Repeated oral administration of chitosan/DNA nanoparticles delivers functional FVIII with the absence of antibodies in hemophilia A mice von DHADWAR, S. S., KIERNAN, J., WEN, J., HORTELANO, G.

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Encapsulated engineered myoblasts can cure Hurler syndrome: preclinical experiments in the mouse model von Piller Puicher, E, Tomanin, R, Salvalaio, M, Friso, A, Hortelano, G, Marin, O, Scarpa, M

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History, challenges and perspectives of cell microencapsulation von Orive, Gorka, Maria Hernández, Rose, Rodrı́guez Gascón, Alicia, Calafiore, Riccardo, Swi Chang, Thomas Ming, Vos, Paul de, Hortelano, Gonzalo, Hunkeler, David, Lacı́k, Igor, Luis Pedraz, José

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Cell encapsulation: Promise and progress von Pedraz, José Luis, Orive, Gorka, Hernández, Rosa María, Gascón, Alicia R, Calafiore, Riccardo, Chang, Thomas M.S, Vos, Paul De, Hortelano, Gonzalo, Hunkeler, David, Lacík, Igor, Shapiro, A.M. James

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Ex-Vivo Gene Therapy Approach for Continuous Delivery of BDNF and Its Potential Use for Neurological Disorders (P02.013) von Gomez-Vargas, A., Hortelano, G., Rathbone, M.

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Ex-Vivo Gene Therapy Approach for Continuous Delivery of BDNF and Its Potential Use for Neurological Disorders (IN6-1.008) von Gomez-Vargas, A., Hortelano, G., Rathbone, M.

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Sustained and therapeutic delivery of factor IX in nude haemophilia B mice by encapsulated C2C12 myoblasts: concurrent tumourigenesis von Hortelano, G., Wang, L., Xu, N., Ofosu, F. A.

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Non-viral transfer approaches for the gene therapy of mucopolysaccharidosis type II (Hunter syndrome) von Tomanin, R, Friso, A, Alba, S, Puicher, E Piller, Mennuni, C, Monica, N La, Hortelano, G, Zacchello, F, Scarpa, M

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Permeability of alginate microcapsules to secretory recombinant gene products von Awrey, D. E., Tse, M., Hortelano, G., Chang, P. L.

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Growth of recombinant fibroblasts in alginate microcapsules von Chang, P. L., Hortelano, G., Awrey, D. E., Tse, M.

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Delivery of a secretable adenosine deaminase through microcapsules--a novel approach to somatic gene therapy von Hughes, M, Vassilakos, A, Andrews, D W, Hortelano, G, Belmont, J W, Chang, P L

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Therapeutic approaches for haemophilia von Hortelano, Gonzalo, Ofosu, Frederick A

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An important role for the activation peptide domain in controlling factor IX levels in the blood of haemophilia B mice von Begbie, Megan E., Mamdani, Asif, Gataiance, Sharon, Eltringham-Smith, Louise J., Bhakta, Varsha, Hortelano, Gonzalo, Sheffield, William P.

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Nonviral Gene Therapy Approaches to Hemophilia von Gómez-Vargas, Andrew, Hortelano, Gonzalo

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Reduction of GAG storage in MPS II mouse model following implantation of encapsulated recombinant myoblasts von Friso, Adelaide, Tomanin, Rosella, Alba, Sabrina, Gasparotto, Nicoletta, Puicher, Elisabetta Piller, Fusco, Mariella, Hortelano, Gonzalo, Muenzer, Joseph, Marin, Oriano, Zacchello, Franco, Scarpa, Maurizio

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Effects of genetic fusion of factor IX to albumin on in vivo clearance in mice and rabbits von Sheffield, William P., Mamdani, Asif, Hortelano, Gonzalo, Gataiance, Sharon, Eltringham‐Smith, Louise, Begbie, Megan E., Leyva, Rina A., Liaw, Peter S., Ofosu, Frederick A.

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Delivery of Human Factor IX in Mice by Encapsulated Recombinant Myoblasts: A Novel Approach Towards Allogeneic Gene Therapy of Hemophilia B von Hortelano, Gonzalo, Al-Hendy, Ayman, Ofosu, Frederick A., Chang, Patricia L.

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Correction of the growth defect in dwarf mice with nonautologous microencapsulated myoblasts--an alternate approach to somatic gene therapy von al-Hendy, A, Hortelano, G, Tannenbaum, G S, Chang, P L

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Continuous antigenic stimulation system (CASS) as a new immunization strategy von Gomez-Vargas, Andrew, Rosenthal, Kenneth L., McDermott, Mark R., Hortelano, Gonzalo

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The in vivo delivery of heterologous proteins by microencapsulated recombinant cells von Chang, Patricia L, Van Raamsdonk, Jeremy M, Hortelano, Gonzalo, Barsoum, Susan C, MacDonald, Nicole C, Stockley, Tracy L

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