Viral vector platforms within the gene therapy landscape von Bulcha, Jote T., Wang, Yi, Ma, Hong, Tai, Phillip W. L., Gao, Guangping

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Improved prime editors enable pathogenic allele correction and cancer modelling in adult mice von Liu, Pengpeng, Liang, Shun-Qing, Zheng, Chunwei, Mintzer, Esther, Zhao, Yan G., Ponnienselvan, Karthikeyan, Mir, Aamir, Sontheimer, Erik J., Gao, Guangping, Flotte, Terence R., Wolfe, Scot A., Xue, Wen

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Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo von Ibraheim, Raed, Tai, Phillip W. L., Mir, Aamir, Javeed, Nida, Wang, Jiaming, Rodríguez, Tomás C., Namkung, Suk, Nelson, Samantha, Khokhar, Eraj Shafiq, Mintzer, Esther, Maitland, Stacy, Chen, Zexiang, Cao, Yueying, Tsagkaraki, Emmanouela, Wolfe, Scot A., Wang, Dan, Pai, Athma A., Xue, Wen, Gao, Guangping, Sontheimer, Erik J.

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Developing AAV-delivered nonsense suppressor tRNAs for neurological disorders von Wang, Jiaming, Gao, Guangping, Wang, Dan

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Dynamics of a disinhibitory prefrontal microcircuit in controlling social competition von Zhang, Chaoyi, Zhu, Hong, Ni, Zheyi, Xin, Qiuhong, Zhou, Tingting, Wu, Runlong, Gao, Guangping, Gao, Zhihua, Ma, Huan, Li, Haohong, He, Miao, Zhang, Jue, Cheng, Heping, Hu, Hailan

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Adenovirus-Mediated Somatic Genome Editing of Pten by CRISPR/Cas9 in Mouse Liver in Spite of Cas9-Specific Immune Responses von Wang, Dan, Mou, Haiwei, Li, Shaoyong, Li, Yingxiang, Hough, Soren, Tran, Karen, Li, Jia, Yin, Hao, Anderson, Daniel G, Sontheimer, Erik J, Weng, Zhiping, Gao, Guangping, Xue, Wen

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Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo von Yin, Hao, Song, Chun-Qing, Dorkin, Joseph R, Zhu, Lihua J, Li, Yingxiang, Wu, Qiongqiong, Park, Angela, Yang, Junghoon, Suresh, Sneha, Bizhanova, Aizhan, Gupta, Ankit, Bolukbasi, Mehmet F, Walsh, Stephen, Bogorad, Roman L, Gao, Guangping, Weng, Zhiping, Dong, Yizhou, Koteliansky, Victor, Wolfe, Scot A, Langer, Robert, Xue, Wen, Anderson, Daniel G

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Structural characterization of a novel human adeno-associated virus capsid with neurotropic properties von Hsu, Hung-Lun, Brown, Alexander, Loveland, Anna B., Lotun, Anoushka, Xu, Meiyu, Luo, Li, Xu, Guangchao, Li, Jia, Ren, Lingzhi, Su, Qin, Gessler, Dominic J., Wei, Yuquan, Tai, Phillip W. L., Korostelev, Andrei A., Gao, Guangping

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Bone-targeting AAV-mediated silencing of Schnurri-3 prevents bone loss in osteoporosis von Yang, Yeon-Suk, Xie, Jun, Wang, Dan, Kim, Jung-Min, Tai, Phillip W. L., Gravallese, Ellen, Gao, Guangping, Shim, Jae-Hyuck

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Worldwide Epidemiology of Neutralizing Antibodies to Adeno-Associated Viruses von Calcedo, Roberto, Vandenberghe, Luk H., Gao, Guangping, Lin, Jianping, Wilson, James M.

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LATS suppresses mTORC1 activity to directly coordinate Hippo and mTORC1 pathways in growth control von Gan, Wenjian, Dai, Xiaoming, Dai, Xiangpeng, Xie, Jun, Yin, Shasha, Zhu, Junjie, Wang, Chen, Liu, Yuchen, Guo, Jianping, Wang, Min, Liu, Jing, Hu, Jia, Quinton, Ryan J., Ganem, Neil J., Liu, Pengda, Asara, John M., Pandolfi, Pier Paolo, Yang, Yingzi, He, Zhigang, Gao, Guangping, Wei, Wenyi

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Adeno-Associated Virus Delivery of Anti-HIV Monoclonal Antibodies Can Drive Long-Term Virologic Suppression von Martinez-Navio, José M., Fuchs, Sebastian P., Pantry, Shara N., Lauer, William A., Duggan, Natasha N., Keele, Brandon F., Rakasz, Eva G., Gao, Guangping, Lifson, Jeffrey D., Desrosiers, Ronald C.

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Adeno-associated virus as a delivery vector for gene therapy of human diseases von Wang, Jiang-Hui, Gessler, Dominic J., Zhan, Wei, Gallagher, Thomas L., Gao, Guangping

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Vectored Immunotherapeutics for Infectious Diseases: Can rAAVs Be The Game Changers for Fighting Transmissible Pathogens? von Zhan, Wei, Muhuri, Manish, Tai, Phillip W. L., Gao, Guangping

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Streamlined ex vivo and in vivo genome editing in mouse embryos using recombinant adeno-associated viruses von Yoon, Yeonsoo, Wang, Dan, Tai, Phillip W. L., Riley, Joy, Gao, Guangping, Rivera-Pérez, Jaime A.

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Suppression of heterotopic ossification in fibrodysplasia ossificans progressiva using AAV gene delivery von Yang, Yeon-Suk, Kim, Jung-Min, Xie, Jun, Chaugule, Sachin, Lin, Chujiao, Ma, Hong, Hsiao, Edward, Hong, Jaehyoung, Chun, Hyonho, Shore, Eileen M., Kaplan, Frederick S., Gao, Guangping, Shim, Jae-Hyuck

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Down-regulation of microRNA-203-3p initiates type 2 pathology during schistosome infection via elevation of interleukin-33 von He, Xing, Xie, Jun, Wang, Yange, Fan, Xiaobin, Su, Qin, Sun, Yue, Lei, Nanhang, Zhang, Dongmei, Gao, Guangping, Pan, Weiqing

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Domain-inlaid Nme2Cas9 adenine base editors with improved activity and targeting scope von Bamidele, Nathan, Zhang, Han, Dong, Xiaolong, Cheng, Haoyang, Gaston, Nicholas, Feinzig, Hailey, Cao, Hanbing, Kelly, Karen, Watts, Jonathan K., Xie, Jun, Gao, Guangping, Sontheimer, Erik J.

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AAV-Mediated Gene Therapy for Glycosphingolipid Biosynthesis Deficiencies von Yang, Huiya, Brown, Robert H., Wang, Dan, Strauss, Kevin A., Gao, Guangping

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Impaired mitochondrial oxidative metabolism in skeletal progenitor cells leads to musculoskeletal disintegration von Lin, Chujiao, Yang, Qiyuan, Guo, Dongsheng, Xie, Jun, Yang, Yeon-Suk, Chaugule, Sachin, DeSouza, Ngoc, Oh, Won-Taek, Li, Rui, Chen, Zhihao, John, Aijaz A., Qiu, Qiang, Zhu, Lihua Julie, Greenblatt, Matthew B., Ghosh, Sankar, Li, Shaoguang, Gao, Guangping, Haynes, Cole, Emerson, Charles P., Shim, Jae-Hyuck

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