Delivery of oligonucleotide‐based therapeutics: challenges and opportunities von Hammond, Suzan M, Aartsma‐Rus, Annemieke, Alves, Sandra, Borgos, Sven E, Buijsen, Ronald A M, Collin, Rob W J, Covello, Giuseppina, Denti, Michela A, Desviat, Lourdes R, Echevarría, Lucía, Foged, Camilla, Gaina, Gisela, Garanto, Alejandro, Goyenvalle, Aurelie T, Guzowska, Magdalena, Holodnuka, Irina, Jones, David R, Krause, Sabine, Lehto, Taavi, Montolio, Marisol, Van Roon‐Mom, Willeke, Arechavala‐Gomeza, Virginia

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Delivery of oligonucleotide‐based therapeutics: challenges and opportunities von Hammond, Suzan M., Aartsma-Rus, Annemieke, Alves, Sandra, Borgos, Sven Even F., Buijsen, Ronald A.M, Collin, Rob W.J., Covello, Giuseppina, Denti, Michela A., Desviat, Lourdes R., Echevarria, Lucia, Foged, Camilla, Gaina, Gisela, Garanto, Alejandro, Goyenvalle, Aurelie T., Guzowska, Magdalena, Holodnuka, Irina, Jones, David R., Krause, Sabine, Lehto, Taavi, Montolio, Marisol, Van Roon-Mom, Willeke, Arechavala-Gomeza, Virginia

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Delivery of oligonucleotide-based therapeutics: challenges and opportunities von Hammond, Suzan M., Aartsma-Rus, Annemieke, Alves, Sandra, Borgos, Sven Even F., Buijsen, Ronald A.M., Collin, Rob W.J., Covello, Giuseppina, Denti, Michela A., Desviat, Lourdes R., Echevarria, Lucia, Foged, Camilla, Gaina, Gisela, Garanto, Alejandro, Goyenvalle, Aurelie T., Guzowska, Magdalena, Holodnuka, Irina, Jones, David R., Krause, Sabine, Lehto, Taavi, Van Roon-Mom, Willeke, Arechavala-Gomeza, Virginia

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Delivery of oligonucleotide-based therapeutics: challenges and opportunities von Hammond, Suzan M, Aartsma-Rus, Annemieke, Alves, Sandra, Borgos, Sven Even F, Buijsen, Ronald A.M, Collin, Rob W.J, Covello, Giuseppina, Denti, Michela A, Desviat, Lourdes R, Echevarria, Lucia, Foged, Camilla, Gaina, Gisela, Garanto, Alejandro, Goyenvalle, Aurelie T, Guzowska, Magdalena, Holodnuka, Irina, Jones, David R, Krause, Sabine, Lehto, Taavi, Van Roon-Mom, Willeke, Arechavala-Gomeza, Virginia

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Delivery of oligonucleotide‐based therapeutics: challenges and opportunities von Hammond, Suzan M, Aartsma-Rus, Annemieke, Alves, Sandra, Borgos, Sven Even F, Buijsen, Ronald A.M, Collin, Rob W.J, Covello, Giuseppina, Denti, Michela A, Desviat, Lourdes R, Echevarria, Lucia, Foged, Camilla, Gaina, Gisela, Garanto, Alejandro, Goyenvalle, Aurelie T, Guzowska, Magdalena, Holodnuka, Irina, Jones, David R, Krause, Sabine, Lehto, Taavi, Montolio, Marisol, Van Roon-Mom, Willeke, Arechavala-Gomeza, Virginia

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Exon-skipping advances for Duchenne muscular dystrophy von Echevarría, Lucía, Aupy, Philippine, Goyenvalle, Aurélie

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Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers von Goyenvalle, Aurélie, Griffith, Graziella, Babbs, Arran, Andaloussi, Samir El, Ezzat, Kariem, Avril, Aurélie, Dugovic, Branislav, Chaussenot, Rémi, Ferry, Arnaud, Voit, Thomas, Amthor, Helge, Bühr, Claudia, Schürch, Stefan, Wood, Matthew J A, Davies, Kay E, Vaillend, Cyrille, Leumann, Christian, Garcia, Luis

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The Use of Antisense Oligonucleotides for the Treatment of Duchenne Muscular Dystrophy von Relizani, Karima, Goyenvalle, Aurelie

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RNA-targeted drugs for neuromuscular diseases von Ferlini, Alessandra, Goyenvalle, Aurelie, Muntoni, Francesco

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Partial Restoration of Brain Dystrophin and Behavioral Deficits by Exon Skipping in the Muscular Dystrophy X‐Linked (mdx) Mouse von Zarrouki, Faouzi, Relizani, Karima, Bizot, Flavien, Tensorer, Thomas, Garcia, Luis, Vaillend, Cyrille, Goyenvalle, Aurélie

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Use of Tricyclo-DNA Antisense Oligonucleotides for Exon Skipping von Relizani, Karima, Goyenvalle, Aurelie

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Impact of the Inhibition of Organic Anion Transporter on Tricyclo-DNA-Mediated Exon Skipping in the mdx Mouse Model von Bizot, Flavien, Tensorer, Thomas, Garcia, Luis, Goyenvalle, Aurélie

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Rescue of Dystrophic Muscle through U7 snRNA-Mediated Exon Skipping von Goyenvalle, Aurélie, Vulin, Adeline, Fougerousse, Françoise, Leturcq, France, Kaplan, Jean-Claude, Garcia, Luis, Danos, Olivier

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The bench to bedside journey of tricyclo-DNA antisense oligonucleotides for the treatment of Duchenne muscular dystrophy von Blitek, Mathilde, Phongsavanh, Xaysongkhame, Goyenvalle, Aurélie

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Palmitic acid conjugation enhances potency of tricyclo-DNA splice switching oligonucleotides von Relizani, Karima, Echevarría, Lucía, Zarrouki, Faouzi, Gastaldi, Cécile, Dambrune, Chloe, Aupy, Philippine, Haeberli, Adrian, Komisarski, Marek, Tensorer, Thomas, Larcher, Thibaut, Svinartchouk, Fedor, Vaillend, Cyrille, Garcia, Luis, Goyenvalle, Aurélie

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Current Status of Antisense Oligonucleotide-Based Therapy in Neuromuscular Disorders (Aug, 10.1007/s40265-020-01363-3, 2020) von Bizot, Flavien, Vulin, Adeline, Goyenvalle, Aurelie

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RNA splicing modulation: Therapeutic progress and perspectives von Saoudi, Amel, Goyenvalle, Aurelie

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Emotional behavior and brain anatomy of the mdx52 mouse model of Duchenne muscular dystrophy von Saoudi, Amel, Zarrouki, Faouzi, Sebrie, Catherine, Izabelle, Charlotte, Goyenvalle, Aure'lie, Vaillend, Cyrille

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Current Status of Antisense Oligonucleotide-Based Therapy in Neuromuscular Disorders von Bizot, Flavien, Vulin, Adeline, Goyenvalle, Aurélie

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Lowering Mutant Huntingtin Using Tricyclo-DNA Antisense Oligonucleotides As a Therapeutic Approach for Huntington's Disease von Imbert, Marine, Blandel, Florence, Leumann, Christian, Garcia, Luis, Goyenvalle, Aurelie

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