Generation of Isogenic Pluripotent Stem Cells Differing Exclusively at Two Early Onset Parkinson Point Mutations von Soldner, Frank, Laganière, Josée, Cheng, Albert W., Hockemeyer, Dirk, Gao, Qing, Alagappan, Raaji, Khurana, Vikram, Golbe, Lawrence I., Myers, Richard H., Lindquist, Susan, Zhang, Lei, Guschin, Dmitry, Fong, Lauren K., Vu, B. Joseph, Meng, Xiangdong, Urnov, Fyodor D., Rebar, Edward J., Gregory, Philip D., Zhang, H. Steve, Jaenisch, Rudolf

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LRRK2 mutations cause mitochondrial DNA damage in iPSC-derived neural cells from Parkinson's disease patients: Reversal by gene correction von Sanders, Laurie H, Laganière, Josée, Cooper, Oliver, Mak, Sally K, Vu, B. Joseph, Huang, Y. Anne, Paschon, David E, Vangipuram, Malini, Sundararajan, Ramya, Urnov, Fyodor D, Langston, J. William, Gregory, Philip D, Zhang, H. Steve, Greenamyre, J. Timothy, Isacson, Ole, Schüle, Birgitt

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Genome editing with engineered zinc finger nucleases von Gregory, Philip D, Urnov, Fyodor D, Rebar, Edward J, Holmes, Michael C, Zhang, H. Steve

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An engineered zinc finger protein activator of the endogenous glial cell line-derived neurotrophic factor gene provides functional neuroprotection in a rat model of Parkinson's dis... von Laganiere, Josee, Kells, Adrian P, Lai, Jeffrey T, Guschin, Dmitry, Paschon, David E, Meng, Xiangdong, Fong, Lauren K, Yu, Qi, Rebar, Edward J, Gregory, Philip D, Bankiewicz, Krystof S, Forsayeth, John, Zhang, H Steve

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A TALE nuclease architecture for efficient genome editing von Rebar, Edward J, Miller, Jeffrey C, Tan, Siyuan, Qiao, Guijuan, Barlow, Kyle A, Wang, Jianbin, Xia, Danny F, Meng, Xiangdong, Paschon, David E, Leung, Elo, Hinkley, Sarah J, Dulay, Gladys P, Hua, Kevin L, Ankoudinova, Irina, Cost, Gregory J, Urnov, Fyodor D, Zhang, H Steve, Holmes, Michael C, Zhang, Lei, Gregory, Philip D

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A Designed Zinc-finger Transcriptional Repressor of Phospholamban Improves Function of the Failing Heart von Zhang, H Steve, Liu, Dingang, Huang, Yan, Schmidt, Stefan, Hickey, Reed, Guschin, Dmitry, Su, Haili, Jovin, Ion S, Kunis, Mike, Hinkley, Sarah, Liang, Yuxin, Hinh, Linda, Spratt, S Kaye, Case, Casey C, Rebar, Edward J, Ehrlich, Barbara, Gregory, Philip D, Giordano, Frank J

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Locus-specific epigenetic remodeling controls addiction- and depression-related behaviors von Heller, Elizabeth A, Cates, Hannah M, Peña, Catherine J, Sun, Haosheng, Shao, Ningyi, Feng, Jian, Golden, Sam A, Herman, James P, Walsh, Jessica J, Mazei-Robison, Michelle, Ferguson, Deveroux, Knight, Scott, Gerber, Mark A, Nievera, Christian, Han, Ming-Hu, Russo, Scott J, Tamminga, Carol S, Neve, Rachael L, Shen, Li, Zhang, H Steve, Zhang, Feng, Nestler, Eric J

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Transduction of striatum and cortex tissues by adeno-associated viral vectors produced by herpes simplex virus- and baculovirus-based methods von Zhang, H. Steve, Kim, Eunmi, Lee, Slgirim, Ahn, Ik-Sung, Jang, Jae-Hyung

