In Vivo Transduction of Cerebellar Purkinje Cells Using Adeno-Associated Virus Vectors von Kaemmerer, William F., Reddy, Rukmini G., Warlick, Christopher A., Hartung, Seth D., McIvor, R. Scott, Low, Walter C.

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Correction of metabolic, craniofacial, and neurologic abnormalities in MPS I mice treated at birth with adeno-associated virus vector transducing the human alpha-L-iduronidase gene von Hartung, Seth D, Frandsen, Joel L, Pan, Dao, Koniar, Brenda L, Graupman, Patrick, Gunther, Roland, Low, Walter C, Whitley, Chester B, McIvor, R Scott

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Correction of Metabolic, Craniofacial, and Neurologic Abnormalities in MPS I Mice Treated at Birth with Adeno-associated Virus Vector Transducing the Human [alpha]-L-Iduronidase Ge... von Hartung, Seth D, Frandsen, Joel L, Pan, Dao, Koniar, Brenda L, Graupman, Patrick, Gunther, Roland, Low, Walter C, Whitley, Chester B, Mcivor, R Scott

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Enzymatic correction and cross-correction of mucopolysaccharidosis type I fibroblasts by adeno-associated virus-mediated transduction of the α-L-iduronidase gene von HARTUNG, S. D, REDDY, R. G, WHITLEY, C. B, MCIVOR, R. S

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