Long-Term Patient-Reported Outcomes Following Treatment with betibeglogene autotemcel in Patients with Transfusion-Dependent β-Thalassemia von Locatelli, Franco, Walters, Mark C., Kwiatkowski, Janet L., Cavazzana, Marina, Hongeng, Suradej, Porter, John B., Thrasher, Adrian J., Kulozik, Andreas E., Thuret, Isabelle, Rasko, John E.J., Yannaki, Evangelia, Sauer, Martin G., Ali, Shamshad, Thakar, Himal, Gruppioni, Katiana, Thompson, Alexis A.

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Clinical Outcomes after Allogeneic Hematopoietic Stem Cell Transplantation in Patients with Transfusion-Dependent β-Thalassemia Treated at the Bambino Gesù Children's Hospital, Rom... von Merli, Pietro, Ruggeri, Annalisa, Algeri, Mattia, Li Pira, Giuseppina, Ceglie, Giulia, Gruppioni, Katiana, Kommera, Sanjeev, Maa, Jenfue, Locatelli, Franco

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Sustained Efficacy, Safety, and Improved Quality of Life in Adult and Pediatric Patients with Transfusion-Dependent β-Thalassemia up to 9 Years Post Treatment with Betibeglogene Au... von Thompson, Alexis A., Olson, Timothy S., Walters, Mark C., Porter, John B., Schneiderman, Jennifer, Hongeng, Suradej, Kulozik, Andreas, Cavazzana, Marina, Sauer, Martin G., Thrasher, Adrian J., Thuret, Isabelle, Lal, Ashutosh, Rasko, John E. J., Yannaki, Evangelia, Ali, Shamshad, Tao, Gloria, Thakar, Himal L., Deora, Ami, Gruppioni, Katiana, Colvin, Richard A., Locatelli, Franco, Kwiatkowski, Janet L.

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Efficacy, Safety, and Health-Related Quality of Life (HRQOL) in Patients with Sickle Cell Disease (SCD) Who Have Received Lovotibeglogene Autotemcel (Lovo-cel) Gene Therapy: Up to... von Kanter, Julie, Thompson, Alexis A., Kwiatkowski, Janet L., Parikh, Suhag, Mapara, Markus, Rifkin-Zenenberg, Stacey, Aygun, Banu, Kasow, Kimberly A., Gupta, Ashish O., Zhang, Lixin, Sheldon-Waniga, Emily, Gallagher, Meghan, Gruppioni, Katiana, Chawla, Anjulika, Elliot, Heidi, Pierciey, Francis J., Walters, Mark C., Tisdale, John F.

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Improvement in Health-Related Quality of Life Following Treatment with Betibeglogene Autotemcel in Patients with Transfusion-Dependent β-Thalassemia Enrolled in Phase 3 Studies von Kwiatkowski, Janet L., Locatelli, Franco, Walters, Mark C., Porter, John B., Hongeng, Suradej, Yannaki, Evangelia, Kulozik, Andreas E., Sauer, Martin G., Thrasher, Adrian J., Thuret, Isabelle, Lal, Ashutosh, Guo, Ruiting, Colvin, Richard A., Gruppioni, Katiana, Thompson, Alexis A.

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Sustained Efficacy and Safety in Adult and Pediatric Patients with Transfusion-Dependent β-Thalassemia up to 9 Years Post Treatment with Betibeglogene Autotemcel (Beti-cel) von Walters, Mark C., Thompson, Alexis A., Olson, Timothy S., Porter, John B., Schneiderman, Jennifer, Hongeng, Suradej, Kulozik, Andreas E., Cavazzana, Marina, Sauer, Martin G., Thrasher, Adrian J., Thuret, Isabelle, Lal, Ashutosh, Rasko, John E.J., Yannaki, Evangelia, Ali, Shamshad, Tao, Ge, Thakar, Himal L., Deora, Ami, Gruppioni, Katiana, Colvin, Richard A., Locatelli, Franco, Kwiatkowski, Janet L.

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Efficacy and Safety in Patients (Pts) with Sickle Cell Disease (SCD) Who Have Received Lovotibeglogene Autotemcel (Lovo-cel) Gene Therapy: Up to 60 Months of Follow-up von Kanter, Julie, Thompson, Alexis A., Kwiatkowski, Janet L., Parikh, Suhag, Mapara, Markus Y., Rifkin-Zenenberg, Stacey, Aygun, Banu, Kasow, Kimberly A., Gupta, Ashish O., Zhang, Lixin, Sheldon-Waniga, Emily, Gallagher, Meghan, Gruppioni, Katiana, Chawla, Anjulika, Elliot, Heidi, Pierciey, Francis J., Walters, Mark C., Tisdale, John F.

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