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Persistent repression of tau in the brain using engineered zinc finger protein transcription factors von Wegmann, Susanne, DeVos, Sarah L, Zeitler, Bryan, Marlen, Kimberly, Bennett, Rachel E, Perez-Rando, Marta, MacKenzie, Danny, Yu, Qi, Commins, Caitlin, Bannon, Riley N, Corjuc, Bianca T, Chase, Alison, Diez, Lisa, Nguyen, Hoang-Oanh B, Hinkley, Sarah, Zhang, Lei, Goodwin, Alicia, Ledeboer, Annemarie, Lam, Stephen, Ankoudinova, Irina, Tran, Hung, Scarlott, Nicholas, Amora, Rainier, Surosky, Richard, Miller, Jeffrey C, Robbins, Ashley B, Rebar, Edward J, Urnov, Fyodor D, Holmes, Michael C, Pooler, Amy M, Riley, Brigit, Zhang, H Steve, Hyman, Bradley T

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Ocular Gene Transfer with Self-Complementary AAV Vectors von Yokoi, Katsutoshi, Kachi, Shu, Zhang, H. Steve, Gregory, Philip D, Spratt, S. Kaye, Samulski, R. Jude, Campochiaro, Peter A

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Generation of Isogenic Pluripotent Stem Cells Differing Exclusively at Two Early Onset Parkinson Point Mutations von Soldner, Frank, Laganière, Josée, Cheng, Albert W., Hockemeyer, Dirk, Gao, Qing, Alagappan, Raaji, Khurana, Vikram, Golbe, Lawrence I., Myers, Richard H., Lindquist, Susan, Zhang, Lei, Guschin, Dmitry, Fong, Lauren K., Vu, B. Joseph, Meng, Xiangdong, Urnov, Fyodor D., Rebar, Edward J., Gregory, Philip D., Zhang, H. Steve, Jaenisch, Rudolf

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Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease von Zeitler, Bryan, Froelich, Steven, Marlen, Kimberly, Shivak, David A, Yu, Qi, Li, Davis, Pearl, Jocelynn R, Miller, Jeffrey C, Zhang, Lei, Paschon, David E, Hinkley, Sarah J, Ankoudinova, Irina, Lam, Stephen, Guschin, Dmitry, Kopan, Lexi, Cherone, Jennifer M, Nguyen, Hoang-Oanh B, Qiao, Guijuan, Ataei, Yasaman, Mendel, Matthew C, Amora, Rainier, Surosky, Richard, Laganiere, Josee, Vu, B Joseph, Narayanan, Anand, Sedaghat, Yalda, Tillack, Karsten, Thiede, Christina, Gärtner, Annette, Kwak, Seung, Bard, Jonathan, Mrzljak, Ladislav, Park, Larry, Heikkinen, Taneli, Lehtimäki, Kimmo K, Svedberg, Marie M, Häggkvist, Jenny, Tari, Lenke, Tóth, Miklós, Varrone, Andrea, Halldin, Christer, Kudwa, Andrea E, Ramboz, Sylvie, Day, Michelle, Kondapalli, Jyothisri, Surmeier, D James, Urnov, Fyodor D, Gregory, Philip D, Rebar, Edward J, Muñoz-Sanjuán, Ignacio, Zhang, H Steve

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Axonal transport of AAV9 in nonhuman primate brain von Green, F, Samaranch, L, Zhang, H S, Manning-Bog, A, Meyer, K, Forsayeth, J, Bankiewicz, K S

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A7 Drug discovery approach for rare neurological diseases: using novel zinc finger protein technology to develop potential therapy for huntington’s disease von Chiocco, Matthew, Choi, Vivian, Graham, Anne-Renee, Klatte, Debra, Francone, Omar, Thomson, David, Zeitler, Bryan, Froelich, Steven, Yu, Qi, Paschon, David E, Miller, Jeffrey C, Marlen, Kimberly, Rebar, Edward J, Urnov, Fyodor D, Gregory, Philip D, Steve Zhang, H

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Methods and compositions for treating huntington's disease von Zhang, H. Steve

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A Designed Zinc-finger Transcriptional Repressor of Phospholamban Improves Function of the Failing Heart

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VARIANTS OF CAS NUCLEASE von ZHENG, Qi, ZHANG, H. Steve

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VARIANTS OF CAS NUCLEASE von ZHENG, Qi, ZHANG, H. Steve

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Methods and compositions for treating Huntington's Disease von Zhang, H. Steve

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VARIANTS OF CAS NUCLEASE von ZHENG, Qi, ZHANG, H. Steve

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