Biexponential R2 relaxometry for estimation of liver iron concentration in children: A better fit for high liver iron states von Barrera, Christian A., Khrichenko, Dmitry, Serai, Suraj D., Hartung, Helge D., Biko, David M., Otero, Hansel J.

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Protocol optimization for cardiac and liver iron content assessment using MRI: What sequence should I use? von Barrera, Christian A., Otero, Hansel J., Hartung, Helge D., Biko, David M., Serai, Suraj D.

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Genome architecture marked by retrotransposons modulates predisposition to DNA methylation in cancer von Estécio, Marcos R H, Gallegos, Juan, Vallot, Céline, Castoro, Ryan J, Chung, Woonbok, Maegawa, Shinji, Oki, Yasuhiro, Kondo, Yutaka, Jelinek, Jaroslav, Shen, Lanlan, Hartung, Helge, Aplan, Peter D, Czerniak, Bogdan A, Liang, Shoudan, Issa, Jean-Pierre J

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Severe hemolytic transfusion reaction due to anti-D in a D+ patient with sickle cell disease von Ipe, Tina S, Wilkes, Jennifer J, Hartung, Helge D, Westhoff, Connie M, Chou, Stella T, Friedman, David F

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Dehydrated hereditary stomatocytosis masquerading as MDS von Paessler, Michele, Hartung, Helge

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Pancytopenia in a patient with methylmalonic acidemia von MacFarland, Suzanne, Hartung, Helge

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SPRINTing to Innovation: Children’s Hospital of Philadelphia’s Strategic Approach to Discovering Its Untapped Innovation Potential von Hunter, Ryan Brandon, Winston, Flaura K., Dehel, Paul, Oh, Kelsey, Nicklas, Joshua, Hartung, Helge

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L‐leucine improves anemia and growth in patients with transfusion‐dependent Diamond‐Blackfan anemia: Results from a multicenter pilot phase I/II study from the Diamond‐Blackfan Ane... von Vlachos, Adrianna, Atsidaftos, Evangelia, Lababidi, Mohammad Lutfi, Muir, Ellen, Rogers, Zora R., Alhushki, Waseem, Bernstein, Jonathan, Glader, Bertil, Gruner, Barbara, Hartung, Helge, Knoll, Christine, Loew, Thomas, Nalepa, Grzegorz, Narla, Anupama, Panigrahi, Arun R., Sieff, Colin A., Walkovich, Kelly, Farrar, Jason E., Lipton, Jeffrey M.

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Effects of the COVID-19 Pandemic on Caregivers of Young Children with Sickle Cell Disease Enrolled in the Engage-HU Trial von Hood, Anna M, Hildenbrand, Aimee K, Rebitski, Joanna, Stallworth, Jasmine, Johnson, Yolanda, Gomes, Stacey, Whitacre, Catharine, Mara, Constance A, Shook, Lisa M, Quinn, Charles T., Raphael, Jean L., Yates, Amber M, Badawy, Sherif M., Thompson, Alexis A., Smith-Whitley, Kim, Hartung, Helge, King, Allison A., Creary, Susan E, Bhasin, Neha, Reader, Steven K, Meier, Emily R., Tubman, Venee N., Crosby, Lori E.

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Metformin for Treatment of Cytopenias in Children and Young Adults with Fanconi Anemia von Pollard, Jessica A., Furutani, Elissa M., Liu, Shanshan, Esrick, Erica B., Cohen, Laurie, Bledsoe, Jacob, Lu, Kun, Ramirez, Maria Jose, Surrallés, Jordi, Malsch, Maggie, Kuniholm, Ashley, Galvin, Ashley, Armant, Myriam, Kim, Annette S., Ballotti, Kaitlyn, Moreau, Lisa, Zhou, Yu, Babushok, Daria V., Boulad, Farid, Carroll, Clinton, Hartung, Helge, Hont, Amy, Nakano, Taizo A., Olson, Timothy S., Sze, Sei-Gyung K., Thompson, Alexis A, Wlodarski, Marcin W., Libermann, Towia A, D'Andrea, Alan D., Grompe, Markus, Weller, Edie A., Shimamura, Akiko

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Red blood cell alloimmunization in transfused patients with bone marrow failure syndromes von Cohen, Devin, Hartung, Helge, Evans, Perry, Friedman, David F., Chou, Stella T.

