Mitochondrial abnormalities in spinal and bulbar muscular atrophy von Ranganathan, Srikanth, Harmison, George G., Meyertholen, Kristin, Pennuto, Maria, Burnett, Barrington G., Fischbeck, Kenneth H.

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A small-molecule Nrf1 and Nrf2 activator mitigates polyglutamine toxicity in spinal and bulbar muscular atrophy von Bott, Laura C, Badders, Nisha M, Chen, Ke-Lian, Harmison, George G, Bautista, Elaine, Shih, Charles C-Y, Katsuno, Masahisa, Sobue, Gen, Taylor, J Paul, Dantuma, Nico P, Fischbeck, Kenneth H, Rinaldi, Carlo

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MiR-298 Counteracts Mutant Androgen Receptor Toxicity in Spinal and Bulbar Muscular Atrophy von Pourshafie, Naemeh, Lee, Philip R, Chen, Ke-lian, Harmison, George G, Bott, Laura C, Katsuno, Masahisa, Sobue, Gen, Burnett, Barrington G, Fischbeck, Kenneth H, Rinaldi, Carlo

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Insulinlike growth factor (IGF)-1 administration ameliorates disease manifestations in a mouse model of spinal and bulbar muscular atrophy von Rinaldi, Carlo, Bott, Laura C, Chen, Ke-lian, Harmison, George G, Katsuno, Masahisa, Sobue, Gen, Pennuto, Maria, Fischbeck, Kenneth H

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SMN mRNA and protein levels in peripheral blood : Biomarkers for SMA clinical trials von SUMNER, C. J, KOLB, S. J, HARMISON, G. G, JEFFRIES, N. O, SCHADT, K, FINKEL, R. S, DREYFUSS, G, FISCHBECK, K. H

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Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy von Winkelsas, Audrey M., Grunseich, Christopher, Harmison, George G., Chwalenia, Katarzyna, Rinaldi, Carlo, Hammond, Suzan M., Johnson, Kory, Bowerman, Melissa, Arya, Sukrat, Talbot, Kevin, Wood, Matthew J., Fischbeck, Kenneth H.

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motor neuron disease-associated mutation in p150[superscript Glued] perturbs dynactin function and induces protein aggregation von Levy, Jennifer R, Sumner, Charlotte J, Caviston, Juliane P, Tokito, Mariko K, Ranganathan, Srikanth, Ligon, Lee A, Wallace, Karen E, LaMonte, Bernadette H, Harmison, George G, Puls, Imke, Fischbeck, Kenneth H, Holzbaur, Erika L.F

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Protein kinase C gamma mutations in spinocerebellar ataxia 14 increase kinase activity and alter membrane targeting von Verbeek, D. S., Knight, M. A., Harmison, G. G., Fischbeck, K. H., Howell, B. W.

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Stem cell-derived motor neurons from spinal and bulbar muscular atrophy patients von Grunseich, Christopher, Zukosky, Kristen, Kats, Ilona R, Ghosh, Laboni, Harmison, George G, Bott, Laura C, Rinaldi, Carlo, Chen, Ke-lian, Chen, Guibin, Boehm, Manfred, Fischbeck, Kenneth H

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B2 attenuates polyglutamine-expanded androgen receptor toxicity in cell and fly models of spinal and bulbar muscular atrophy von Palazzolo, Isabella, Nedelsky, Natalia B., Askew, Caitlin E., Harmison, George G., Kasantsev, Aleksey G., Taylor, J. Paul, Fischbeck, Kenneth H., Pennuto, Maria

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Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents von Pourshafie, Naemeh, Lee, Philip R, Chen, Ke-Lian, Harmison, George G, Bott, Laura C, Fischbeck, Kenneth H, Rinaldi, Carlo

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Role of matrix protein in cytopathogenesis of vesicular stomatitis virus von BLONDEL, D, HARMISON, G. G, SCHUBERT, M

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Targeted infection of HIV-1 Env expressing cells by HIV(CD4/CXCR4) vectors reveals a potential new rationale for HIV-1 mediated down-modulation of CD4 von Ye, Zhiping, Harmison, George G, Ragheb, Jack A, Schubert, Manfred

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Primary structure of the vesicular stomatitis virus polymerase (L) gene: evidence for a high frequency of mutations von SCHUBERT, M, HARMISON, G. G, MEIER, E

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A motor neuron disease-associated mutation in p150Glued perturbs dynactin function and induces protein aggregation von Levy, Jennifer R, Sumner, Charlotte J, Caviston, Juliane P, Tokito, Mariko K, Ranganathan, Srikanth, Ligon, Lee A, Wallace, Karen E, LaMonte, Bernadette H, Harmison, George G, Puls, Imke, Fischbeck, Kenneth H, Holzbaur, Erika L F

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Mutation in CPT1C Associated With Pure Autosomal Dominant Spastic Paraplegia von Rinaldi, Carlo, Schmidt, Thomas, Situ, Alan J, Johnson, Janel O, Lee, Philip R, Chen, Ke-lian, Bott, Laura C, Fadó, Rut, Harmison, George H, Parodi, Sara, Grunseich, Christopher, Renvoisé, Benoît, Biesecker, Leslie G, De Michele, Giuseppe, Santorelli, Filippo M, Filla, Alessandro, Stevanin, Giovanni, Dürr, Alexandra, Brice, Alexis, Casals, Núria, Traynor, Bryan J, Blackstone, Craig, Ulmer, Tobias S, Fischbeck, Kenneth H

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Inducible and conditional inhibition of human immunodeficiency virus proviral expression by vesicular stomatitis virus matrix protein von Paik, S Y, Banerjea, A C, Harmison, G G, Chen, C J, Schubert, M

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Sexual Reassignment Fails to Prevent Kennedy’s Disease von Lanman, Tyler A., Bakar, Dara, Badders, Nisha M., Burke, Ailbhe, Kokkinis, Angela, Shrader, Joseph A., Joe, Galen O., Schindler, Alice B., Bott, Laura C., Harmison, George G., Taylor, J. Paul, Fischbeck, Kenneth H., Grunseich, Christopher

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Insertion of the human immunodeficiency virus CD4 receptor into the envelope of vesicular stomatitis virus particles von SCHUBERT, M, JOSHI, B, BLONDEL, D, HARMISON, GG

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Altered transcriptional regulation in cells expressing the expanded polyglutamine androgen receptor von Lieberman, Andrew P., Harmison, George, Strand, Andrew D., Olson, James M., Fischbeck, Kenneth H.

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