Mechanism of Scrapie Prion Precipitation with Phosphotungstate Anions von Levine, Dana J, Stöhr, Jan, Falese, Lillian E, Ollesch, Julian, Wille, Holger, Prusiner, Stanley B, Long, Jeffrey R

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AAV2/6 Gene Therapy in a Murine Model of Fabry Disease Results in Supraphysiological Enzyme Activity and Effective Substrate Reduction von Yasuda, Makiko, Huston, Marshall W., Pagant, Silvere, Gan, Lin, St. Martin, Susan, Sproul, Scott, Richards, Daniel, Ballaron, Stephen, Hettini, Khaled, Ledeboer, Annemarie, Falese, Lillian, Cao, Liching, Lu, Yanmei, Holmes, Michael C., Meyer, Kathleen, Desnick, Robert J., Wechsler, Thomas

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Spermcasting of spermatozeugmata by the bivalves Nutricola confusa and N. tantilla von Falese, Lillian E, Russell, Michael P, Dollahon, Norman R

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A 3-month gene therapy single-dose IV administration pharmacology and safety study with ST-920 (isaralgagene civaparvovec) for Fabry disease in mice von Meyer, Kathleen E., Lorget, Florence, Prawdzik, Gregg, Falaleeva, Marina, Cao, Liching, Falese, Lillian, Huston, Marshall W., Hettini, Khaled, Lu, Yanmei, Ledeboer, Annemarie

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Impact of Pre-Existing Immunogenicity to AAV on Vector Transduction By Bmn 270, an AAV5-Based Gene Therapy Treatment for Hemophilia A von Long, Brian, Sandza, Krystal, Holcomb, Jennifer, Pherarolis, Juli, Crockett, Lucy, Falese, Lillian, Hayes, Greg, Arens, Jeremy, O'Neill, Charles A., Pryer, Nancy, Fonck, Carlos, Zoog, Stephen, Vettermann, Christian

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Liver-targeted AAV gene therapy vectors produced by a clinical scale manufacturing process result in high, continuous therapeutic levels of enzyme activity and effective substrate... von Huston, Marshall W., Yasuda, Makiko, Pagant, Silvere, Martin, Susan St, Cao, Liching, Falese, Lillian, Meyer, Kathleen, Desnick, Robert J., Wechsler, Thomas

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Spermcasting of spermatozeugmata by the bivalves N utricola confusa and N . tantilla von Falese, Lillian E., Russell, Michael P., Dollahon, Norman R.

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