Gene Therapy for Rare Neurological Disorders von Flotte, Terence R., Gessler, Dominic J.

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GammaTile (R): Surgically targeted radiation therapy for glioblastomas von Gessler, Dominic J., Ferreira, Clara, Dusenbery, Kathryn, Chen, Clark C.

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Global CNS Transduction of Adult Mice by Intravenously Delivered rAAVrh.8 and rAAVrh.10 and Nonhuman Primates by rAAVrh.10 von Yang, Bin, Li, Shaoyong, Wang, Hongyan, Guo, Yansu, Gessler, Dominic J, Cao, Chunyan, Su, Qin, Kramer, Joshua, Zhong, Li, Ahmed, Seemin Seher, Zhang, Hongwei, He, Ran, Desrosiers, Ronald C, Brown, Robert, Xu, Zuoshang, Gao, Guangping

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Canavan Disease as a Model for Gene Therapy-Mediated Myelin Repair von Lotun, Anoushka, Gessler, Dominic J., Gao, Guangping

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Adeno-associated virus as a delivery vector for gene therapy of human diseases von Wang, Jiang-Hui, Gessler, Dominic J., Zhan, Wei, Gallagher, Thomas L., Gao, Guangping

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Gene Therapy for the Treatment of Neurological Disorders: Metabolic Disorders von Gessler, Dominic J., Gao, Guangping

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Structural characterization of a novel human adeno-associated virus capsid with neurotropic properties von Hsu, Hung-Lun, Brown, Alexander, Loveland, Anna B., Lotun, Anoushka, Xu, Meiyu, Luo, Li, Xu, Guangchao, Li, Jia, Ren, Lingzhi, Su, Qin, Gessler, Dominic J., Wei, Yuquan, Tai, Phillip W. L., Korostelev, Andrei A., Gao, Guangping

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Editorial: Myelin Repair: At the Crossing-Lines of Myelin Biology and Gene Therapy von Fröhlich, Dominik, Gessler, Dominic J, Klugmann, Matthias

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GammaTile® (GT) as a brachytherapy platform for rapidly proliferating glioblastomas: from case series to clinical trials von Yekula, Anudeep, Gessler, Dominic J., Ferreira, Clara, Shah, Rena, Reynolds, Margaret, Dusenbery, Kathryn, Chen, Clark C.

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Intravenous Infusion of AAV for Widespread Gene Delivery to the Nervous System von Gessler, Dominic J., Tai, Phillip W. L., Li, Jia, Gao, Guangping

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Cas9-mediated allelic exchange repairs compound heterozygous recessive mutations in mice von Wang, Dan, Li, Jia, Song, Chun-Qing, Tran, Karen, Mou, Haiwei, Wu, Pei-Hsuan, Tai, Phillip W L, Mendonca, Craig A, Ren, Lingzhi, Wang, Blake Y, Su, Qin, Gessler, Dominic J, Zamore, Phillip D, Xue, Wen, Gao, Guangping

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Reuben Matalon, MD, PhD, FACMG (1935-2021) von Matalon, Dena R, Velagaleti, Gopalrao, Ahmed, Seemin S, Gessler, Dominic J, Gao, Guangping

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Renewal of oligodendrocyte lineage reverses dysmyelination and CNS neurodegeneration through corrected N-acetylaspartate metabolism von Lotun, Anoushka, Li, Danning, Xu, Hongxia, Su, Qin, Tuncer, Serafettin, Sanmiguel, Julio, Mooney, Morgan, Baer, Christina E., Ulbrich, Russell, Eyles, Stephen J., Strittmatter, Lara, Hayward, Lawrence J., Gessler, Dominic J., Gao, Guangping

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Adeno-associated virus serotype rh.10 displays strong muscle tropism following intraperitoneal delivery von Ai, Jianzhong, Li, Jia, Gessler, Dominic J., Su, Qin, Wei, Qiang, Li, Hong, Gao, Guangping

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Transcriptome Profiling of Neovascularized Corneas Reveals miR-204 as a Multi-target Biotherapy Deliverable by rAAVs von Lu, Yi, Tai, Phillip W.L., Ai, Jianzhong, Gessler, Dominic J., Su, Qin, Yao, Xieyi, Zheng, Qiang, Zamore, Phillip D., Xu, Xun, Gao, Guangping

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A Rationally Engineered Capsid Variant of AAV9 for Systemic CNS-Directed and Peripheral Tissue-Detargeted Gene Delivery in Neonates von Wang, Dan, Li, Shaoyong, Gessler, Dominic J, Xie, Jun, Zhong, Li, Li, Jia, Tran, Karen, Van Vliet, Kim, Ren, Lingzhi, Su, Qin, He, Ran, Goetzmann, Jason E, Flotte, Terence R, Agbandje-McKenna, Mavis, Gao, Guangping

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Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation von Corti, Manuela, Byrne, Barry J., Gessler, Dominic J., Thompson, Grace, Norman, Samantha, Lammers, Jenna, Coleman, Kirsten E., Liberati, Cristina, Elder, Melissa E., Escolar, Maria L., Tuna, Ibrahim S., Mesaros, Clementina, Kleiner, Gary I., Barbouth, Deborah S., Gray-Edwards, Heather L., Clement, Nathalie, Cleaver, Brian D., Gao, Guangping

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Redirecting N -acetylaspartate metabolism in the central nervous system normalizes myelination and rescues Canavan disease von Gessler, Dominic J, Li, Danning, Xu, Hongxia, Su, Qin, Sanmiguel, Julio, Tuncer, Serafettin, Moore, Constance, King, Jean, Matalon, Reuben, Gao, Guangping

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GammaTile® brachytherapy in the treatment of recurrent glioblastomas von Gessler, Dominic J, Neil, Elizabeth C, Shah, Rena, Levine, Joseph, Shanks, James, Wilke, Christopher, Reynolds, Margaret, Zhang, Shunqing, Özütemiz, Can, Gencturk, Mehmet, Folkertsma, Mark, Bell, W Robert, Chen, Liam, Ferreira, Clara, Dusenbery, Kathryn, Chen, Clark C

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Producing high-quantity and high-quality recombinant adeno-associated virus by low-cis triple transfection von Liu, Hao, Zhang, Yue, Yip, Mitchell, Ren, Lingzhi, Liang, Jialing, Chen, Xiupeng, Liu, Nan, Du, Ailing, Wang, Jiaming, Chang, Hao, Oh, Hyejin, Zhou, Chen, Xing, Ruxiao, Xu, Mengyao, Guo, Peiyi, Gessler, Dominic, Xie, Jun, Tai, Phillip W.L., Gao, Guangping, Wang, Dan

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