A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa von Kocher, Thomas, Bischof, Johannes, Haas, Simone Alexandra, March, Oliver Patrick, Liemberger, Bernadette, Hainzl, Stefan, Illmer, Julia, Hoog, Anna, Muigg, Katharina, Binder, Heide-Marie, Klausegger, Alfred, Strunk, Dirk, Bauer, Johann Wolfgang, Cathomen, Toni, Koller, Ulrich

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Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa von Bischof, Johannes, March, Oliver Patrick, Liemberger, Bernadette, Haas, Simone Alexandra, Hainzl, Stefan, Petković, Igor, Leb-Reichl, Victoria, Illmer, Julia, Korotchenko, Evgeniia, Klausegger, Alfred, Hoog, Anna, Binder, Heide-Marie, Garcia, Marta, Duarte, Blanca, Strunk, Dirk, Larcher, Fernando, Reichelt, Julia, Guttmann-Gruber, Christina, Wally, Verena, Hofbauer, Josefina Piñón, Bauer, Johann Wolfgang, Cathomen, Toni, Kocher, Thomas, Koller, Ulrich

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A TRULY UNBIASED IN VITRO ASSAY TO PROFILE OFF-TARGET ACTIVITY OF ONE OR MORE TARGET-SPECIFIC PROGRAMMABLE NUCLEASES IN CELLS (ABNOBA-SEQ) von HAAS, Simone Alexandra, HILDENBEUTEL, Markus, CATHOMEN, Toni, ANDRIEUX, Geoffroy, BÖRRIES, Melanie, MUSSOLINO, Claudio

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VIRKELIG UVILDIG IN VITRO-UNDERSØGELSE TIL PROFILERING AF OFF-TARGET-AKTIVITET AF EN ELLER FLERE MÅLSPECIFIKKE PROGRAMMERBARE NUKLEASER I CELLER (ABNOBA-SEQ) von Mussolino, Claudio, HAAS, Simone Alexandra, HILDENBEUTEL, Markus, CATHOMEN, Toni, ANDRIEUX, Geoffroy, BÖRRIES, Melanie

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A TRULY UNBIASED IN VITRO ASSAY TO PROFILE OFF-TARGET ACTIVITY OF ONE OR MORE TARGET-SPECIFIC PROGRAMMABLE NUCLEASES IN CELLS (ABNOBA-SEQ) von HAAS, Simone Alexandra, HILDENBEUTEL, Markus, CATHOMEN, Toni, ANDRIEUX, Geoffroy, BÖRRIES, Melanie, MUSSOLINO, Claudio

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A TRULY UNBIASED IN VITRO ASSAY TO PROFILE OFF-TARGET ACTIVITY OF ONE OR MORE TARGET-SPECIFIC PROGRAMMABLE NUCLEASES IN CELLS (ABNOBA-SEQ) von HAAS, Simone Alexandra, HILDENBEUTEL, Markus, CATHOMEN, Toni, ANDRIEUX, Geoffroy, MUSSOLINO, Claudio, BOERRIES, Melanie

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A TRULY UNBIASED IN VITRO ASSAY TO PROFILE OFF-TARGET ACTIVITY OF ONE OR MORE TARGET-SPECIFIC PROGRAMMABLE NUCLEASES IN CELLS (ABNOBA-SEQ) von HAAS, Simone Alexandra, HILDENBEUTEL, Markus, CATHOMEN, Toni, ANDRIEUX, Geoffroy, BÖRRIES, Melanie, MUSSOLINO, Claudio

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Un ensayo in vitro verdaderamente imparcial para perfilar la actividad fuera de objetivo de una o más nucleasas programables específicas de objetivo en células (ABNOBA-SEQ) von HAAS, Simone Alexandra, HILDENBEUTEL, Markus, CATHOMEN, Toni, ANDRIEUX, Geoffroy, BÖRRIES, Melanie, MUSSOLINO, Claudio

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세포에서 하나 이상의 표적-특이적인 프로그램 가능한 뉴클레아제의 오프-타겟 활성을 프로파일링하는 진정한 편향되지 않은 시험관내 분석(ABNOBA-SEQ)... von MUSSOLINO CLAUDIO, ANDRIEUX GEOFFROY, CATHOMEN TONI, HILDENBEUTEL MARKUS, HAAS SIMONE ALEXANDRA, BOERRIES MELANIE

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DNA hypomethylation leads to cGAS‐induced autoinflammation in the epidermis von Beck, Mirjam A, Fischer, Heinz, Grabner, Lisa M, Groffics, Tamara, Winter, Mircea, Tangermann, Simone, Meischel, Tina, Zaussinger‐Haas, Barbara, Wagner, Patrick, Fischer, Carina, Folie, Christina, Arand, Julia, Schöfer, Christian, Ramsahoye, Bernard, Lagger, Sabine, Machat, Georg, Eisenwort, Gregor, Schneider, Stephanie, Podhornik, Alexandra, Kothmayer, Michael, Reichart, Ursula, Glösmann, Martin, Tamir, Ido, Mildner, Michael, Sheibani‐Tezerji, Raheleh, Kenner, Lukas, Petzelbauer, Peter, Egger, Gerda, Sibilia, Maria, Ablasser, Andrea, Seiser, Christian

