A different type of genetic therapy: correcting a defective gene using antisense oligonucleotide treatment in CEP290 p.Cys998X LCA von Drack, Arlene V., Russell, Stephen R., Cideciyan, Artur V., Jacobson, Samuel G., Leroy, Bart P., Pfeifer, Wanda L., Dumitrescu, Alina V., Garafolo, Alexandra V., Ho, Allen C., Van Cauwenbergh, Caroline, De Zaeytijd, Julie, Hollander, Wil den, Schwartz, Michael R., Asmus, Fredrich, Girach, Aniz

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