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Disrupted Lymphocyte Homeostasis in Hepatitis-Associated Acquired Aplastic Anemia Is Associated with Very Low Telomere Lengths von Grignon, Anne-Laure, Babushok, Daria V., Yimei, Li, Hartung, Helge, Lam, Ho-Sun, Bessler, Monica, Olson, Timothy S.

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Emergence of clonal hematopoiesis in the majority of patients with acquired aplastic anemia von Babushok, Daria V, Perdigones, Nieves, Perin, Juan C, Olson, Timothy S, Ye, Wenda, Roth, Jacquelyn J, Lind, Curt, Cattier, Carine, Li, Yimei, Hartung, Helge, Paessler, Michele E, Frank, Dale M, Xie, Hongbo M, Cross, Shanna, Cockroft, Joshua D, Podsakoff, Gregory M, Monos, Dimitrios, Biegel, Jaclyn A, Mason, Philip J, Bessler, Monica

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A Standardized Clinical Pathway to Decrease Hospital Admissions Among Febrile Children With Sickle Cell Disease von Ellison, Angela M, Smith Whitley, Kim, Kittick, Marlena, Schast, Aileen, Norris, Cynthia, Hartung, Helge, McKnight, Therese, Coyne, Erin, Lavelle, Jane

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Leucine for the Treatment of Transfusion Dependence in Patients with Diamond Blackfan Anemia von Vlachos, Adrianna, Atsidaftos, Evangelia, Muir, Ellen, Rogers, Zora R., Lababidi, Mohammad Lufti, Alhushki, Waseem, Farrar, Jason E., Glader, Bertil, Gruner, Barbara, Hartung, Helge, Knoll, Christine M., Nalepa, Grzegorz, Narla, Anupama, Panigrahi, Arun Ranjan, Sieff, Colin A., Walkovich, Kelly J., Lipton, Jeffrey M

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Retroviral insertional mutagenesis identifies genes that collaborate with NUP98-HOXD13 during leukemic transformation von SLAPE, Christopher, HARTUNG, Helge, LIN, Ying-Wei, BIES, Juraj, WOLFF, Linda, APIAN, Peter D

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Disrupted lymphocyte homeostasis in hepatitis‐associated acquired aplastic anemia is associated with short telomeres von Babushok, Daria V., Grignon, Anne‐Laure, Li, Yimei, Atienza, Jamie, Xie, Hongbo M., Lam, Ho‐Sun, Hartung, Helge, Bessler, Monica, Olson, Timothy S.

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Metformin for treatment of cytopenias in children and young adults with Fanconi anemia von Pollard, Jessica A, Furutani, Elissa, Liu, Shanshan, Esrick, Erica, Cohen, Laurie E, Bledsoe, Jacob, Liu, Chih-Wei, Lu, Kun, de Haro, Maria Jose Ramirez, Surrallés, Jordi, Malsch, Maggie, Kuniholm, Ashley, Galvin, Ashley, Armant, Myriam, Kim, Annette S, Ballotti, Kaitlyn, Moreau, Lisa, Zhou, Yu, Babushok, Daria, Boulad, Farid, Carroll, Clint, Hartung, Helge, Hont, Amy, Nakano, Taizo, Olson, Tim, Sze, Sei-Gyung, Thompson, Alexis A, Wlodarski, Marcin W, Gu, Xuesong, Libermann, Towia A, D'Andrea, Alan, Grompe, Markus, Weller, Edie, Shimamura, Akiko

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32. Genetic diagnosis of bone marrow failure syndromes: Strategies, yields, and challenges von Luo, Minjie, Surrey, Lea F., Zhong, Yiming, Gallo, Daniel J., Denenberg, Elizabeth H., Fanning, Elizabeth A., Lin, Fumin, Zhao, Xiaonan, Wu, Jinhua, Schubert, Jeffery, Zelley, Kristin, Paessler, Michele E., Oved, Joseph H., Hartung, Helge D., Lambert, Michele P., Kurre, Peter, Olson, Timothy S., Li, Marilyn M.

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26. Uncovering the genetic etiology of inherited bone marrow failure syndromes using a custom-designed NGS panel von Lin, Fumin, Chang, Fengqi, Cao, Kajia, Hartung, Helge, Lambert, Michele, Surrey, Lea, Luo, Minjie, Paessler, Michele, Zelley, Kristin, Gallo, Daniel, Denenberg, Elizabeth, Romasko, Edward, Zhao, Xiaonan, Olson, Tim, Li, Marilyn

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