The 2017 IUIS Phenotypic Classification for Primary Immunodeficiencies von Bousfiha, Aziz, Jeddane, Leïla, Picard, Capucine, Ailal, Fatima, Bobby Gaspar, H., Al-Herz, Waleed, Chatila, Talal, Crow, Yanick J., Cunningham-Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Holland, Steven M., Klein, Christoph, Morio, Tomohiro, Ochs, Hans D., Oksenhendler, Eric, Puck, Jennifer, Tang, Mimi L. K., Tangye, Stuart G., Torgerson, Troy R., Casanova, Jean-Laurent, Sullivan, Kathleen E.

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International Union of Immunological Societies: 2017 Primary Immunodeficiency Diseases Committee Report on Inborn Errors of Immunity von Picard, Capucine, Bobby Gaspar, H., Al-Herz, Waleed, Bousfiha, Aziz, Casanova, Jean-Laurent, Chatila, Talal, Crow, Yanick J., Cunningham-Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Holland, Steven M., Klein, Christoph, Morio, Tomohiro, Ochs, Hans D., Oksenhendler, Eric, Puck, Jennifer, Tang, Mimi L. K., Tangye, Stuart G., Torgerson, Troy R., Sullivan, Kathleen E.

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Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy von Eichler, Florian, Duncan, Christine, Musolino, Patricia L, Orchard, Paul J, De Oliveira, Satiro, Thrasher, Adrian J, Armant, Myriam, Dansereau, Colleen, Lund, Troy C, Miller, Weston P, Raymond, Gerald V, Sankar, Raman, Shah, Ami J, Sevin, Caroline, Gaspar, H. Bobby, Gissen, Paul, Amartino, Hernan, Bratkovic, Drago, Smith, Nicholas J.C, Paker, Asif M, Shamir, Esther, O’Meara, Tara, Davidson, David, Aubourg, Patrick, Williams, David A

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Primary Immunodeficiency Diseases: an Update on the Classification from the International Union of Immunological Societies Expert Committee for Primary Immunodeficiency 2015 von Picard, Capucine, Al-Herz, Waleed, Bousfiha, Aziz, Casanova, Jean-Laurent, Chatila, Talal, Conley, Mary Ellen, Cunningham-Rundles, Charlotte, Etzioni, Amos, Holland, Steven M., Klein, Christoph, Nonoyama, Shigeaki, Ochs, Hans D., Oksenhendler, Eric, Puck, Jennifer M., Sullivan, Kathleen E., Tang, Mimi L K., Franco, Jose Luis, Gaspar, H. Bobby

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Neonatal diagnosis of severe combined immunodeficiency leads to significantly improved survival outcome: the case for newborn screening von Brown, Lucinda, Xu-Bayford, Jinhua, Allwood, Zoe, Slatter, Mary, Cant, Andrew, Davies, E. Graham, Veys, Paul, Gennery, Andrew R., Gaspar, H. Bobby

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Primary immunodeficiency diseases: an update on the classification from the international union of immunological societies expert committee for primary immunodeficiency von Al-Herz, Waleed, Bousfiha, Aziz, Casanova, Jean-Laurent, Chatila, Talal, Conley, Mary Ellen, Cunningham-Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Gaspar, H Bobby, Holland, Steven M, Klein, Christoph, Nonoyama, Shigeaki, Ochs, Hans D, Oksenhendler, Erik, Picard, Capucine, Puck, Jennifer M, Sullivan, Kate, Tang, Mimi L K

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How I treat ADA deficiency von Gaspar, H. Bobby, Aiuti, Alessandro, Porta, Fulvio, Candotti, Fabio, Hershfield, Michael S., Notarangelo, Luigi D.

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Thymus transplantation for complete DiGeorge syndrome: European experience von Davies, E. Graham, FRCPCH, Cheung, Melissa, BSc, Gilmour, Kimberly, PhD, Maimaris, Jesmeen, MRCPCH, Curry, Joe, FRCS, Furmanski, Anna, PhD, Sebire, Neil, FRCPATH, Halliday, Neil, MB, BSc, Mengrelis, Konstantinos, PhD, Adams, Stuart, PhD, Bernatoniene, Jolanta, MD, Bremner, Ronald, FRCPCH, Browning, Michael, FRCPATH, Devlin, Blythe, PhD, Erichsen, Hans Christian, MD, Gaspar, H. Bobby, PhD, Hutchison, Lizzie, RCN, Ip, Winnie, PhD, Ifversen, Marianne, MD, Leahy, T. Ronan, PhD, McCarthy, Elizabeth, PhD, Moshous, Despina, PhD, Neuling, Kim, FRCPCH, Pac, Malgorzata, MD, Papadopol, Alina, MD, Parsley, Kathryn L., PhD, Poliani, Luigi, PhD, Ricciardelli, Ida, PhD, Sansom, David M., PhD, Voor, Tiia, MD, Worth, Austen, PhD, Crompton, Tessa, PhD, Markert, M. Louise, PhD, Thrasher, Adrian J., PhD

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The 2015 IUIS Phenotypic Classification for Primary Immunodeficiencies von Bousfiha, Aziz, Jeddane, Leïla, Al-Herz, Waleed, Ailal, Fatima, Casanova, Jean‐Laurent, Chatila, Talal, Conley, Mary Ellen, Cunningham‐Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Gaspar, H. Bobby, Holland, Steven M., Klein, Christoph, Nonoyama, Shigeaki, Ochs, Hans D., Oksenhendler, Eric, Picard, Capucine, Puck, Jennifer M., Sullivan, Kathleen E., Tang, Mimi L. K.

