ELX-02 Generates Protein via Premature Stop Codon Read-Through without Inducing Native Stop Codon Read-Through Proteins von Crawford, Daniel K., Alroy, Iris, Sharpe, Neal, Goddeeris, Matthew M., Williams, Greg

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LARGE glycans on dystroglycan function as a tunable matrix scaffold to prevent dystrophy von Goddeeris, Matthew M., Wu, Biming, Venzke, David, Yoshida-Moriguchi, Takako, Saito, Fumiaki, Matsumura, Kiichiro, Moore, Steven A., Campbell, Kevin P.

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An HMGA2-IGF2BP2 Axis Regulates Myoblast Proliferation and Myogenesis von Li, Zhizhong, Gilbert, Jason A., Zhang, Yunyu, Zhang, Minsi, Qiu, Qiong, Ramanujan, Krishnan, Shavlakadze, Tea, Eash, John K., Scaramozza, Annarita, Goddeeris, Matthew M., Kirsch, David G., Campbell, Kevin P., Brack, Andrew S., Glass, David J.

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Independent requirements for Hedgehog signaling by both the anterior heart field and neural crest cells for outflow tract development von Goddeeris, Matthew M, Schwartz, Robert, Klingensmith, John, Meyers, Erik N

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Intracardiac septation requires hedgehog-dependent cellular contributions from outside the heart von Goddeeris, Matthew M, Rho, Silvia, Petiet, Alexandra, Davenport, Chandra L, Johnson, G Allan, Meyers, Erik N, Klingensmith, John

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High-Resolution Magnetic Resonance Histology of the Embryonic and Neonatal Mouse: A 4D Atlas and Morphologic Database von Petiet, Alexandra E., Kaufman, Matthew H., Goddeeris, Matthew M., Brandenburg, Jeffrey, Elmore, Susan A., Johnson, G. Allan

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Genetics of cystogenesis in base-edited human organoids reveal therapeutic strategies for polycystic kidney disease von Vishy, Courtney E., Thomas, Chardai, Vincent, Thomas, Crawford, Daniel K., Goddeeris, Matthew M., Freedman, Benjamin S.

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Targeting G542X CFTR nonsense alleles with ELX-02 restores CFTR function in human-derived intestinal organoids von Crawford, Daniel K., Mullenders, Jasper, Pott, Johanna, Boj, Sylvia F., Landskroner-Eiger, Shira, Goddeeris, Matthew M.

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Intravitreal administration of small molecule read-through agents demonstrate functional activity in a nonsense mutation mouse model von Crawford, Daniel K., Vanlandingham, Phillip, Schneider, Susan, Goddeeris, Matthew M.

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Highly selective peroxisome proliferator-activated receptor δ (PPARδ) modulator demonstrates improved safety profile compared to GW501516 von Lagu, Bharat, Kluge, Arthur F., Goddeeris, Matthew M., Tozzo, Effie, Fredenburg, Ross A., Chellur, Shekar, Senaiar, Ramesh S., Jaleel, Mahaboobi, Babu, D. Ravi Krishna, Tiwari, Nirbhay K., Takahashi, Taisuke, Patane, Michael A.

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Selective PPARδ Modulators Improve Mitochondrial Function: Potential Treatment for Duchenne Muscular Dystrophy (DMD) von Lagu, Bharat, Kluge, Arthur F, Tozzo, Effie, Fredenburg, Ross, Bell, Eric L, Goddeeris, Matthew M, Dwyer, Peter, Basinski, Andrew, Senaiar, Ramesh S, Jaleel, Mahaboobi, Tiwari, Nirbhay Kumar, Panigrahi, Sunil K, Krishnamurthy, Narasimha Rao, Takahashi, Taisuke, Patane, Michael A

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Correction to “Selective PPARδ Modulators Improve Mitochondrial Function: Potential Treatment for Duchenne Muscular Dystrophy (DMD)” von Lagu, Bharat, Kluge, Arthur F, Tozzo, Effie, Fredenburg, Ross, Bell, Eric L, Goddeeris, Matthew M, Dwyer, Peter, Basinski, Andrew, Senaiar, Ramesh S, Jaleel, Mahaboobi, Tiwari, Nirbhay Kumar, Panigrahi, Sunil K, Krishnamurthy, Narasimha Rao, Takahashi, Taisuke, Patane, Michael A

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Sarcoglycan Complex: IMPLICATIONS FOR METABOLIC DEFECTS IN MUSCULAR DYSTROPHIES von Groh, Séverine, Zong, Haihong, Goddeeris, Matthew M, Lebakken, Connie S, Venzke, David, Pessin, Jeffrey E, Campbell, Kevin P

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An HMGA2-IGF2BP2 Axis Regulates Myoblast Proliferation and Myogenesis von Li, Zhizhong, Gilbert, Jason A., Zhang, Yunyu, Zhang, Minsi, Qiu, Qiong, Ramanujan, Krishnan, Shavlakadze, Tea, Eash, John K., Scaramozza, Annarita, Goddeeris, Matthew M., Kirsch, David G., Campbell, Kevin P., Brack, Andrew S., Glass, David J.

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Sarcoglycan Complex von Groh, Séverine, Zong, Haihong, Goddeeris, Matthew M., Lebakken, Connie S., Venzke, David, Pessin, Jeffrey E., Campbell, Kevin P.

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Behavioral Responses to Odorants in Drosophila Require Nervous System Expression of the β Integrin Gene Myospheroid von Bhandari, Poonam, Gargano, Julia Warner, Goddeeris, Matthew M., Grotewiel, Michael S.

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Behavioral Responses to Odorants in Drosophila Require Nervous System Expression of the   Integrin Gene Myospheroid von Bhandari, P.

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