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International cooperative study identifies treatment strategy in childhood ambiguous lineage leukemia von Hrusak, Ondrej, de Haas, Valerie, Stancikova, Jitka, Vakrmanova, Barbora, Janotova, Iveta, Mejstrikova, Ester, Capek, Vaclav, Trka, Jan, Zaliova, Marketa, Luks, Ales, Bleckmann, Kirsten, Möricke, Anja, Irving, Julie, Konatkowska, Benigna, Alexander, Thomas B., Inaba, Hiroto, Schmiegelow, Kjeld, Stokley, Simone, Zemanova, Zuzana, Moorman, Anthony V., Rossi, Jorge Gabriel, Felice, Maria Sara, Dalla-Pozza, Luciano, Morales, Jessa, Dworzak, Michael, Buldini, Barbara, Basso, Giuseppe, Campbell, Myriam, Cabrera, Maria Elena, Marinov, Neda, Elitzur, Sarah, Izraeli, Shai, Luria, Drorit, Feuerstein, Tamar, Kolenova, Alexandra, Svec, Peter, Kreminska, Olena, Rabin, Karen R., Polychronopoulou, Sophia, da Costa, Elaine, Marquart, Hanne Vibeke, Kattamis, Antonis, Ratei, Richard, Reinhardt, Dirk, Choi, John K., Schrappe, Martin, Stary, Jan

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Dual guidance structure for evaluation of patients with unclear diagnosis in centers for rare diseases (ZSE-DUO): study protocol for a controlled multi-center cohort study von Hebestreit, Helge, Zeidler, Cornelia, Schippers, Christopher, de Zwaan, Martina, Deckert, Jürgen, Heuschmann, Peter, Krauth, Christian, Bullinger, Monika, Berger, Alexandra, Berneburg, Mark, Brandstetter, Lilly, Deibele, Anna, Dieris-Hirche, Jan, Graessner, Holm, Gündel, Harald, Herpertz, Stephan, Heuft, Gereon, Lapstich, Anne-Marie, Lücke, Thomas, Maisch, Tim, Mundlos, Christine, Petermann-Meyer, Andrea, Müller, Susanne, Ott, Stephan, Pfister, Lisa, Quitmann, Julia, Romanos, Marcel, Rutsch, Frank, Schaubert, Kristina, Schubert, Katharina, Schulz, Jörg B, Schweiger, Susann, Tüscher, Oliver, Ungethüm, Kathrin, Wagner, Thomas O F, Haas, Kirsten

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Effect of the addition of a mental health specialist for evaluation of undiagnosed patients in centres for rare diseases (ZSE-DUO): a prospective, controlled trial with a two-phase... von Helge Hebestreit, Anne-Marie Lapstich, Lilly Brandstetter, Christian Krauth, Jürgen Deckert, Kirsten Haas, Lisa Pfister, Stefanie Witt, Christopher Schippers, Jan Dieris-Hirche, Tim Maisch, Oliver Tüscher, Lavinia Bârlescu, Alexandra Berger, Mark Berneburg, Vanessa Britz, Anna Deibele, Holm Graeßner, Harald Gündel, Gereon Heuft, Thomas Lücke, Christine Mundlos, Julia Quitmann, Frank Rutsch, Katharina Schubert, Jörg Bernhard Schulz, Susann Schweiger, Cornelia Zeidler, Lena Zeltner, Martina de Zwaan, Federica Akkaya, Christine Babka, Lisa Bannert, Anja Bärsch-Michelmann, Leonie Böhm, Folke Brinkmann, Monika Bullinger, Holger Cario, Moritz de Greck, Klaus-Michael Debatin, Katrin Dillmann-Jehn, Jutta Eymann, Julia Frisch, Anja Glode, Vega Gödecke, Corinna Grasemann, Eva Grauer, Astrid Haas, Lea Haisch, Isabell, Heinrich, Melissa Held, Julia Hennermann, Stephan Herpertz, Anne Herrmann-Werner, Julian Hett, Peter Heuschmann, Bettina Hilbig, Laura Holthöfer, Christiane Imhof, Florian Junne, Jan Kassubek, Kevin-Thomas Koschitzki, Heike Krassort, Birgit Kropff, Julia Kuhn, Philipp Latzko, Thomas Loew, Albert C. Ludolph, Torsten Meyer, Isabell Meyer dos Santos, Klaus Mohnike, Martina Monninger, Martin Mücke, Susanne Müller, Thomas Musacchio, Margret Nießen, Mariel Nöhre, Stephan Ott, Andrea Petermann-Meyer, Christina Pfeifer-Duck, Lea-Sophie Piduhn, Carina Rampp, Olaf Rieß, Kristina Schaubert, Annika Schmidt, Simone Schneider, Ludger Schoels, Martina Schwalba, Udo Selig, Alexandra Sroka, Toni Steinbüchel, Sebastian Stösser, Steffi Suchant, Kathrin Ungethüm, Matthias Vogel, Daniela Volk, Christoph Vollmuth, Solange Volnov, Thomas O.F. Wagner

