The transformative potential of HSC gene therapy as a genetic medicine von Sagoo, Pervinder, Gaspar, H. Bobby

Volltext

Severe combined immunodeficiency: recent developments and guidance on clinical management von Rivers, Lizzy, Gaspar, H Bobby

Volltext

The 2017 IUIS Phenotypic Classification for Primary Immunodeficiencies von Bousfiha, Aziz, Jeddane, Leïla, Picard, Capucine, Ailal, Fatima, Bobby Gaspar, H., Al-Herz, Waleed, Chatila, Talal, Crow, Yanick J., Cunningham-Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Holland, Steven M., Klein, Christoph, Morio, Tomohiro, Ochs, Hans D., Oksenhendler, Eric, Puck, Jennifer, Tang, Mimi L. K., Tangye, Stuart G., Torgerson, Troy R., Casanova, Jean-Laurent, Sullivan, Kathleen E.

Volltext

Gene and cell therapy for children — New medicines, new challenges? von Buckland, Karen F., Bobby Gaspar, H.

Volltext

Tearing RAGs apart von Gaspar, H. Bobby

Volltext

Gene therapy for ADA-SCID: defining the factors for successful outcome von Gaspar, H. Bobby

Volltext

International Union of Immunological Societies: 2017 Primary Immunodeficiency Diseases Committee Report on Inborn Errors of Immunity von Picard, Capucine, Bobby Gaspar, H., Al-Herz, Waleed, Bousfiha, Aziz, Casanova, Jean-Laurent, Chatila, Talal, Crow, Yanick J., Cunningham-Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Holland, Steven M., Klein, Christoph, Morio, Tomohiro, Ochs, Hans D., Oksenhendler, Eric, Puck, Jennifer, Tang, Mimi L. K., Tangye, Stuart G., Torgerson, Troy R., Sullivan, Kathleen E.

Volltext

Gene-ectomy: Gene Ablation with CRISPR/Cas9 in Human Hematopoietic Cells von Calero-Garcia, Miguel, Gaspar, H. Bobby

Volltext

How We Manage Adenosine Deaminase-Deficient Severe Combined Immune Deficiency (ADA SCID) von Kohn, Donald B., Gaspar, H. Bobby

Volltext

Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy von Eichler, Florian, Duncan, Christine, Musolino, Patricia L, Orchard, Paul J, De Oliveira, Satiro, Thrasher, Adrian J, Armant, Myriam, Dansereau, Colleen, Lund, Troy C, Miller, Weston P, Raymond, Gerald V, Sankar, Raman, Shah, Ami J, Sevin, Caroline, Gaspar, H. Bobby, Gissen, Paul, Amartino, Hernan, Bratkovic, Drago, Smith, Nicholas J.C, Paker, Asif M, Shamir, Esther, O’Meara, Tara, Davidson, David, Aubourg, Patrick, Williams, David A

Volltext

Gene therapy for monogenic disorders of the bone marrow von Ghosh, Sujal, Thrasher, Adrian J., Gaspar, H. Bobby

Volltext

Primary immunodeficiency diseases: an update on the classification from the international union of immunological societies expert committee for primary immunodeficiency von Al-Herz, Waleed, Bousfiha, Aziz, Casanova, Jean-Laurent, Chatila, Talal, Conley, Mary Ellen, Cunningham-Rundles, Charlotte, Etzioni, Amos, Franco, Jose Luis, Gaspar, H Bobby, Holland, Steven M, Klein, Christoph, Nonoyama, Shigeaki, Ochs, Hans D, Oksenhendler, Erik, Picard, Capucine, Puck, Jennifer M, Sullivan, Kate, Tang, Mimi L K

Volltext

Induced pluripotent stem cells and primary immunodeficiencies: A new frontier reached, a new world beyond? von Gaspar, H. Bobby, MD, PhD

Volltext

Primary Immunodeficiency Diseases: an Update on the Classification from the International Union of Immunological Societies Expert Committee for Primary Immunodeficiency 2015 von Picard, Capucine, Al-Herz, Waleed, Bousfiha, Aziz, Casanova, Jean-Laurent, Chatila, Talal, Conley, Mary Ellen, Cunningham-Rundles, Charlotte, Etzioni, Amos, Holland, Steven M., Klein, Christoph, Nonoyama, Shigeaki, Ochs, Hans D., Oksenhendler, Eric, Puck, Jennifer M., Sullivan, Kathleen E., Tang, Mimi L K., Franco, Jose Luis, Gaspar, H. Bobby

Volltext

A Practical Guide to Implementing Population Newborn Screening (NBS) for Severe Combined Immunodeficiency (SCID) von Gaspar, H.

Volltext

Pegademase bovine (PEG-ADA) for the treatment of infants and children with severe combined immunodeficiency (SCID) von Booth, Claire, Gaspar, H Bobby

Volltext

How I treat ADA deficiency von Gaspar, H. Bobby, Aiuti, Alessandro, Porta, Fulvio, Candotti, Fabio, Hershfield, Michael S., Notarangelo, Luigi D.

Volltext

Adenosine Deaminase Deficiency - More Than Just an Immunodeficiency von Whitmore, Kathryn V, Gaspar, Hubert B

Volltext

Neonatal diagnosis of severe combined immunodeficiency leads to significantly improved survival outcome: the case for newborn screening von Brown, Lucinda, Xu-Bayford, Jinhua, Allwood, Zoe, Slatter, Mary, Cant, Andrew, Davies, E. Graham, Veys, Paul, Gennery, Andrew R., Gaspar, H. Bobby

Volltext

Thymus transplantation for complete DiGeorge syndrome: European experience von Davies, E. Graham, FRCPCH, Cheung, Melissa, BSc, Gilmour, Kimberly, PhD, Maimaris, Jesmeen, MRCPCH, Curry, Joe, FRCS, Furmanski, Anna, PhD, Sebire, Neil, FRCPATH, Halliday, Neil, MB, BSc, Mengrelis, Konstantinos, PhD, Adams, Stuart, PhD, Bernatoniene, Jolanta, MD, Bremner, Ronald, FRCPCH, Browning, Michael, FRCPATH, Devlin, Blythe, PhD, Erichsen, Hans Christian, MD, Gaspar, H. Bobby, PhD, Hutchison, Lizzie, RCN, Ip, Winnie, PhD, Ifversen, Marianne, MD, Leahy, T. Ronan, PhD, McCarthy, Elizabeth, PhD, Moshous, Despina, PhD, Neuling, Kim, FRCPCH, Pac, Malgorzata, MD, Papadopol, Alina, MD, Parsley, Kathryn L., PhD, Poliani, Luigi, PhD, Ricciardelli, Ida, PhD, Sansom, David M., PhD, Voor, Tiia, MD, Worth, Austen, PhD, Crompton, Tessa, PhD, Markert, M. Louise, PhD, Thrasher, Adrian J., PhD

Volltext