268th ENMC workshop - Genetic diagnosis, clinical classification, outcome measures, and biomarkers in Facioscapulohumeral Muscular Dystrophy (FSHD): Relevance for clinical trials von Montagnese, Federica, de Valle, Katy, Lemmers, Richard J.L.F., Mul, Karlien, Dumonceaux, Julie, Voermans, Nicol, Tasca, Giorgio, Gomez-Rodulfo, Maria, Voermans, Nicol , Sacconi, Sabrina, Montagnese, Federica , de Valle, Katy, Lemmers, Richard, Dumonceaux, Julie, Camano, Pilar, Giardina, Emiliano, van der Stoep, Nienke, Burton-Jones, Sarah, Magdinier, Frederique, Race, Valerie, Hawkins, Sheila, Mejat, Alexandre, Oflazer, Piraye, Guizzaro, Lorenzo, Arjomand, Jamshid, Pereon, Yann, Ricci, Giulia, Bugiardini, Enrico, Belayew, Alexandra

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S8.4 Resting state cortical electroencephalographic rhythms are related to gray matter volume in subjects with mild cognitive impairment and Alzheimer's disease: an ADNI project von Lizio, R, Babiloni, C, Carducci, F, Vecchio, F, Baglieri, A, Bernardini, S, Boccardi, M, Bozzao, A, Buttinelli, C, Esposito, F, Giubilei, F, Guizzaro, A, Marino, S, Montella, P, Quattrocchi, C.C, Redolfi, A, Soricelli, A, Tedeschi, G, Ferri, R, Triggiani, A.I, Rossi-Fedele, G, Parisi, L, Vernieri, F, Rossini, P.M, Frisoni, G.B

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Health-related quality of life in epilepsy: Findings obtained with a new Italian instrument von Piazzini, Ada, Beghi, Ettore, Turner, Katherine, Ferraroni, Monica

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Daily fluctuation of plasma levels with conventional and controlled-release carbamazepine: correlation with adverse effects von Bareggi, S R, Tata, M R, Guizzaro, A, Pirola, R, Parisi, A, Monza, C G

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Ipoplasia del verme cerebellare ed epilessia von Muras, I., Volpe, E., Guizzaro, A., Bravaccio, F., Bernini, F.P.

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Be open about drug failures to speed up research von Alteri, Enrica, Guizzaro, Lorenzo

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Developing medicines for the pre-symptomatic stage of degenerative neurological conditions: Challenges and opportunities von Mészáros, L., Guizzaro, L.

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Estimators for handling COVID‐19‐related intercurrent events with a hypothetical strategy von Lasch, Florian, Guizzaro, Lorenzo

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The Impact of COVID‐19 on the Initiation of Clinical Trials in Europe and the United States von Lasch, Florian, Psarelli, Eftychia‐Eirini, Herold, Ralf, Mattsson, Andrea, Guizzaro, Lorenzo, Pétavy, Frank, Schiel, Anja

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The association of financial difficulties with clinical outcomes in cancer patients: secondary analysis of 16 academic prospective clinical trials conducted in Italy von Perrone, F., Jommi, C., Di Maio, M., Gimigliano, A., Gridelli, C., Pignata, S., Ciardiello, F., Nuzzo, F., de Matteis, A., Del Mastro, L., Bryce, J., Daniele, G., Morabito, A., Piccirillo, M.C., Rocco, G., Guizzaro, L., Gallo, C.

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Beyond “Intent‐to‐treat” and “Per protocol”: Improving assessment of treatment effects in clinical trials through the specification of an estimand von Pétavy, Frank, Guizzaro, Lorenzo, Antunes dos Reis, Inês, Teerenstra, Steven, Roes, Kit C.B.