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Acute Leukemia of Ambiguous Lineage: A Comprehensive Survival Analysis Enables Designing New Treatment Strategies von Hrusak, Ondrej, De Haas, Valerie, Luks, Ales, Janotova, Iveta, Mejstrikova, Ester, Bleckmann, Kirsten, Moricke, Anja, Irving, Julie, Konatkowska, Benigna, Alexander, Thomas B., Inaba, Hiroto, Schmiegelow, Kjeld, Stokley, Simone, Rossi, Jorge Gabriel, Felice, Maria Sara, Dalla-Pozza, Luciano, Morales, Jessa, Dworzak, Michael, Buldini, Barbara, Basso, Giuseppe, Campbell, Myriam, Cabrera, Maria Elena, Marinov, Neda, Elitzur, Sarah, Izraeli, Shai, Luria, Drorit, Feuerstein, Tamar, Kolenova, Alexandra, Svec, Peter, Kreminska, Elena, Rabin, Karen R., Polychronopoulou, Sophia, da Costa, Elaine, Marquart, Hanne Vibeke, Kattamis, Antonis, Ratei, Richard, Reinhardt, Dirk, Moorman, Anthony V, Schrappe, Martin, Stary, Jan

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Acute Leukemias of Ambiguous Lineage; Study on 247 Pediatric Patients von Hrusak, Ondrej, Luks, Ales, Janotova, Iveta, Mejstrikova, Ester, Vaskova, Martina, Bleckmann, Kirsten, Konatkowska, Benigna, Irving, Julie, Polgarova, Kamila, Inaba, Hiroto, Schmiegelow, Kjeld, Rossi, Jorge Gabriel, Felice, Maria Sara, Dalla-Pozza, Luciano, Morales, Jessa, Sartor, Mary, Dworzak, Michael, Moricke, Anja, Campbell, Myriam, Cabrera, Maria Elena, Marinov, Neda, Elitzur, Sarah, Izraeli, Shai, De Haas, Valerie, Kolenova, Alexandra, Svec, Peter, Kreminska, Elena, Stokley, Simone, Polychronopoulou, Sophia, da Costa, Elaine, Marquart, Hanne Vibeke, Kattamis, Antonis, Ratei, Richard, Reinhardt, Dirk, Jackson, Kathy, Moorman, Anthony V, Schrappe, Martin, Stary, Jan

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Incremental Context Creation and Its Effects on Semantic Query Precision von Dumitrescu, Alexandra, Santini, Simone

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Architectural Design for Data Migration Application Software von HEUSERMANN KNUT, YU TAO, RAMAN GURURAJ, KASCHNER ROLAND, SUDBRACK ANDREA, SCHOTT VOLKER, HEINZ STEPHAN, DUCHENE GUILLAUME, DEHN RENE, HEGER ACHIM, MARK ALEXANDRA, HARTEL MICHAEL, STEFFEN HEIKO, KIMME KARSTEN, HAAS CHRISTIAN, HE YONGBIN, DIETERICH SIMON, JORDA SIMONE, WEISSENBERGER CHRISTOF, REINELT KLAUS, GROTH KLAUS, BILDMAYER REINER, GABRIEL JAN, MEISWINKEL RALPH, JUNG MICHAEL, VOGT THOMAS, RINGL BENJAMIN, KOKKALIS PANAGIOTIS, BOEHRER CHRISTIAN, GAGLIARDI STEFANO, ROSENPFLANZER LUTZ, LAMPRECHT SABINE, ENENKIEL ACHIM, RUMIG JAN, LIVNEH YARON, FISCHBACH SANDRA, BARNBECK JOACHIM, RECCIUS ANDREAS, ROHDEMANN DIRK, FICATIER OLIVIER, MEYER PETRA, HAURY AXEL, REDDY ARUN KUMAR, KLEHR BENJAMIN, WESTBERG GESA, STORZ DIETMAR, SHAH AHMED ALI, POLAT EBRU, TATZEL STEFFEN, SONNEK MATHIAS, BORREILL HENRY, LE MAIRE RENE, PATIL SHAILAJA POLICE, MOREY MONIKA, SCHMITT JOCHEN

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