles GUILD BC, Christian PLANK C, Lianne SMITH L, Frank DEROSA F, Carsten RUDOLPH C

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Chromosome Instability Associated with Human Alphoid DNA Transfected into the Chinese Hamster Genome von Heartlein, M. W., Knoll, J. H., Latt, S. A.

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