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Hematopoietic SCT in Europe: data and trends in 2011 von Passweg, J R, Baldomero, H, Bregni, M, Cesaro, S, Dreger, P, Duarte, R F, Falkenburg, J H F, Kröger, N, Farge-Bancel, D, Bobby Gaspar, H, Marsh, J, Mohty, M, Peters, C, Sureda, A, Velardi, A, Ruiz de Elvira, C, Madrigal, A

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Gene and cell therapy for children — New medicines, new challenges? von Buckland, Karen F., Bobby Gaspar, H.

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How I treat severe combined immunodeficiency von Gaspar, H. Bobby, Qasim, Waseem, Davies, E. Graham, Rao, Kanchan, Amrolia, Persis J., Veys, Paul

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Gene therapy for ADA-SCID: defining the factors for successful outcome von Gaspar, H. Bobby

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Long-Term Immune Recovery After Hematopoietic Stem Cell Transplantation for ADA Deficiency: a Single-Center Experience von Kreins, Alexandra Y., Velasco, Helena F., Cheong, Kai-Ning, Rao, Kanchan, Veys, Paul, Worth, Austen, Gaspar, H. Bobby, Booth, Claire

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Outcome of hematopoietic stem cell transplantation for adenosine deaminase–deficient severe combined immunodeficiency von Hassan, Amel, Booth, Claire, Brightwell, Alex, Allwood, Zoe, Veys, Paul, Rao, Kanchan, Hönig, Manfred, Friedrich, Wilhelm, Gennery, Andrew, Slatter, Mary, Bredius, Robbert, Finocchi, Andrea, Cancrini, Caterina, Aiuti, Alessandro, Porta, Fulvio, Lanfranchi, Arnalda, Ridella, Michela, Steward, Colin, Filipovich, Alexandra, Marsh, Rebecca, Bordon, Victoria, Al-Muhsen, Saleh, Al-Mousa, Hamoud, Alsum, Zobaida, Al-Dhekri, Hasan, Al Ghonaium, Abdulaziz, Speckmann, Carsten, Fischer, Alain, Mahlaoui, Nizar, Nichols, Kim E., Grunebaum, Eyal, Al Zahrani, Daifulah, Roifman, Chaim M., Boelens, Jaap, Davies, E. Graham, Cavazzana-Calvo, Marina, Notarangelo, Luigi, Gaspar, H. Bobby

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Metabolite and thymocyte development defects in ADA-SCID mice receiving enzyme replacement therapy von Moretti, Federico A., Giardino, Giuliana, Attenborough, Teresa C. H., Gkazi, Athina Soragia, Margetts, Ben K., la Marca, Giancarlo, Fairbanks, Lynette, Crompton, Tessa, Gaspar, H. Bobby

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Author Correction: Metabolite and thymocyte development defects in ADA-SCID mice receiving enzyme replacement therapy von Moretti, Federico A., Giardino, Giuliana, Attenborough, Teresa C. H., Gkazi, Athina Soragia, Margetts, Ben K., la Marca, Giancarlo, Fairbanks, Lynette, Crompton, Tessa, Gaspar, H. Bobby

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Long-term lymphoid progenitors independently sustain naïve T and NK cell production in humans von Izotova, Natalia, Rivat, Christine, Baricordi, Cristina, Blanco, Elena, Pellin, Danilo, Watt, Eleanor, Gkazi, Athina S., Adams, Stuart, Gilmour, Kimberly, Bayford, Jinhua, Booth, Claire, Gaspar, H. Bobby, Thrasher, Adrian J., Biasco, Luca

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Autoimmune lymphoproliferative syndrome: molecular basis of disease and clinical phenotype von Worth, Austen, Thrasher, Adrian J., Bobby Gaspar, H.

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Mutations in linker for activation of T cells (LAT) lead to a novel form of severe combined immunodeficiency von Bacchelli, Chiara, PhD, Moretti, Federico A., PhD, Carmo, Marlene, PhD, Adams, Stuart, PhD, Stanescu, Horia C., PhD, Pearce, Kerra, PhD, Madkaikar, Manisha, MD, PhD, Gilmour, Kimberly C., PhD, Nicholas, Adeline K., PhD, Woods, C. Geoffrey, MD, PhD, Kleta, Robert, MD, PhD, Beales, Phil L., MD, PhD, Qasim, Waseem, MD, PhD, Gaspar, H. Bobby, MD, PhD

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