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Estimands in CNS trials – A review of strategies for addressing intercurrent events von Mészáros, Lisa, Lasch, Florian, Delafont, Bruno, Guizzaro, Lorenzo

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Hamilton scale and MADRS are interchangeable in meta-analyses but can disagree at trial level von Guizzaro, Lorenzo, Morgan, David Dickinson Vaughan, Falco, Andrea, Gallo, Ciro

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The opportunity of patient-journey studies for academic clinical research in oncology von Perrone, Francesco, Di Liello, Raimondo, Gargiulo, Piera, Arenare, Laura, Guizzaro, Lorenzo, Chiodini, Paolo, Gallo, Ciro, Piccirillo, Maria Carmela

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A qualitative analysis and development of a conceptual model assessing financial toxicity in cancer patients accessing the universal healthcare system von Riva, Silvia, Efficace, Fabio, Di Maio, Massimo, Bryce, Jane, Del Campo, Laura, De Lorenzo, Francesco, Frontini, Luciano, Giannarelli, Diana, Gitto, Lara, Iannelli, Elisabetta, Jommi, Claudio, Montesarchio, Vincenzo, Traclò, Francesca, Vaccaro, Concetta Maria, Arenare, Laura, Canzanella, Giuliana, Gimigliano, Anna, Romano, Fiorella, Savio, Alfonso, Sparavigna, Lucia, Piccirillo, Maria Carmela, Guizzaro, Lorenzo, Gallo, Ciro, Perrone, Francesco

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Challenges in drug development for central nervous system disorders: a European Medicines Agency perspective von Butlen-Ducuing, Florence, Pétavy, Frank, Guizzaro, Lorenzo, Zienowicz, Malgorzata, Salmonson, Tomas, Haas, Manuel, Corruble, Emmanuelle, Alteri, Enrica

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Cross-sectional study to develop and describe psychometric characteristics of a patient-reported instrument (PROFFIT) for measuring financial toxicity of cancer within a public hea... von Riva, Silvia, Arenare, Laura, Di Maio, Massimo, Efficace, Fabio, Montesarchio, Vincenzo, Frontini, Luciano, Giannarelli, Diana, Bryce, Jane, Del Campo, Laura, De Lorenzo, Francesco, Iannelli, Elisabetta, Traclò, Francesca, Gitto, Lara, Jommi, Claudio, Vaccaro, Concetta Maria, Barberio, Daniela, Cinieri, Saverio, Porta, Camillo, Del Mastro, Lucia, Zagonel, Vittorina, Cogoni, Alessio Aligi, Bordonaro, Roberto, Gimigliano, Anna, Piccirillo, Maria Carmela, Guizzaro, Lorenzo, Gallo, Ciro, Perrone, Francesco

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Regulatory watch: Challenges in drug development for central nervous system disorders: a European Medicines Agency perspective von Butlen-Ducuing, Florence, Pétavy, Frank, Guizzaro, Lorenzo, Zienowicz, Malgorzata, Haas, Manuel, Alteri, Enrica, Salmonson, Tomas, Corruble, Emmanuelle

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Resting state cortical electroencephalographic rhythms are related to gray matter volume in subjects with mild cognitive impairment and Alzheimer's disease von Babiloni, Claudio, Carducci, Filippo, Lizio, Roberta, Vecchio, Fabrizio, Baglieri, Annalisa, Bernardini, Silvia, Cavedo, Enrica, Bozzao, Alessandro, Buttinelli, Carla, Esposito, Fabrizio, Giubilei, Franco, Guizzaro, Antonio, Marino, Silvia, Montella, Patrizia, Quattrocchi, Carlo C., Redolfi, Alberto, Soricelli, Andrea, Tedeschi, Gioacchino, Ferri, Raffaele, Rossi-Fedele, Giancarlo, Ursini, Francesca, Scrascia, Federica, Vernieri, Fabrizio, Pedersen, Torleif Jan, Hardemark, Hans-Goran, Rossini, Paolo M., Frisoni, Giovanni B.

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Clinically Manifest Infections Do Not Increase the Relapse Risk in People with Multiple Sclerosis Treated with Disease-Modifying Therapies: A Prospective Study von Miele, Giuseppina, Cepparulo, Simone, Abbadessa, Gianmarco, Lavorgna, Luigi, Sparaco, Maddalena, Simeon, Vittorio, Guizzaro, Lorenzo, Bonavita, Simona

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