Industry Perspective on Artificial Intelligence/Machine Learning in Pharmacovigilance von Kassekert, Raymond, Grabowski, Neal, Lorenz, Denny, Schaffer, Claudia, Kempf, Dieter, Roy, Promit, Kjoersvik, Oeystein, Saldana, Griselda, ElShal, Sarah

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Using social media in safety signal management: is it reliable? von Rees, Sue, Mian, Sadiqa, Grabowski, Neal

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Therapeutic goals in the treatment of Gaucher disease von Pastores, Gregory M., Weinreb, Neal J., Aerts, Hans, Andria, Generoso, Cox, Timothy M., Giralt, Manuel, Grabowski, Gregory A., Mistry, Pramod K., Tylki-Szymańska, Anna

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Shifting perceptions of rapid temperature changes’ effects on marine fisheries, 1945–2017 von McClenachan, Loren, Grabowski, Jonathan H., Marra, Madison, McKeon, C. Seabird, Neal, Benjamin P., Record, Nicholas R., Scyphers, Steven B.

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Gaucher disease and SARS-CoV-2 infection: Emerging management challenges von Mistry, Pramod, Balwani, Manisha, Barbouth, Deborah, Burrow, T. Andrew, Ginns, Edward I., Goker-Alpan, Ozlem, Grabowski, Gregory A., Kartha, Reena V., Kishnani, Priya S., Lau, Heather, Lee, Chung U., Lopez, Grisel, Maegawa, Gustavo, Packman, Seymour, Prada, Carlos, Rosenbloom, Barry, Lal, Tamanna Roshan, Schiffmann, Rapheal, Weinreb, Neal, Sidransky, Ellen

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Screening, patient identification, evaluation, and treatment in patients with Gaucher disease: Results from a Delphi consensus von Kishnani, Priya S., Al-Hertani, Walla, Balwani, Manisha, Göker-Alpan, Özlem, Lau, Heather A., Wasserstein, Melissa, Weinreb, Neal J., Grabowski, Gregory

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The HARMONY Trial: Combined Ranolazine and Dronedarone in the Management of Paroxysmal Atrial Fibrillation: Mechanistic and Therapeutic Synergism von Reiffel, James A, Camm, A John, Belardinelli, Luiz, Zeng, Dewan, Karwatowska-Prokopczuk, Ewa, Olmsted, Ann, Zareba, Wojciech, Rosero, Spencer, Kowey, Peter

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Long-Acting Risperidone and Oral Antipsychotics in Unstable Schizophrenia von Rosenheck, Robert A, Krystal, John H, Lew, Robert, Barnett, Paul G, Fiore, Louis, Valley, Danielle, Thwin, Soe Soe, Vertrees, Julia E, Liang, Matthew H

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A validated disease severity scoring system for adults with type 1 Gaucher disease von Weinreb, Neal J., Cappellini, Maria D., Cox, Timothy M., Giannini, Edward H., Grabowski, Gregory A., Hwu, Wuh-Liang, Mankin, Henry, Martins, Ana Maria, Sawyer, Carolyn, Vom Dahl, Stephan, Yeh, Michael S., Zimran, Ari

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Roscoe Owen Brady, MD: Remembrances of co-investigators and colleagues von Desnick, Robert J, Barton, Norman W, Furbish, Scott, Grabowski, Gregory A, Karlsson, Stefan, Kolodny, Edwin H, Medin, Jeffrey A, Murray, Gary J, Mistry, Pramod K, Patterson, Marc C, Schiffmann, Raphael, Weinreb, Neal J

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Guidance on the use of miglustat for treating patients with type 1 Gaucher disease von Weinreb, Neal J., Barranger, John A., Charrow, Joel, Grabowski, Gregory A., Mankin, Henry J., Mistry, Pramod

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Position statement: National Gaucher Foundation Medical Advisory Board, January 7, 2014 von Barranger, John A., Brady, Roscoe O., Grabowski, Gregory A., Mankin, Henry, Mistry, Pramod K., Weinreb, Neal J.

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COVID-19 patient impact: A survey of the Gaucher community involving patients, caregivers and family members based in the US to determine impact of the pandemic von Ryan, Emory, Lopez, Grisel, Balwani, Manisha, Barbouth, Deborah, Burrow, T. Andrew, Ginns, Edward, Goker-Alpan, Ozlem, Grabowski, Gregory, Kartha, Reena, Kishnani, Priya, Lau, Heather, Lee, Chung, Mistry, Pramod, Maegawa, Gustavo, Packman, Seymour, Prada, Carlos, Rosenbloom, Barry, Lal, Tamanna Roshan, Schiffmann, Raphael, Weinreb, Neal, Sidransky, Ellen

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A multicenter open-label treatment protocol (HGT-GCB-058) of velaglucerase alfa enzyme replacement therapy in patients with Gaucher disease type 1: safety and tolerability von Pastores, Gregory M., Rosenbloom, Barry, Weinreb, Neal, Goker-Alpan, Ozlem, Grabowski, Gregory, Cohn, Gabriel M., Zahrieh, David

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Gaucher disease: Resetting the clinical and scientific agenda von Mistry, Pramod K., Weinreb, Neal J., Brady, Roscoe O., Grabowski, Gregory A.

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Weighted median filters with sigma-delta modulation encoding von Arce, G.R., Grabowski, N.A., Gallagher, N.C.

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How do clinical trial participants compare to other patients with schizophrenia? von Barnett, Paul G, Scott, Jennifer Y, Rosenheck, Robert A

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Challenges in the design and conduct of controlled clinical effectiveness trials in schizophrenia von Rosenheck, Robert A, Krystal, John H, Lew, Robert, Barnett, Paul G, Thwin, Soe Soe, Fiore, Louis, Valley, Danielle, Huang, Grant D, Neal, Carla, Vertrees, Julia E, Liang, Matthew H

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Enzyme Replacement Therapy in Gaucher Disease: Beneficial Effects on Bone Crisis and Bone Pain von Grabowski, Gregory, Charrow, Joel, Weinreb, Neal J., Dulisse, Brian

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Pharmacological Chaperone Therapy for the Treatment of Gaucher Disease: Results of Phase 1 Clinical Trials and a Clinical Ex Vivo Response Study with a Survey of Blood Markers for... von Weinreb, Neal J., Grabowski, G.A., Pastores, G.M., Fernhoff, P.M., Kaplan, P.B., Palling, D., Pine, C.W., Raines, B.E., Insinga, F., Lockhart, D.J., Do, H.V., Wustman, B.A.

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